未登录Engineering and Development of Optimal CRISPR Based Genome Modification Molecules for Safe and Effective LDL-C Lowering工程化开发最优CRISPR基基因组修饰分子以实现安全有效的LDL-C降低
Duncan-Lewis, Christopher; Harms, Matthew; Adil, Maroof; Alcantra-Lee, Raniel; Bardai, Farah; Bender, Kristina Oresic; Bale, Shyam Sundhar; Charles, Emeric; Chen, Kai-Yuan; Colin, Isabel; Corbo, Lana; Deiter, Fred; Demaree, Benjamin; Denny, Sarah; Fernandes, Jason; Gardner, Matthew; Hadaczek, Piotr; Hochman, Myles; Hsu, Bernadette; Karanth, Santhosh; Karmarkar, Maitreyee; Keller, Steven; Kozy, Heather; Krupa, Oleh; Leeman, Dena; Li, Yuexuan; Mirotsou, Maria; Mok, Amanda; Mrak, Anna; Narsineni, Lokesh; Ripley-Phipps, Sterling; Reimer, Kirsten; Szulwach, Keith; Shroff, Shilpa; Tran, Vanessa; Tung, Kuei-Ling; Wright, Addison; Oakes, Benjamin; Khakoo, Aarif .png)
分享.png)
收藏Persistent GDNF Expression 45 Months after Putaminal Infusion of AAV2-GDNF in a Patient with Parkinson's DiseaseHeiss, John D.; Ray-Chaudhury, Abhik; Kleiner, David E.; Ehrlich, Debra J.; Scott, Gretchen; Edwards, Nancy A.; Goldstein, David S.; Hammoud, Dima A.; Hadaczek, Piotr; Van Laar, Victor S.; Graff, Shantelle A.; Herscovitch, Peter; Lungu, Codrin; Hallett, Mark; Lonser, Russell R.; Zaghloul, Kareem A.; Bankiewicz, Krystof S. 分享 收藏 GDNF gene therapy for alcohol use disorder in male non-human primatesFord, Matthew M.; George, Brianna E.; Van Laar, Victor S.; Holleran, Katherine M.; Naidoo, Jerusha; Hadaczek, Piotr; Vanderhooft, Lauren E.; Peck, Emily G.; Dawes, Monica H.; Ohno, Kousaku; Bringas, John; McBride, Jodi L.; Samaranch, Lluis; Forsayeth, John R.; Jones, Sara R.; Grant, Kathleen A.; Bankiewicz, Krystof S. 分享 收藏 A traceless linker for aliphatic amines that rapidly and quantitatively fragments after reductionHe, Maomao; Li, Jie; Han, Hesong; Borges, Clarissa Araujo; Neiman, Gabriel; Roise, Joachim Justad; Hadaczek, Piotr; Mendonsa, Rima; Holm, Victoria R.; Wilson, Ross C.; Bankiewicz, Krystof; Zhang, Yumiao; Sadlowski, Corinne M.; Healy, Kevin; Riley, Lee W.; Murthy, Niren 分享 收藏 Adeno-associated viral vector serotype 9-based gene therapy for Niemann-Pick disease type ASamaranch, Lluis; Perez-Canamas, Azucena; Soto-Huelin, Beatriz; Sudhakar, Vivek; Jurado-Arjona, Jeronimo; Hadaczek, Piotr; Avila, Jesus; Bringas, John R.; Casas, Josefina; Chen, Haifeng; He, Xingxuan; Schuchman, Edward H.; Cheng, Seng H.; Forsayeth, John; Bankiewicz, Krystof S.; Dolores Ledesma, Maria 分享 收藏 分享 收藏 Extensive Transduction and Enhanced Spread of a Modified AAV2 Capsid in the Non-human Primate CNSNaidoo, Jerusha; Stanek, Lisa M.; Ohno, Kousaku; Trewman, Savanah; Samaranch, Lluis; Hadaczek, Piotr; O'Riordan, Catherine; Sullivan, Jennifer; Sebastian, Waldy San; Bringas, John R.; Snieckus, Christopher; Mahmoodi, Amin; Mahmoodi, Amir; Forsayeth, John; Bankiewicz, Krystof S.; Shihabuddin, Lamya S. 分享 收藏 Widespread Gene Delivery to the Nonhuman Primate Brain for the Treatment of Huntington's DiseaseHadaczek, Piotr; Stanek, Lisa; Ciesielska, Agnieszka; Pivirotto, Philip; O'Riordan, Catherine; Mastis, Bryan; Sebastian, Waldy San; Forsayeth, John; Cheng, Seng H.; Bankiewicz, Krystof S.; Shihabuddin, Lamya S. 分享 收藏 Cytomegalovirus Immediate-Early Proteins Promote Stemness Properties in GlioblastomaSoroceanu, Liliana; Matlaf, Lisa; Khan, Sabeena; Akhavan, Armin; Singer, Eric; Bezrookove, Vladimir; Decker, Stacy; Ghanny, Saleena; Hadaczek, Piotr; Bengtsson, Henrik; Ohlfest, John; Luciani-Torres, Maria-Gloria; Harkins, Lualhati; Perry, Arie; Guo, Hong; Soteropoulos, Patricia; Cobbs, Charles S. 分享 收藏 分享 收藏 Repeated Infusion of AAV2-hAADC Into the Thalamus of Non-Human Primates: Effect of Anti-AAV2 Antibodies on Transgene ExpressionSamaranch, Lluis; Hadaczek, Piotr; Kells, Adrian P.; Bringas, John; Stockinger, Diane; San Sebastian, Waldy; Macayan, Michael; Samineni, Sridhar; Pivirotto, Philip; Forsayeth, John; Bankiewicz, Krystof 分享 收藏 The influence of AAV2-mediated gene transfer of human IL-10 on neurodegeneration and immune response in a murine model of Parkinson's diseaseJoniec-Maciejak, Ilona; Ciesielska, Agnieszka; Wawer, Adriana; Sznejder-Pacholek, Anna; Schwenkgrub, Joanna; Cudna, Agnieszka; Hadaczek, Piotr; Bankiewicz, Kristof S.; Czlonkowska, Anna; Czlonkowski, Andrzej 分享 收藏 分享 收藏 分享 收藏 分享 收藏 分享 收藏 分享 收藏 分享 收藏 Real-time MR Imaging With Gadoteridol Predicts Distribution of Transgenes After Convection-enhanced Delivery of AAV2 VectorsSu, Xiaomin; Kells, Adrian P.; Salegio, Ernesto Aguilar; Richardson, R. Mark; Hadaczek, Piotr; Beyer, Janine; Bringas, John; Pivirotto, Philip; Forsayeth, John; Bankiewicz, Krystof S. 分享 收藏 分享 收藏 
.png){kind=icon}
.png){kind=icon}
.png){kind=icon}
.png){kind=icon}
