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Gene-based Therapy in a Mouse Model of Blue Cone Monochromacy (vol 8, 2017) Zhang, Yuxin; Deng, Wen-Tao; Du, Wei; Zhu, Ping; Li, Jie; Xu, Fan; Sun, Jingfen; Gerstner, Cecilia D.; Baehr, Wolfgang; Boye, Sanford L.; Zhao, Chen; Hauswirth, William W.; Pang, Ji-jing 分享 收藏
Gene-based Therapy in a Mouse Model of Blue Cone Monochromacy Zhang, Yuxin; Deng, Wen-Tao; Du, Wei; Zhu, Ping; Li, Jie; Xu, Fan; Sun, Jingfen; Gerstner, Cecilia D.; Baehr, Wolfgang; Sanford, L. Boye; Zhao, Chen; Hauswirth, William W.; Pang, Ji-jing 分享 收藏
AAV-Mediated Lysophosphatidylcholine Acyltransferase 1 (Lpcat1) Gene Replacement Therapy Rescues Retinal Degeneration in rd11 Mice AAV介导的溶血磷脂酰胆碱酰基转移酶1 (Lpcat1) 基因替代疗法挽救rd11小鼠视网膜变性 Dai, Xufeng; Han, Juanjuan; Qi, Yan; Zhang, Hua; Xiang, Lue; Lv, Jineng; Li, Jie; Deng, Wen-Tao; Chang, Bo; Hauswirth, William W.; Pang, Ji-jing 分享 收藏
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Tyrosine-Mutant AAV8 Delivery of Human MERTK Provides Long-Term Retinal Preservation in RCS Rats Deng, Wen-Tao; Dinculescu, Astra; Li, Qiuhong; Boye, Sanford L.; Li, Jie; Gorbatyuk, Marina S.; Pang, Jijing; Chiodo, Vince A.; Matthes, Michael T.; Yasumura, Douglas; Liu, Li; Alkuraya, Fowzan S.; Zhang, Kang; Vollrath, Douglas; LaVail, Matthew M.; Hauswirth, William W. 分享 收藏
AAV5-mediated sFLT01 gene therapy arrests retinal lesions in Ccl2-/-/Cx3cr1-/- mice Tuo, Jingsheng; Pang, Ji-Jing; Cao, Xiaoguang; Shen, Defen; Zhang, Jun; Scaria, Abraham; Wadsworth, Samuel C.; Pechan, Peter; Boye, Sanford L.; Hauswirth, William W.; Chan, Chi-Chao 分享 收藏
Long-term Preservation of Cone Photoreceptors and Restoration of Cone Function by Gene Therapy in the Guanylate Cyclase-1 Knockout (GC1KO) Mouse Boye, Sanford L.; Conlon, Thomas; Erger, Kirsten; Ryals, Renee; Neeley, Andy; Cossette, Travis; Pang, Jijing; Dyka, Frank M.; Hauswirth, William W.; Boye, Shannon E. 分享 收藏
Long-term Retinal Function and Structure Rescue Using Capsid Mutant AAV8 Vector in the rd10 Mouse, a Model of Recessive Retinitis Pigmentosa Pang, Ji-jing; Dai, Xufeng; Boye, Shannon E.; Barone, Ilaria; Boye, Sanford L.; Mao, Song; Everhart, Drew; Dinculescu, Astra; Liu, Li; Umino, Yumiko; Lei, Bo; Chang, Bo; Barlow, Robert; Strettoi, Enrica; Hauswirth, William W. 分享 收藏
Novel Properties of Tyrosine-mutant AAV2 Vectors in the Mouse Retina Petrs-Silva, Hilda; Dinculescu, Astra; Li, Qiuhong; Deng, Wen-Tao; Pang, Ji-jing; Min, Seok-Hong; Chiodo, Vince; Neeley, Andy W.; Govindasamy, Lakshmanan; Bennett, Antonette; Agbandje-McKenna, Mavis; Zhong, Li; Li, Baozheng; Jayandharan, Giridhara R.; Srivastava, Arun; Lewin, Alfred S.; Hauswirth, William W. 分享 收藏
Gene Therapy Rescues Cone Structure and Function in the 3-Month-Old rd12 Mouse: A Model for Midcourse RPE65 Leber Congenital Amaurosis Li, Xia; Li, Wensheng; Dai, Xufeng; Kong, Fansheng; Zheng, Qinxiang; Zhou, Xiangtian; Lue, Fan; Chang, Bo; Rohrer, Baerbel; Hauswirth, William. W.; Qu, Jia; Pang, Ji-jing 分享 收藏
Self-complementary AAV5 vector facilitates quicker transgene expression in photoreceptor and retinal pigment epithelial cells of normal mouse Kong, Fansheng; Li, Wensheng; Li, Xia; Zheng, Qinxiang; Dai, Xufeng; Zhou, Xiangtian; Boye, Sanford L.; Hauswirth, William W.; Qu, Jia; Pang, Ji-Jing 分享 收藏
Functional interchangeability of rod and cone transducin α-subunits Deng, Wen-Tao; Sakurai, Keisuke; Liu, Jianwen; Dinculescu, Astra; Li, Jie; Pang, Jijing; Min, Seok-Hong; Chiodo, Vince A.; Boye, Sanford L.; Chang, Bo; Kefalov, Vladimir J.; Hauswirth, William W. 分享 收藏
High-efficiency Transduction of the Mouse Retina by Tyrosine-mutant AAV Serotype Vectors Petrs-Silva, Hilda; Dinculescu, Astra; Li, Qiuhong; Min, Seok-Hong; Chiodo, Vince; Pang, Ji-Jing; Zhong, Li; Zolotukhin, Sergei; Srivastava, Arun; Lewin, Alfred S.; Hauswirth, William W. 分享 收藏
AAV-mediated gene therapy for retinal degeneration in the rd10 mouse containing a recessive PDEβ mutation Pang, Ji-jing; Boye, Sanford L.; Kumar, Ashok; Dinculescu, Astra; Deng, Wentao; Li, Jie; Li, Qiuhong; Rani, Asha; Foster, Thomas C.; Chang, Bo; Hawes, Norman L.; Boatright, Jeffrey H.; Hauswirth, William W. 分享 收藏
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Human gene therapy for RPE65 isomerase deficiency activates the retinoid cycle of vision but with slow rod kinetics Cideciyan, Artur V.; Aleman, Tomas S.; Boye, Sanford L.; Schwartz, Sharon B.; Kaushal, Shalesh; Roman, Alejandro J.; Pang, Ji-Jing; Sumaroka, Alexander; Windsor, Elizabeth A. M.; Wilson, James M.; Flotte, Terence R.; Fishman, Gerald A.; Heon, Elise; Stone, Edwin M.; Byrne, Barry J.; Jacobson, Samuel G.; Hauswirth, William W. 分享 收藏