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Haydar Frangoul

Sarah Cannon Research Institute

42H指数
266论文数
7.5K被引数
收录论文 41
发表时间
Incidence of Human Leukocyte Antigen (HLA) Class I Antibodies and Impact on Platelet Engraftment, Transfusions and Bleeding in Recipients of Gene Therapy for Sickle Cell Disease and Transfusion Dependent Beta Thalassemia人类白细胞抗原(HLA)I类抗体的发生率及其对镰状细胞病和依赖输血的β地中海贫血基因治疗受者血小板植入、输血和出血的影响
err2026-08-15
err0
PREAI
errHaydar Frangoul; Meghann McManus; Clinton Carroll; Sallyanne Fossey; Mathew Rowe; Addison Roelandts; Eileen McCartney; Shelby Aide; Amanda Stults; Sam Forbes; Christy Riggins; Kala Morgan; Rayea Tilman; Morgan Duckworth; Natalie Davis; Katie Bruce; Minoo Battiwala; Jennifer Domm; Misty Evans
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Prime Editing for p47phox-Deficient Chronic Granulomatous DiseaseGori, J.L.; Haddad, E.; Frangoul, H.; Kohn, D.B.; Morris, E.C.; Martin, B.N.; Deary, B.A.; Nickerson, M.; Scholz, R.L.; Fernandez, I.; et al. 基因组编辑技术用于p47phox缺陷型慢性肉芽肿病。N. Engl. J. Med. 2025. [Google Scholar] [CrossRef] [PubMed]
err2025-12-01
err0
PREAI
errGori, Jennifer L.; Haddad, Elie; Frangoul, Haydar; Kohn, Donald B.; Morris, Emma C.; Martin, Bradley N.; Deary, Briana A.; Nickerson, McKinley; Scholz, Rebecca L.; Fernandez, Isabel; Leveille, Karine; De Ravin, Suk See; Kang, Elizabeth M.; Pierzynski, Marie; Estwick, Tyra; Littel, Patricia; Kuhns, Douglas B.; Long Priel, Debra A.; Teira, Pierre; Turvey, Stuart; Arnold, Jordyn; Evans, Misty D.; McManus, Meghann; Carpenter, Ben; Waterman, David P.; Anzalone, Andrew V.; Petrusich, Alexandria; Osuna, Christa E.; O'Malley, Tiernan T.; Stewart-Ornstein, Jacob; Heath, Jack M.; Nehilla, Barrett J.; Asmal, Mohammed; Malech, Harry L.
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Improvements in Health-Related Quality of Life in Patients with Transfusion-Dependent β-Thalassemia After Exagamglogene Autotemcel输血依赖性β-地中海贫血患者在接受Exagamglogene autotemcel治疗后健康相关生活质量改善
err2025-08-28
err0
errOAAI
errJosu de la Fuente; Haydar Frangoul; Peter Lang; Donna Wall; Roland Meisel; Selim Corbacioglu; Amanda M. Li; Ami J. Shah; Ben Carpenter; Janet L. Kwiatkowski; Markus Y. Mapara; Robert I. Liem; Joachim Rupprecht; Kevin H.M. Kuo; Hayley Merkeley; Mattia Algeri; Wally Smith; Puja Kohli; Nanxin Li; Jaime Rubin; Siyu Zhang; William Hobbs; Franco Locatelli
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Improvements in Health-Related Quality of Life in Patients with Severe Sickle Cell Disease After Exagamglogene Autotemcel重症镰状细胞病患者在Exagamglogene autotemcel治疗后健康相关生活质量改善
err2025-08-28
err0
errOAAI
errAkshay Sharma; Franco Locatelli; Monica Bhatia; Lyndsay Molinari; Markus Y. Mapara; Robert I. Liem; Laurence Dedeken; Donna Wall; Michael J. Eckrich; Kevin H. M. Kuo; Wally Smith; Suzan Imren; Puja Kohli; Nanxin Li; Tina Liu; Jaime Rubin; William Hobbs; Stephan A. Grupp; Haydar Frangoul
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Best Practices in Gene Therapy for Sickle Cell Disease and Transfusion-dependent β-Thalassemia基因疗法在镰状细胞病和依赖输血的β-地中海贫血中的最佳实践
err2025-06-01
err0
PREAI
errHaydar Frangoul; Amanda Stults; Katie Bruce; Jennifer Domm; Clinton Carroll; Shelby Aide; Morgan Duckworth; Misty Evans; Meghann McManus
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Impact of Race and Ethnicity on Outcomes After Umbilical Cord Blood Transplantation种族和民族对脐血移植后结局的影响
err2024-10-01
err0
PREAI
errBallen, Karen; Wang, Tao; He, Naya; Knight, Jennifer M.; Hong, Sanghee; Frangoul, Haydar; Verdonck, Leo F.; Steinberg, Amir; Diaz, Miguel A.; Lemaistre, C. Fred; Badawy, Sherif M.; Pu, Jeffrey J.; Hashem, Hasan; Savani, Bipin; Sharma, Akshay; Lazarus, Hillard M.; Abid, Muhammad Bilal; Tay, Jason; Rangarajan, Hemalatha G.; Kindwall-Keller, Tamila; Freytes, Cesar O.; Beitinjaneh, Amer; Winestone, Lena E.; Gergis, Usama; Farhadfar, Nosha; Bhatt, Neel S.; Schears, Raquel M.; Gomez-Almaguer, David; Aljurf, Mahmoud; Agrawal, Vaibhav; Kuwatsuka, Yachiyo; Seo, Sachiko; Marks, David I.; Lehmann, Leslie; Wood, William A.; Hashmi, Shahrukh; Saber, Wael
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Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia
err2024-05-09
err21
PREAI
errLocatelli, F.; Lang, P.; Wall, D.; Meisel, R.; Corbacioglu, S.; Li, A. M.; de la Fuente, J.; Shah, A. J.; Carpenter, B.; Kwiatkowski, J. L.; Mapara, M.; Liem, R. I.; Cappellini, M. D.; Algeri, M.; Kattamis, A.; Sheth, S.; Grupp, S.; Handgretinger, R.; Kohli, P.; Shi, D.; Ross, L.; Bobruff, Y.; Simard, C.; Zhang, L.; Morrow, P. K.; Hobbs, W. E.; Frangoul, H.
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Exagamglogene Autotemcel for Severe Sickle Cell Disease
err2024-05-09
err54
PREAI
errFrangoul, H.; Locatelli, F.; Sharma, A.; Bhatia, M.; Mapara, M.; Molinari, L.; Wall, D.; Liem, R. I.; Telfer, P.; Shah, A. J.; Cavazzana, M.; Corbacioglu, S.; Rondelli, D.; Meisel, R.; Dedeken, L.; Lobitz, S.; de Montalembert, M.; Steinberg, M. H.; Walters, M. C.; Eckrich, M. J.; Imren, S.; Bower, L.; Simard, C.; Zhou, W.; Xuan, F.; Morrow, P. K.; Hobbs, W. E.; Grupp, S. A.
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Autologous gene therapy for hemoglobinopathies: From bench to patient's bedside
err2024-05-01
err6
errOAAI
errLocatelli, Franco; Cavazzana, Marina; Frangoul, Haydar; de la Fuente, Josu; Algeri, Mattia; Meisel, Roland
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An integrated therapeutic approach to sickle cell disease management beyond infancy
err2023-05-12
err4
PREAI
errRibeil, Jean-Antoine; Pollock, Galia; Frangoul, Haydar; Steinberg, Martin H.
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Clinical Characteristics and Outcomes of COVID-19 in Pediatric and Early Adolescent and Young Adult Hematopoietic Stem Cell Transplant Recipients: A Cohort Study儿童、青少年和年轻成人造血干细胞移植受者新型冠状病毒肺炎的临床特征和结局: 一项队列研究
err2022-10-01
err10
errOAAI
errBhatt, Neel S.; Sharma, Akshay; St Martin, Andrew; Abid, Muhammad Bilal; Brown, Valerie, I; Diaz Perez, Miguel Angel; Frangoul, Haydar; Gadalla, Shahinaz M.; Herr, Megan M.; Krem, Maxwell M.; Lazarus, Hillard M.; Martens, Michael J.; Mehta, Parinda A.; Nishihori, Taiga; Prestidge, Tim; Pulsipher, Michael A.; Rangarajan, Hemalatha G.; Williams, Kirsten M.; Winestone, Lena E.; Yin, Dwight E.; Riches, Marcie L.; Dandoy, Christopher E.; Auletta, Jeffery J.
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Safety, Tolerability, and Population Pharmacokinetics of Intravenous and Oral Isavuconazonium Sulfate in Pediatric Patients
err2021-07-16
err31
errOAAI
errArrieta, Antonio C.; Neely, Michael; Day, J. Christopher; Rheingold, Susan R.; Sue, Paul K.; Muller, William J.; Danziger-Isakov, Lara A.; Chu, Julie; Yildirim, Inci; McComsey, Grace A.; Frangoul, Haydar A.; Chen, Tempe K.; Statler, Victoria A.; Steinbach, William J.; Yin, Dwight E.; Hamed, Kamal; Jones, Mark E.; Lademacher, Christopher; Desai, Amit; Micklus, Kelley; Phillips, Desiree Leiva; Kovanda, Laura L.; Walsh, Thomas J.
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CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia镰状细胞病和 β-地中海贫血的CRISPR-Cas9基因编辑
err2021-01-21
err1.1K
errOAAI
errFrangoul, H.; Altshuler, D.; Cappellini, M. D.; Chen, Y-S; Domm, J.; Eustace, B. K.; Foell, J.; de la Fuente, J.; Grupp, S.; Handgretinger, R.; Ho, T. W.; Kattamis, A.; Kernytsky, A.; Lekstrom-Himes, J.; Li, A. M.; Locatelli, F.; Mapara, M. Y.; de Montalembert, M.; Rondelli, D.; Sharma, A.; Sheth, S.; Soni, S.; Steinberg, M. H.; Wall, D.; Yen, A.; Corbacioglu, S.
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