未登录Titin-truncating variants in hiPSC cardiomyocytes induce pathogenic proteinopathy and sarcomere defects with preserved core contractile machinery
Huang, Guanyi; Bisaria, Anjali; Wakefield, Devin L.; Yamawaki, Tracy M.; Luo, Xin; Zhang, Jingli A.; Vigneault, Patrick; Wang, Jinghong; Reagan, Jeffrey D.; Oliverio, Oliver; Zhou, Hong; Li, Chi -Ming; Vila, Olaia F.; Wang, Songli; Malik, Fady I.; Hartman, James J.; Hale, Christopher M.
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收藏Induction of site-specific chromosomal translocations in embryonic stem cells by CRISPR/Cas9
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