未登录.png)
分享.png)
收藏分享 收藏 Role of Longitudinal Strain in the Evaluation of Contractile Dysfunction in Japanese Fabry Disease Patients纵向应变在评估日本法布里病患者收缩功能障碍中的作用
Nojiri, Ayumi; Morimoto, Satoshi; Fukuro, Eiko; Okuyama, Toraaki; Anan, Ikuko; Kawai, Makoto; Sakurai, Ken; Kobayashi, Masahisa; Kobayashi, Hiroshi; Ida, Hiroyuki; Ohashi, Toya; Yoshimura, Michihiro; Eto, Yoshikatsu; Hongo, Kenichi 分享 收藏 Integrated long-term efficacy and safety data on enzyme replacement therapy with pabinafusp alfa for neuronopathic mucopolysaccharidosis type II (MPS II): Updated clinical data from Japan and BrazilEto, Yoshikatsu; Giugliani, Roberto; Nakamura, Kimitoshi; Sakai, Norio; Martins, Ana Maria; Tanizawa, Kazunori; So, Sairei; Yamamoto, Tatsuyoshi; Cunegundes, Ricardo; Ikeda, Toshiaki; Moriuchi, Hiroaki; Schmidt, Mathias; Sato, Yuji 分享 收藏 分享 收藏 分享 收藏 Real-world data of enzyme replacement therapy with pabinafusp alfa for neuronopathic MPS-II: Updated clinical data from JapanEto, Yoshikatsu; Nakamura, Kimitoshi; Sakai, Norio; Tanizawa, Kazunori; So, Sairei; Yamamoto, Tatsuyoshi; Ikeda, Toshiaki; Moriuchi, Hiroaki; Sonoda, Hiroyuki; Sato, Yuji 分享 收藏 Long-term neurodevelopmental changes in subjects with MPS II following long-term treatment with pabinafusp alfa: An integrated analysis from pre- and post-approval clinical trials in Brazil and JapanGiugliani, Roberto; Eto, Yoshikatsu; Nakamura, Kimitoshi; Sakai, Norio; Martins, Ana Maria; Cunegundes, Ricardo; So, Sairei; Tanizawa, Kazunori; Yamamoto, Tatsuyoshi; Ikeda, Toshiaki; Moriuchi, Hiroaki; Sonoda, Hiroyuki; Schmidt, Mathias; Sato, Yuji 分享 收藏 Long term efficacy and safety of pabinafusp-alfa (JR-141) in Hunter syndrome (MPS-II): 104-week data from the clinical trials in Japan and BrazilGiugliani, Roberto; Martins, Ana M.; Okuyama, Torayuki; Eto, Yoshikatsu; Sakai, Norio; Nakamura, Kimitoshi; So, Sairei; Yamamoto, Tatsuyoshi; Yamaoka, Mariko; Ikeda, Toshiaki; Moriuchi, Hiroaki; Tanizawa, Kazunori; Sonoda, Hiroyuki; Schmidt, Mathias; Sato, Yuji 分享 收藏 Prevalence of patients with lysosomal storage disorders and peroxisomal disorders: A nationwide survey in JapanKoto, Yuta; Sakai, Norio; Lee, Yoko; Kakee, Naoko; Matsuda, Junko; Tsuboi, Kazuya; Shimozawa, Nobuyuki; Okuyama, Torayuki; Nakamura, Kimitoshi; Narita, Aya; Kobayashi, Hiroshi; Uehara, Ritei; Nakamura, Yoshikazu; Kato, Koji; Eto, Yoshikatsu 分享 收藏 Drug delivery across the blood-brain barrier and resultant reduction of heparan sulfate in the cerebrospinal fluid in the patients with Hunter syndrome (MPS II): An integrated analysis of 25-week Japanese and Brazilian data on pabinafusp alfa (JR-141)Okuyama, Torayuki; Eto, Yoshikatsu; Sakai, Norio; Nakamura, Kimitoshi; Giugliani, Roberto; Martins, Ana Maria; So, Sairei; Yamamoto, Tatsuyoshi; Yamaoka, Mariko; Ikeda, Toshiaki; Tanizawa, Kazunori; Sonoda, Hiroyuki; Schmidt, Mathias; Sato, Yuji 分享 收藏 A Phase 2/3 Trial of Pabinafusp Alfa, IDS Fused with Anti-Human Transferrin Receptor Antibody, Targeting Neurodegeneration in MPS-IIOkuyama, Torayuki; Eto, Yoshikatsu; Sakai, Norio; Nakamura, Kimitoshi; Yamamoto, Tatsuyoshi; Yamaoka, Mariko; Ikeda, Toshiaki; So, Sairei; Tanizawa, Kazunori; Sonoda, Hiroyuki; Sato, Yuji 分享 收藏 Exploration of the efficacy of pabinafusp-alfa (JR-141) on neurocognitive development in Hunter syndrome (MPS II): 52week data from clinical trials in Japan and BrazilGiugliani, Roberto; Martins, Ana Maria; Okuyama, Torayuki; Eto, Yoshikatsu; Sakai, Norio; Nakamura, Kimitoshi; So, Sairei; Yamamoto, Tatsuyoshi; Yamaoka, Mariko; Ikeda, Toshiaki; Tanizawa, Kazunori; Sonoda, Hiroyuki; Schmidt, Mathias; Sato, Yuji 分享 收藏 Pharmacokinetics and pharmacodynamics of JR-051, a biosimilar of agalsidase beta, in healthy adults and patients with Fabry disease: Phase I and II/III clinical studiesNakamura, Kimitoshi; Kawashima, Satoshi; Tozawa, Hirotaka; Yamaoka, Mariko; Yamamoto, Tatsuyoshi; Tanaka, Noboru; Yamamoto, Ryuji; Okuyama, Torayuki; Eto, Yoshikatsu 分享 收藏 Therapy for mucopolysaccharidosis type II with an intravenous blood-brain barrier-crossing enzyme (JR-141): 26-week results from a phase 3 study in Japan suggesting significant efficacy against central nervous system and systemic symptomsOkuyama, Torayuki; Eto, Yoshikatsu; Nakamura, Kimitoshi; Sakai, Norio; Sato, Yuji; Tanizawa, Kazunori; Yamamoto, Tatsuyoshi; So, Sairei; Yamaoka, Mariko; Kobayashi, Minako 分享 收藏 分享 收藏 An update on biomarkers of 7-ketocholesterol, lysosphingomyelin, bile acid-408 and glucosylsphingosine for Niemann-Pick disease type CWu, Chen; Iwamoto, Takeo; Hossain, Mohammad Arif; Akiyama, Keiko; Igarashi, Junko; Miyajima, Takashi; Saito, Ryo; Eto, Yoshikatsu 分享 收藏 分享 收藏 Investigation of diagnostic performance of five urinary cholesterol metabolites for Niemann-Pick disease type C[S]Maekawa, Masamitsu; Jinnoh, Isamu; Narita, Aya; Iida, Takashi; Saigusa, Daisuke; Iwahori, Anna; Nittono, Hiroshi; Okuyama, Torayuki; Eto, Yoshikatsu; Ohno, Kousaku; Clayton, Peter T.; Yamaguchi, Hiroaki; Mano, Nariyasu 分享 收藏 Diagnostic performance evaluation of sulfate-conjugated cholesterol metabolites as urinary biomarkers of Niemann-Pick disease type CMaekawa, Masamitsu; Narita, Aya; Jinnoh, Isamu; Iida, Takashi; Marquardt, Thorsten; Mengel, Eugen; Eto, Yoshikatsu; Clayton, Peter T.; Yamaguchi, Hiroaki; Mano, Nariyasu 分享 收藏 
.png){kind=icon}
.png){kind=icon}
.png){kind=icon}
.png){kind=icon}
