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收藏Gene Therapy for Spinal Muscular Atrophy: Safety and Early Outcomes
Waldrop, Megan A.; Karingada, Cassandra; Storey, Mike A.; Powers, Brenna; Iammarino, Megan A.; Miller, Natalie F.; Alfano, Lindsay N.; Noritz, Garey; Rossman, Ian; Ginsberg, Matthew; Mosher, Kathryn A.; Broomall, Eileen; Goldstein, Jessica; Bass, Nancy; Lowes, Linda P.; Tsao, Chang-Yong; Mendell, Jerry R.; Connolly, Anne M.
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