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收藏Care Utilization for Acute Respiratory Infections in Children Requiring Invasive Long-Term Mechanical Ventilation儿童需要侵入性长期机械通气时急性呼吸道感染的医疗利用
Foster, Carolyn C.; Florin, Todd A.; Williams, Derek J.; Freundlich, Katherine L.; Steuart, Rebecca L.; Heneghan, Julia A.; Cecil, Cara; Pajor, Nathan M.; Graham, Robert J.; Ramgopal, Sriram
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收藏Spinal Muscular Atrophy Update in Best Practices
Schroth, Mary K.; Deans, Jennifer; Goebel, Diana X. Bharucha; Burnette, W. Bryan; Darras, Basil T.; Elsheikh, Bakri H.; Felker, Marcia V.; Klein, Andrea; Krueger, Jena; Proud, Crystal M.; Veerapandiyan, Aravindhan; Graham, Robert J.
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收藏Characterization of swallowing biomechanics and function in untreated infants with spinal muscular atrophy: A natural history dataset未治疗的脊髓性肌萎缩症婴儿的吞咽生物力学与功能特征:一项自然病史数据集
McGrattan, Katlyn Elizabeth; Graham, Robert J.; Mohr, Alicia Hofelich; Miles, Anna; Allen, Jacqui; Ochura, Juliet; Hernandez, Kayla; Walsh, Katie; Rao, Vamshi; Stevens, Melanie; Alfano, Lindsay; Coker, Mackenzi; Leon-Astudillo, Carmen; Smith, Leann Schow; Brandsema, John; Farah, Hiba; Welc, Julia; Levy, Deborah Salle; Clements, Miranda; Tang, Whitney J.; Rocha, Carolina Tesi; Schenck, Graham; Mcghee, Heather; Nichols, Keeley; Brown, Ashley; Brown, Allison; Castro, Diana; Darras, Basil T.
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收藏Achieving Enteral Autonomy in Children with Intestinal Failure Following Inpatient Admission: A Case Series
Fialkowski, Allison; Broyles, Kathryn; Depaula, Brittany; Flores, Alejandro; Gray, Megan; Graham, Robert J.; Hoch, Rachel; Hope, Kayla E.; Mcgivney, Megan; Mcclelland, Jennifer; Nurko, Samuel; Puder, Mark; Stamm, Danielle; Duggan, Christopher P.; Carey, Alexandra
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收藏Categorization of a Universal Coding System to Distinguish Use of Durable Medical Equipment and Supplies in Pediatric Patients
Hotz, Arda; Sprecher, Eli; Bastianelli, Lucia; Rodean, Jonathan; Stringfellow, Isabel; Barkoudah, Elizabeth; Cohen, Laurie E.; Estrada, Carlos; Graham, Robert; Greenwood, Jonathan; Kyle, Jennifer; Mann, Nina; Pinkham, Maria; Solari, Toni; Rosen, Rachel; Saleeb, Susan; Shah, Ankoor S.; Watters, Karen; Wells, Sarah; Berry, Jay G.
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收藏INCEPTUS Natural History, Run-in Study for Gene Replacement Clinical Trial in X-Linked Myotubular Myopathy
Dowling, James J.; Mueller-Felber, Wolfgang; Smith, Barbara K.; Bonnemann, Carsten G.; Kuntz, Nancy L.; Muntoni, Francesco; Servais, Laurent; Alfano, Lindsay N.; Beggs, Alan H.; Bilder, Deborah A.; Blaschek, Astrid; Duong, Tina; Graham, Robert J.; Jain, Minal; Lawlor, Michael W.; Lee, Jun; Coats, Julie; Lilien, Charlotte; Lowes, Linda P.; MacBean, Victoria; Neuhaus, Sarah; Noursalehi, Mojtaba; Pitts, Teresa; Finlay, Caroline; Christensen, Sarah; Rafferty, Gerrard; Seferian, Andreea M.; Tsuchiya, Etsuko; James, Emma S.; Miller, Weston; Sepulveda, Bryan; Vila, Maria Candida; Prasad, Suyash; Rico, Salvador; Shieh, Perry B.
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收藏Nusinersen for Patients With Spinal Muscular Atrophy: 1415 Doses via an Interdisciplinary Institutional ApproachNusinersen用于脊髓性肌萎缩症患者: 通过跨学科机构方法1415剂量
Madan, Elena; Carri, Sabrina; Donado, Carolina; Lobo, Kimberly; Souris, Michelle; Laine, Regina; Beers, Elizabeth; Cornelissen, Laura; Darras, Basil T.; Koka, Anjali; Riley, Bobbie; Dinakar, Pradeep; Stone, Scellig; Snyder, Brian; Graham, Robert J.; Padua, Horacio; Sethna, Navil; Berde, Charles
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收藏Intrahepatic Cholestasis Is a Clinically Significant Feature Associated with Natural History of X-Linked Myotubular Myopathy (XLMTM): A Case Series and Biopsy Report
Molera, Cristina; Sarishvili, Tinatin; Nascimento, Andres; Rtskhiladze, Irakli; Munoz Bartolo, Gema; Fernandez Cebrian, Santiago; Valverde Fernandez, Justo; Munoz Cabello, Beatriz; Graham, Robert J.; Miller, Weston; Sepulveda, Bryan; Kamath, Binita M.; Meng, Hui; Lawlor, Michael W.
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收藏Tracing the affordances of long-acting injectable depot buprenorphine: A qualitative study of patients' experiences in Australia
Barnett, Anthony; Savic, Michael; Lintzeris, Nicholas; Bathish, Ramez; Arunogiri, Shalini; Dunlop, Adrian J.; Haber, Paul; Graham, Robert; Hayes, Vicky; Lubman, Dan, I
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