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Targetable somatostatin receptor expression assessed by DOTATATE PET imaging in children and young adults with recurrent/progressive high-risk central nervous system (CNS) tumors: Initial screening results from the CONNECT2007 Lutathera Phase I/II trial 在复发/进展性高风险中枢神经系统(CNS)肿瘤的儿童和年轻患者中,通过DOTATATE PET成像评估的可靶向生长抑素受体表达:来自CONNECT2007 Lutathera I/II期试验的初步筛查结果 Lazow, Margot; Bobbey, Adam; Szabo, Sara; Fuller, Christine; White, William; McNeely, David; Gibson, Laurie; Brady, Samuel; Palmer, Joshua; Mardis, Elaine; De Blank, Peter; Rodriguez, Diana; Brandt, Cierra; Khan, Sara; Tanaka, Ryuma; Drabick, Cassidy; Henke, Katie; Harr, Anna; Troyer, Kelsey; Fouladi, Maryam; Salloum, Ralph; Trout, Andrew 分享 收藏
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MOLECULAR AND BIOLOGY CORRELATIVE RESULTS FROM THE PHASE 1B TRIAL OF UNESBULIN (PTC596) WITH RADIOTHERAPY IN CHILDREN NEWLY-DIAGNOSED WITH DIFFUSE INTRINSIC PONTINE GLIOMA (DIPG) AND HIGH-GRADE GLIOMA (HGG): A REPORT FROM THE COLLABORATIVE NETWORK FOR NEURO-ONCOLOGY CLINICAL TRIALS (CONNECT) Lazow, Margot; Baxter, Patricia; Kumar, Shiva Senthil; Mohamad, Maya; Mackay, Alan; Stanek, Joseph; Rodriguez, Diana; Palmer, Joshua; Leach, James; Mikael, Leonie; Thomas, Diana; Fuller, Christine; Boue, Daniel; Pierson, Christopher; Breneman, John; Li, Xiao-Nan; Salloum, Ralph; Ashley, David; de Blank, Peter; Hwang, Eugene; Leary, Sarah; Plant, Ashley; Fisher, Michael; Chi, Susan; Murala, Mythili; Weetall, Marla; Rance, Mark; Baird, John; D'Silva, Dhiren; O'Keefe, Kylie; Leonard, Jeffrey; Stewart, Clinton; Jones, Chris; Mardis, Elaine; Fouladi, Maryam; Drissi, Rachid 分享 收藏
Cardiac Dysfunction in Children and Young Adults Treated With MEK Inhibitors A Retrospective, Single-Center Study Bender, Jonathan D.; Pillay-Smiley, Natasha; Hill, Garick D.; de Blank, Peter; Hummel, Trent R.; Weiss, Brian D.; Kumar, Ashish; Zang, Huaiyu; Ollberding, Nicholas J.; Ryan, Thomas D. 分享 收藏
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DYSREGULATED PURINE METABOLISM IN A LETHAL CHILDHOOD BRAINSTEM TUMOR REVEALS NEW TREATMENT STRATEGIES WITH OLD DRUGS Mersich, Ian; Congrove, Sunny; Horchar, Matthew; Caceres, Roman; Desai, Janki; Desai, Pankaj; Sallans, Larry; Haines, Julie; Menon, Ranjith; Stevenson, Charles; de Blank, Peter; Pillay-Smiley, Natasha; Hummel, Trent; Tavassoli, Ali; D'Alessandro, Angelo; Phoenix, Timothy; Dasgupta, Biplab 分享 收藏
DEMOGRAPHIC, CLINICAL AND IMAGING CHARACTERISTICS OF NEWLY DIAGNOSED OPTIC PATHWAY GLIOMAS ASSOCIATED WITH NF1: RESULTS FROM THE INTERNATIONAL MULTICENTER NF1-OPG NATURAL HISTORY STUDY Fisher, Michael J.; de Blank, Peter; Listernick, Robert; Liu, Grant; Ferner, Rosalie; Gutmann, David; Lasky-Zeid, Janice; Ullrich, Nicole; Heidary, Gena; Bornhorst, Miriam; Stasheff, Steven; Rosser, Teena; Borcher, March; Arden-Holmes, Simone; Flaherty, Maree; Hummel, Trent; Motley, Walker; Bielamowicz, Kevin; Phillips, Paul; Bouffet, Eric; Reginald, Arun; Wolf, David; Peragallo, Jason; El-Dairi, Mays; Van Mater, David; Sato, Aimee; Tarczy-Hornoch, Kristina; Klesse, Laura; Hogan, Nick; Foreman, Nicholas; Mccourt, Emily; Allen, Jeffrey; Ranka, Milan; Campen, Cynthia; Beres, Shannon; Moertel, Christopher; Areaux, Ray; Stearns, Duncan; Orge, Faruk; Crawford, John; O'Halloran, Henry; Oattes, Julius; Reddy, Alyssa; Brodsky, Michael; Esbenshade, Adam; Donahue, Sean; Cutter, Gary; Avery, Robert 分享 收藏
TUMOR VOLUME IN NEWLY DIAGNOSED OPTIC PATHWAY GLIOMAS ASSOCIATED WITH NF1 (NF1-OPG): PRELIMINARY RESULTS FROM THE INTERNATIONAL MULTICENTER NF1-OPG NATURAL HISTORY STUDY Avery, Robert; Jiang, Zhifan; Parida, Abhijeet; Listernick, Robert; Liu, Grant; Ferner, Rosalie; Gutmann, David; de Blank, Peter; Lasky-Zeid, Janice; Ullrich, Nicole; Heidary, Gena; Bornhorst, Miriam; Stasheff, Steven; Rosser, Teena; Borchert, Mark; Arden-Holmes, Simone; Flaherty, Maree; Hummel, Trent; Motley, Walker; Bielamowicz, Kevin; Phillips, Paul; Bouffet, Eric; Reginald, Arun; Wolf, David; Peragallo, Jason; Van Mater, David; El-Diari, Mays; Sato, Aimee; Tarczy-Hornoch, Kristina; Klesse, Laura; Hogan, Nick; Foreman, Nicholas; Mccourt, Emily; Allen, Jeffrey; Ranka, Milan; Campen, Cynthia; Beres, Shannon; Moertel, Christopher; Areaux, Ray; Stearns, Duncan; Orge, Faruk; Crawford, John; O'Halloran, Henry; Brodsky, Michael; Esbenshade, Adam; Donahue, Sean; Oattes, Julius; Reddy, Alyssa; Cutter, Gary; Linguraru, Marius; Fisher, Michael 分享 收藏
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CONNECT1903: A PILOT AND SURGICAL STUDY OF LAROTRECTINIB FOR TREATMENT OF CHILDREN WITH NEWLY DIAGNOSED HGG WITH NTRK FUSION (NCT04655404) Chi, Susan N.; Lazow, Margot; Salloum, Ralph; Lane, Adam; Hargrave, Darren; Witt, Olaf; de Blank, Peter; Leary, Sarah E. S.; Gorsi, Hamza; Pierson, Christopher; Breneman, John; Jones, Jeremy; Yang, Edward; Mikael, Leonie; Jones, David T. W.; Fouladi, Maryam 分享 收藏
Resistance, rebound, and recurrence regrowth patterns in pediatric low-grade glioma treated by MAPK inhibition: A modified Delphi approach to build international consensus-based definitions-International Pediatric Low-Grade Glioma Coalition 通过MAPK抑制治疗的小儿低级别神经胶质瘤的抗性,反弹和复发再生模式: 建立基于国际共识的定义的改良Delphi方法-国际小儿低级别神经胶质瘤联盟 O'Hare, Patricia; Cooney, Tabitha; de Blank, Peter; Gutmann, David H.; Kieran, Mark; Milde, Till; Fangusaro, Jason; Fisher, Michael; Avula, Shivaram; Packer, Roger; Fukuoka, Kohei; Mankad, Kshitij; Mueller, Sabine; Waanders, Angela J.; Opocher, Enrico; Bouffet, Eric; Raabe, Eric; Werle, Natacha Entz; Azizi, Amedeo A.; Robison, Nathan J.; Driever, Pablo Hernaiz; Russo, Mark; Schouten, Netteke; van Tilburg, Cornelis M.; Sehested, Astrid; Grill, Jacques; Bandopadhayay, Pratiti; Kilday, John-Paul; Witt, Olaf; Ashley, David M.; Ertl-Wagner, Birgit Betina; Tabori, Uri; Hargrave, Darren R. 分享 收藏
Safety and pharmacokinetics of ONC201 (dordaviprone) administered two consecutive days per week in pediatric patients with H3 K27M-mutant glioma Odia, Yazmin; Koschmann, Carl; Vitanza, Nicholas A.; de Blank, Peter; Aguilera, Dolly; Allen, Jeffrey; Daghistani, Doured; Hall, Matthew; Khatib, Ziad; Kline, Cassie; Macdonald, Tobey; Mueller, Sabine; Faison, Shamia L.; Allen, Joshua E.; Naderer, Odin J.; Ramage, Samuel C.; Tarapore, Rohinton S.; Mcgovern, Susan Lynne; Khatua, Soumen; Zaky, Wafik; Gardner, Sharon L. 分享 收藏
Consensus framework for conducting phase I/II clinical trials for children, adolescents, and young adults with pediatric low-grade glioma: Guidelines established by the International Pediatric Low-Grade Glioma Coalition Clinical Trial Working Group 开展儿童、青少年和年轻成人低级别胶质瘤I/II期临床试验的共识框架: 国际儿童低级别胶质瘤联盟临床试验工作组制定的指南 Mueller, Sabine; Fangusaro, Jason; Thomas, Arzu Onar; Jacques, Thomas S.; Bandopadhayay, Pratiti; de Blank, Peter; Packer, Roger J.; Fouladi, Maryam; van Meeteren, Antoinette Schouten; Jones, David; Perry, Arie; Nakano, Yoshiko; Hargrave, Darren; Riedl, David; Robinson, Nathan J.; Partanen, Marita; Fisher, Michael J.; Witt, Olaf 分享 收藏
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UPDATED FINDINGS FROM THE PHASE IB STUDY OF UNESBULIN (PTC596) IN CHILDREN WITH NEWLY-DIAGNOSED DIFFUSE INTRINSIC PONTINE GLIOMA (DIPG) AND HIGH-GRADE GLIOMA (HGG): A REPORT FROM THE COLLABORATIVE NETWORK FOR NEURO-ONCOLOGY CLINICAL TRIALS (CONNECT) 新诊断的弥漫性内在性脑桥胶质瘤 (DIPG) 和高级别胶质瘤 (HGG) 儿童UNESBULIN (PTC596) IB期研究的最新发现: 来自神经肿瘤学临床试验合作网络 (CONNECT) 的报告 Lazow, Margot; Baxter, Patricia; Stanek, Joseph; Rodriguez, Diana; Kumar, Shiva Senthil; Palmer, Joshua; Leach, James; Mikael, Leonie; Thomas, Diana; Fuller, Christine; Boue, Daniel; Pierson, Christopher; Breneman, John; Li, Xiao-Nan; Salloum, Ralph; Ashley, David; De Blank, Peter; Hwang, Eugene; Leary, Sarah; Plant, Ashley; Fisher, Michael; Chi, Susan; Crabtree, Dorothy; Murali, Mythili; Weetall, Marla; Rance, Mark; Maliakal, Pius; Baird, John; D'Silva, Dhiren; O'Keefe, Kylie; Leonard, Jeffrey; Stewart, Clinton; Mardis, Elaine; Fouladi, Maryam; Drissi, Rachid 分享 收藏