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Inhibitor development upon switching from plasma-derived to recombinant factor VIII in previously untreated patients with severe hemophilia A: the PUP-SWITCH study 既往未接受治疗的重度A型血友病患者从血浆来源凝血因子VIII转换为重组凝血因子VIII时抑制物的产生:PUP-SWITCH研究 Miri, Syna; Rosendaal, Frits R.; Kavakli, Kaan; Eshghi, Peyman; Moghaddam, Soha Mohammadi; Scardo, Sara; Habibpanah, Behnaz; Elalfy, Mohsen; Halimeh, Susan; Nicolo, Gabriella; Gokcebay, Dilek; Ozbek, Namik; Celkan, Tiraje; Mohammadi, Ahmad; Karimi, Mehran; Shahsavani, Amin; Yilmaz, Baris; Albayrak, Canan; Gunes, Burcak; Kaya, Zuehre; Ay, Yilmaz; Akbayram, Sinan; Sarper, Nazan; Mannucci, Pier Mannuccio; Peyvandi, Flora 分享 收藏
Retrospective analysis of hemophilia B in Turkey: identifying main characteristics and treatment options Zulfikar, Bulent; Koc, Basak; Sahin, Fahri; Sasmaz, Hatice Ilgen; Kavakli, Kaan; Balkan, Can; Antmen, Ali Buelent; Akbayram, Sinan; Guvenc, Birol; Okan, Vahap; Turkkan, Emine; Albayrak, Canan; Albayrak, Davut; Sarper, Nazan; Celkan, Tuelin Tiraje; Ayyildiz, Orhan; Aksu, Salih; Patiroglu, Tuerkan; Salcioglu, Zafer; Gunes, Adalet Meral; Torun, Yasemin Altuner; Caliskan, Umran; Tokgoz, Huseyin; Ay, Yilmaz; Ozdemir, Gul Nihal; Sonmez, Mehmet; Unal, Ekrem; Oner, Ahmet Fayik; Guler, Nil; Kupesiz, Osman Alphan; Oren, Hale; Karaman, Serap; Unuvar, Ayegul; Dagli, Mehmet; Demir, Ahmet Muzaffer; Soker, Murat; Alioglu, Buelent; Kaya, Zuehre; Ayhan, Aylin Canbolat; Bicakci, Zafer; Aral, Yusuf Ziya; Ar, Muhlis Cem 分享 收藏
Sirolimus is effective and safe in childhood relapsed-refractory autoimmune cytopenias: A multicentre study Acar, Sultan Okur; Tahta, Neryal; Al, Isik Odaman; Erdem, Melek; Gozmen, Salih; Karapinar, Tuba Hilkay; Kilinc, Burcu; Celkan, Tiraje; Kirkiz, Serap; Kocak, Ulker; Oren, Hale; Yildirim, Aysen Turedi; Arslantas, Esra; Ayhan, Aylin Canbolat; Oymak, Yesim 分享 收藏
Gain-of-function IKZF1 variants in humans cause immune dysregulation associated with abnormal T/B cell late differentiation 人类的功能获得IKZF1变体导致与异常T/b细胞晚期分化相关的免疫失调 Hoshino, Akihiro; Boutboul, David; Zhang, Yuan; Kuehn, Hye Sun; Hadjadj, Jerome; Ozdemir, Nihal; Celkan, Tiraje; Walz, Christoph; Picard, Capucine; Lenoir, Christelle; Mahlaoui, Nizar; Klein, Christoph; Peng, Xiao; Azar, Antoine; Reigh, Erin; Cheminant, Morgane; Fischer, Alain; Rieux-Laucat, Frederic; Callebaut, Isabelle; Hauck, Fabian; Milner, Joshua; Rosenzweig, Sergio D.; Latour, Sylvain 分享 收藏
Adverse COVID-19 outcomes in immune deficiencies: Inequality exists between subclasses Aydiner, Elif Karakoc; Eltan, Sevgi Bilgic; Babayeva, Royale; Aydiner, Omer; Kepenekli, Eda; Kolukisa, Burcu; Sefer, Asena Pinar; Gungoren, Ezgi Yalcin; Karabiber, Esra; Yucel, Esra Ozek; Ozdemir, Oner; Kiykim, Ayca; Artac, Hasibe; Yakici, Nalan; Yalcin, Koray; Cokugras, Haluk; Celkan, Tulin Tiraje; Orhan, Fazil; Yesilipek, Mehmet Akif; Baris, Safa; Ozen, Ahmet 分享 收藏
Evolution and long-term outcomes of combined immunodeficiency due to CARMIL2 deficiency CARMIL2缺陷引起的联合免疫缺陷的演变和长期结果 Kolukisa, Burcu; Baser, Dilek; Akcam, Bengu; Danielson, Jeffrey; Eltan, Sevgi Bilgic; Haliloglu, Yesim; Sefer, Asena Pinar; Babayeva, Royale; Akgun, Gamze; Charbonnier, Louis-Marie; Schmitz-Abe, Klaus; Demirkol, Yasemin Kendir; Zhang, Yu; Gonzaga-Jauregui, Claudia; Heredia, Raul Jimenez; Kasap, Nurhan; Kiykim, Ayca; Yucel, Esra Ozek; Gok, Veysel; Unal, Ekrem; Kisaarslan, Aysenur Pac; Nepesov, Serdar; Baysoy, Gokhan; Onal, Zerrin; Yesil, Gozde; Celkan, Tulin Tiraje; Cokugras, Haluk; Camcioglu, Yildiz; Eken, Ahmet; Boztug, Kaan; Lo, Bernice; Karakoc-Aydiner, Elif; Su, Helen C.; Ozen, Ahmet; Chatila, Talal A.; Baris, Safa 分享 收藏
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Deregulated WNT signaling in childhood T-cell acute lymphoblastic leukemia Ng, O. H.; Erbilgin, Y.; Firtina, S.; Celkan, T.; Karakas, Z.; Aydogan, G.; Turkkan, E.; Yildirmak, Y.; Timur, C.; Zengin, E.; van Dongen, J. J. M.; Staal, F. J. T.; Ozbek, U.; Sayitoglu, M. 分享 收藏
Coagulation factor activity and clinical bleeding severity in rare bleeding disorders: results from the European Network of Rare Bleeding Disorders Peyvandi, F.; Palla, R.; Menegatti, M.; Siboni, S. M.; Halimeh, S.; Faeser, B.; Pergantou, H.; Platokouki, H.; Giangrande, P.; Peerlinck, K.; Celkan, T.; Ozdemir, N.; Bidlingmaier, C.; Ingerslev, J.; Giansily-Blaizot, M.; Schved, J. F.; Gilmore, R.; Gadisseur, A.; Benedik-Dolnicar, M.; Kitanovski, L.; Mikovic, D.; Musallam, K. M.; Rosendaal, F. R. 分享 收藏
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Sequencing of the factor 8(F8) coding regions in 10 Turkish hemophilia A patients reveals three novel pathological mutations, and one rediagnosis of von Willebrand's disease type 2N Berber, E.; Fidanci, I. D.; Un, C.; El-Maarri, O.; Aktuglu, G.; Gurgey, A.; Celkan, T.; Meral, A.; Oldenburg, J.; Graw, J.; Akar, N.; Caglayan, H. 分享 收藏
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