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Elevated Serum Bile Acids Predict Poor Liver Outcomes in Children With Alagille Syndrome: Results From the GALA Study Group 血清胆汁酸升高可预测Alagille综合征患儿的肝脏不良结局:GALA研究小组的结果 Perez, Carla Fiorella Murillo; Vandriel, Shannon M.; Gonzales, Emmanuel M.; Wang, Jian- She; Li, Li- Ting; She, Huiyu; Jankowska, Irena; Czubkowski, Piotr; Gliwicz-miedzinska, Dorota; Jacquemin, Emmanuel; Bouligand, Jerome; D'antiga, Lorenzo; Nicastro, Emanuele; Fischler, Bjorn; Arnell, Henrik; Siew, Susan M.; Stormon, Michael; Loomes, Kathleen M.; Piccoli, David A.; Rand, Elizabeth B.; Squires, James E.; Karpen, Saul J.; Romero, Rene; Kasahara, Mureo; Onal, Zerrin; Sokal, Etienne; Demaret, Tanguy; Wiecek, Sabina; Lacaille, Florence; Debray, Dominique; Hardikar, Winita; Shankar, Sahana; Valentino, Pamela L.; Sundaram, Shikha S.; Ebel, Noelle H.; Feinstein, Jeffrey A.; Waisbourd-zinman, Orith; Lin, Henry C.; Rock, Nathalie; Verkade, Henkjan J.; Jensen, M. Kyle; Jaramillo, Catalina; Kim, Kyung Mo; Oh, Seak Hee; Brecemiclj, Jernej; Alam, Seema; Indolfi, Giuseppe; Blondet, Niviann; Fawaz, Rima; Nastasio, Silvia; Calvo, Pier Luigi; Nebbia, Gabriella; Arikan, Cigdem; Larson-nath, Catherine; Zizzo, Andreanne N.; Sandahl, Thomas Damgaard; Tzivinikos, Christos; El-koofy, Nehal M.; Elmonem, Mohamed A.; Aqul, Amal A.; Karnsakul, Wikrom; Bulut, Pinar; Kerkar, Nanda; Wolters, Victorien M.; Roberts, Amin J.; Evans, Helen M.; Sanchez, Maria Camila; Cavalieri, Maria Lorena; Kelly, Deirdre A.; Hartley, Jane; Lee, Way Seah; Hajinicolaou, Christina; Lertudomphonwanit, Chatmanee; Fischer, Ryan T.; Bernabeu, Jesus Quintero; Quiros-Tejeira, Ruben E.; Ferreira, Cristina Targa; Carvalho, Elisa; Eshun, John; Zellos, Aglaia; Dezsofi, Antal; Pinto, Raquel Borges; Schwarz, Kathleen; Rogalidou, Maria; Garcia, Jennifer; Tamara, Maria Legarda; Beretta, Marisa; Mujawar, Quais; Santos-Silva, Ermelinda; Busoms, Cristina Molera; Lurz, Eberhard; Goncalves, Cristina; Jimenez-Rivera, Carolina; Banales, Jesus M.; Thompson, Richard J.; Hansen, Bettina E.; Kamath, Binita M. 分享 收藏
Event-free survival of maralixibat-treated patients with Alagille syndrome compared to a real-world cohort from GALA Hansen, Bettina E.; Vandriel, Shannon M.; Vig, Pamela; Garner, Will; Mogul, Douglas B.; Loomes, Kathleen M.; Piccoli, David A.; Rand, Elizabeth B.; Jankowska, Irena; Czubkowski, Piotr; Gliwicz-Miedzinska, Dorota; Gonzales, Emmanuel M.; Jacquemin, Emmanuel; Bouligand, Jerome; D'Antiga, Lorenzo; Nicastro, Emanuele; Arnell, Henrik; Fischler, Bjorn; Sokal, Etienne; Demaret, Tanguy; Siew, Susan; Stormon, Michael; Karpen, Saul J.; Romero, Rene; Ebel, Noelle H.; Feinstein, Jeffrey A.; Roberts, Amin J.; Evans, Helen M.; Sundaram, Shikha S.; Chaidez, Alexander; Hardikar, Winita; Shankar, Sahana; Fischer, Ryan T.; Lacaille, Florence; Debray, Dominique; Lin, Henry C.; Jensen, M. Kyle; Jaramillo, Catalina; Karthikeyan, Palaniswamy; Indolfi, Giuseppe; Verkade, Henkjan J.; Larson-Nath, Catherine; Quiros-Tejeira, Ruben E.; Valentino, Pamela L.; Rogalidou, Maria; Dezsofi, Antal; Squires, James E.; Schwarz, Kathleen; Calvo, Pier Luigi; Bernabeu, Jesus Quintero; Zizzo, Andreanne N.; Nebbia, Gabriella; Bulut, Pinar; Santos-Silva, Ermelinda; Fawaz, Rima; Nastasio, Silvia; Karnsakul, Wikrom; Tamara, Maria Legarda; Busoms, Cristina Molera; Kelly, Deirdre A.; Sandahl, Thomas Damgaard; Jimenez-Rivera, Carolina; Banales, Jesus M.; Mujawar, Quais; Li, Li-Ting; She, Huiyu; Wang, Jian-She; Kim, Kyung Mo; Oh, Seak Hee; Sanchez, Maria Camila; Cavalieri, Maria Lorena; Lee, Way Seah; Hajinicolaou, Christina; Lertudomphonwanit, Chatmanee; Waisbourd-Zinman, Orith; Arikan, Cigdem; Alam, Seema; Carvalho, Elisa; Melere, Melina; Eshun, John; Onal, Zerrin; Desai, Dev M.; Wiecek, Sabina; Pinto, Raquel Borges; Wolters, Victorien M.; Garcia, Jennifer; Beretta, Marisa; Kerkar, Nanda; Brecelj, Jernej; Rock, Nathalie; Lurz, Eberhard; Blondet, Niviann; Shah, Uzma; Thompson, Richard J.; Kamath, Binita M. 分享 收藏
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Pulmonary Hypertension in Children with Down Syndrome: Results from the Pediatric Pulmonary Hypertension Network Registry Hopper, Rachel K.; Abman, Steven H.; Elia, Eleni G.; Avitabile, Catherine M.; Yung, Delphine; Mullen, Mary P.; Austin, Eric D.; Bates, Angela; Handler, Stephanie S.; Feinstein, Jeffrey A.; Ivy, D. Dunbar; Kinsella, John P.; Mandl, Kenneth D.; Raj, J. Usha; Sleeper, Lynn A. 分享 收藏
Natural history of liver disease in a large international cohort of children with Alagille syndrome: Results from the GALA study Vandriel, Shannon M.; Li, Li-Ting; She, Huiyu; Wang, Jian-She; Gilbert, Melissa A.; Jankowska, Irena; Czubkowski, Piotr; Gliwicz-Miedzinska, Dorota; Gonzales, Emmanuel M.; Jacquemin, Emmanuel; Bouligand, Jerome; Spinner, Nancy B.; Loomes, Kathleen M.; Piccoli, David A.; D'Antiga, Lorenzo; Nicastro, Emanuele; Sokal, Etienne; Demaret, Tanguy; Ebel, Noelle H.; Feinstein, Jeffrey A.; Fawaz, Rima; Nastasio, Silvia; Lacaille, Florence; Debray, Dominique; Arnell, Henrik; Fischler, Bjorn; Siew, Susan; Stormon, Michael; Karpen, Saul J.; Romero, Rene; Kim, Kyung Mo; Baek, Woo Yim; Hardikar, Winita; Shankar, Sahana; Roberts, Amin J.; Evans, Helen M.; Jensen, M. Kyle; Kavan, Marianne; Sundaram, Shikha S.; Chaidez, Alexander; Karthikeyan, Palaniswamy; Sanchez, Maria Camila; Cavalieri, Maria Lorena; Verkade, Henkjan J.; Lee, Way Seah; Squires, James E.; Hajinicolaou, Christina; Lertudomphonwanit, Chatmanee; Fischer, Ryan T.; Larson-Nath, Catherine; Mozer-Glassberg, Yael; Arikan, Cigdem; Lin, Henry C.; Bernabeu, Jesus Quintero; Alam, Seema; Kelly, Deirdre A.; Carvalho, Elisa; Ferreira, Cristina Targa; Indolfi, Giuseppe; Quiros-Tejeira, Ruben E.; Bulut, Pinar; Calvo, Pier Luigi; Onal, Zerrin; Valentino, Pamela L.; Desai, Dev M.; Eshun, John; Rogalidou, Maria; Dezsofi, Antal; Wiecek, Sabina; Nebbia, Gabriella; Pinto, Raquel Borges; Wolters, Victorien M.; Tamara, Maria Legarda; Zizzo, Andreanne N.; Garcia, Jennifer; Schwarz, Kathleen; Beretta, Marisa; Sandahl, Thomas Damgaard; Jimenez-Rivera, Carolina; Kerkar, Nanda; Brecelj, Jernej; Mujawar, Quais; Rock, Nathalie; Busoms, Cristina Molera; Karnsakul, Wikrom; Lurz, Eberhard; Santos-Silva, Ermelinda; Blondet, Niviann; Bujanda, Luis; Shah, Uzma; Thompson, Richard J.; Hansen, Bettina E.; Kamath, Binita M. 分享 收藏
ISHLT consensus statement: Perioperative management of patients with pulmonary hypertension and right heart failure undergoing surgery McGlothlin, Dana P.; Granton, John; Klepetko, Walter; Beghetti, Maurice; Rosenzweig, Erika B.; Corris, Paul A.; Horn, Evelyn; Kanwar, Manreet K.; Mcrae, Karen; Roman, Antonio; Tedford, Ryan; Badagliacca, Roberto; Bartolome, Sonja; Benza, Raymond; Caccamo, Marco; Cogswell, Rebecca; Dewachter, Celine; Donahoe, Laura; Fadel, Elie; Farber, Harrison W.; Feinstein, Jeffrey; Franco, Veronica; Frantz, Robert; Gatzoulis, Michael; Goh, Choon Hwa (Anne); Guazzi, Marco; Hansmann, Georg; Hastings, Stuart; Heerdt, Paul M.; Hemnes, Anna; Herpain, Antoine; Hsu, Chih-Hsin; Kerr, Kim; Kolaitis, Nicholas A.; Kukreja, Jasleen; Madani, Michael; McCluskey, Stuart; McCulloch, Michael; Moser, Bernhard; Navaratnam, Manchula; Radegran, Goran; Reimer, Cara; Savale, Laurent; Shlobin, Oksana A.; Svetlichnaya, Jana; Swetz, Keith; Tashjian, Jessica; Thenappan, Thenappan; Vizza, Carmine Dario; West, Shawn; Zuckerman, Warren; Zuckermann, Andreas; De Marco, Teresa 分享 收藏
Dissecting alveolar patterning and maintenance at single-cell resolution Gillich, Astrid; Brownfield, Douglas G.; Travaglini, Kyle J.; Zhang, Fan; Farmer, Collen G.; St. Julien, Krystal R.; Tan, Serena Y.; Gu, Mingxia; Zhou, Bin; Feinstein, Jeffrey A.; Metzger, Ross J.; Krasnow, Mark A. 分享 收藏
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4D flow cardiovascular magnetic resonance recovery profiles following pulmonary endarterectomy in chronic thromboembolic pulmonary hypertension Dong, Melody L.; Azarine, Arshid; Haddad, Francois; Amsallem, Myriam; Kim, Young-Wouk; Yang, Weiguang; Fadel, Elie; Aubrege, Laure; Loecher, Michael; Ennis, Daniel; Pavec, Jerome Le; Vignon-Clementel, Irene; Feinstein, Jeffrey A.; Mercier, Olaf; Marsden, Alison L. 分享 收藏
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Outcomes in Patients with Alagille Syndrome and Complex Pulmonary Artery Disease Luong, Roger; Feinstein, Jeffrey A.; Ma, Michael; Ebel, Noelle H.; Wise-Faberowski, Lisa; Zhang, Yulin; Peng, Lynn F.; Yarlagadda, Vamsi V.; Shek, Jennifer; Hanley, Frank L.; McElhinney, Doff B. 分享 收藏
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Racial and Ethnic Differences in Pediatric Pulmonary Hypertension: An Analysis of the Pediatric Pulmonary Hypertension Network Registry Ong, Mei-Sing; Abman, Steve; Austin, Eric D.; Feinstein, Jeffrey A.; Hopper, Rachel K.; Krishnan, Usha S.; Mullen, Mary P.; Natter, Marc D.; Raj, J. Usha; Rosenzweig, Erika B.; Mandl, Kenneth D. 分享 收藏
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