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收藏Efficacy and safety of recombinant von Willebrand factor in on-demand treatment of children with von Willebrand disease: up to 4 years of phase 3/3b follow-up重组血管性血友病因子在血管性血友病患者儿童按需治疗中的有效性和安全性:长达4年的III/IIIb期随访
Bergmann, Shayla; Ahuja, Sanjay; Albayrak, Canan; Cnossen, Marjon H.; Dunn, Amy L.; Labarque, Veerle; Luciani, Matteo; Male, Christoph; Mullins, Eric S.; Susen, Sophie; Vera, Pascual Marco; Mokdad, Ali G.; Wang, Yi; Weng, Josh; Zhang, Jingmei
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收藏Genetic and clinical characterization of factor VII deficiency: insights from 34 Turkish patients因子Ⅶ缺乏症的遗传与临床特征:来自34例土耳其患者的见解
Atik, Tahir; Durmus Ozen, Basak; Isik, Esra; Avci Durmusalioglu, Enise; Sarper, Nazan; Albayrak, Canan; Kupesiz, Alphan; Sezgin Evim, Melike; Azizoglu, Mehmet; Albayrak, Davut; Kupesiz, Funda Tayfun; Tuysuz Kintrup, Gulen; Unal, Ekrem; Ozcan, Alper; Kavakli, Kaan; Ozkinay, Ferda
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收藏Inhibitor development upon switching from plasma-derived to recombinant factor VIII in previously untreated patients with severe hemophilia A: the PUP-SWITCH study既往未接受治疗的重度A型血友病患者从血浆来源凝血因子VIII转换为重组凝血因子VIII时抑制物的产生:PUP-SWITCH研究
Miri, Syna; Rosendaal, Frits R.; Kavakli, Kaan; Eshghi, Peyman; Moghaddam, Soha Mohammadi; Scardo, Sara; Habibpanah, Behnaz; Elalfy, Mohsen; Halimeh, Susan; Nicolo, Gabriella; Gokcebay, Dilek; Ozbek, Namik; Celkan, Tiraje; Mohammadi, Ahmad; Karimi, Mehran; Shahsavani, Amin; Yilmaz, Baris; Albayrak, Canan; Gunes, Burcak; Kaya, Zuehre; Ay, Yilmaz; Akbayram, Sinan; Sarper, Nazan; Mannucci, Pier Mannuccio; Peyvandi, Flora
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收藏Risk factors for neurologic sequelae in children and adolescents with hemophilia after intracranial hemorrhage儿童青少年血友病颅内出血后神经系统后遗症的危险因素分析
Evim, Melike Sezgin; Unuvar, Aysegul; Albayrak, Canan; Zengin, Emine; Yilmaz, Ebru; Kaya, Zuhre; Karadas, Nihal; Ertekin, Mehtap; Uzel, Hulya; Ozdemir, Gul Nihal; Albayrak, Davut; Kupesiz, Funda Tayfun; Bahadir, Aysenur; Tokgoz, Huseyin; Karaman, Kamuran; Yilmaz, Baris; Akbayram, Sinan; Gunes, Burcak Tatli; Apak, Burcu Belen; Acipayam, Can; Aral, Yusuf Ziya; Karaman, Serap; Oren, Hale
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收藏Retrospective analysis of hemophilia B in Turkey: identifying main characteristics and treatment options
Zulfikar, Bulent; Koc, Basak; Sahin, Fahri; Sasmaz, Hatice Ilgen; Kavakli, Kaan; Balkan, Can; Antmen, Ali Buelent; Akbayram, Sinan; Guvenc, Birol; Okan, Vahap; Turkkan, Emine; Albayrak, Canan; Albayrak, Davut; Sarper, Nazan; Celkan, Tuelin Tiraje; Ayyildiz, Orhan; Aksu, Salih; Patiroglu, Tuerkan; Salcioglu, Zafer; Gunes, Adalet Meral; Torun, Yasemin Altuner; Caliskan, Umran; Tokgoz, Huseyin; Ay, Yilmaz; Ozdemir, Gul Nihal; Sonmez, Mehmet; Unal, Ekrem; Oner, Ahmet Fayik; Guler, Nil; Kupesiz, Osman Alphan; Oren, Hale; Karaman, Serap; Unuvar, Ayegul; Dagli, Mehmet; Demir, Ahmet Muzaffer; Soker, Murat; Alioglu, Buelent; Kaya, Zuehre; Ayhan, Aylin Canbolat; Bicakci, Zafer; Aral, Yusuf Ziya; Ar, Muhlis Cem
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收藏Different Kinetics and Risk Factors for Isolated Extramedullary Relapse after Allogeneic Hematopoietic Stem Cell Transplantation in Children with Acute Leukemia儿童急性白血病异基因造血干细胞移植后孤立性髓外复发的不同动力学及危险因素
Hazar, Volkan; Ozturk, Gulyuz; Yalcin, Koray; Uygun, Vedat; Aksoylar, Serap; Kupesiz, A.; Bozkaya, Ikbal Ok; Karagun, Barbaros Sahin; Bozkurt, Ceyhun; Ileri, Talia; Atay, Didem; Kocak, Ulker; Karasu, Gulsun Tezcan; Yesilipek, Akif; Gokce, Muge; Kansoy, Savas; Kintrup, Gulen Tuysuz; Karakukcu, Musa; Okur, Fatma Visal; Ertem, Mehmet; Kaya, Zuhre; Gursel, Orhan; Yaman, Yontem; Ozbek, Namik; Antmen, Bulent; Tufekci, Ozlem; Albayrak, Canan; Aksoy, Basak Adakli; Sezgin, Gulay; Albayrak, Davut; Evim, Melike Sezgin; Zengin, Emine; Pekpak, Esra
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收藏Once-weekly prophylaxis with glycoPEGylated recombinant factor VIII (N8-GP) in severe haemophilia A: Safety and efficacy results from pathfinder 2 (randomized phase III trial)
Curry, Nicola; Albayrak, Canan; Escobar, Miguel; Holme, Pal Andre; Kearney, Susan; Klamroth, Robert; Misgav, Mudi; Negrier, Claude; Wheeler, Allison; Santagostino, Elena; Shima, Midori; Landorph, Andrea; Tonder, Sidsel Marie; Lentz, Steven R.
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收藏Marked overlap of four genetic syndromes with dyskeratosis congenita confounds clinical diagnosis
Walne, Amanda J.; Collopy, Laura; Cardoso, Shirleny; Ellison, Alicia; Plagnol, Vincent; Albayrak, Canan; Albayrak, Davut; Kilic, Sara Sebnem; Patiroglu, Turkan; Akar, Haluk; Godfrey, Keith; Carter, Tina; Marafie, Makia; Vora, Ajay; Sundin, Mikael; Vulliamy, Thomas; Tummala, Hemanth; Dokal, Inderjeet
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收藏SNX10 Mutations Define a Subgroup of Human Autosomal Recessive Osteopetrosis With Variable Clinical SeveritySNX10突变定义了具有可变临床严重程度的人类常染色体隐性骨硬化症亚组
Pangrazio, Alessandra; Fasth, Anders; Sbardellati, Andrea; Orchard, Paul J.; Kasow, Kimberly A.; Raza, Jamal; Albayrak, Canan; Albayrak, Davut; Vanakker, Olivier M.; De Moerloose, Barbara; Vellodi, Ashok; Notarangelo, Luigi D.; Schlack, Claire; Strauss, Gabriele; Kuehl, Joern-Sven; Caldana, Elena; Lo Iacono, Nadia; Susani, Lucia; Kornak, Uwe; Schulz, Ansgar; Vezzoni, Paolo; Villa, Anna; Sobacchi, Cristina
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