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收藏Preliminary Assessment of the Phase 1/2 Clinical Trial Evaluating the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of AOC 1001 Administered Intravenously to Adult Patients with Myotonic Dystrophy Type 1 (DM1) (MARINA)1/2期临床试验的初步评估,评估静脉注射AOC 1001对1型强直性肌营养不良 (DM1) 成年患者的安全性,耐受性,药代动力学和药效学 (MARINA)
Johnson, Nicholas; Day, John; Hamel, Johanna; Thornton, Charles; Subramony, S.; Soltanzadeh, Payam; Statland, Jeffrey; Arnold, William; Wicklund, Matthew; Ditrapani, Kelly; Heusner, Carrie; Chen, Chao-Yin; McEvoy, Bradley; Zhu, Yiming; Tai, Li-Jung; Ackermann, Elizabeth
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收藏Ligand conjugated antisense oligonucleotide for the treatment of transthyretin amyloidosis: preclinical and phase 1 data
Viney, Nicholas J.; Guo, Shuling; Tai, Li-Jung; Baker, Brenda F.; Aghajan, Mariam; Jung, Shiangtung W.; Yu, Rosie Z.; Booten, Sheri; Murray, Heather; Machemer, Todd; Burel, Sebastien; Murray, Sue; Buchele, Gustavo; Tsimikas, Sotirios; Schneider, Eugene; Geary, Richard S.; Benson, Merrill D.; Monia, Brett P.
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收藏Underlying Immune Disorder May Predispose Some Transthyretin Amyloidosis Subjects to Inotersen-Mediated Thrombocytopenia
Narayanan, PadmaKumar; Curtis, Brian R.; Shen, Lijiang; Schneider, Eugene; Tami, Joseph A.; Paz, Suzanne; Burel, Sebastien A.; Tai, Li-Jung; Machemer, Todd; Kwoh, T. Jesse; Xia, Shuting; Shattil, Sanford J.; Witztum, Joseph L.; Engelhardt, Jeffery A.; Henry, Scott P.; Monia, Brett P.; Hughes, Steven G.
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