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Pharmacokinetics, Hemostatic Efficacy, and Safety of a New Human Fibrinogen Concentrate in Adult and Pediatric Patients with Congenital Fibrinogen Deficiency 一种新型人纤维蛋白原浓缩制剂在先天性纤维蛋白原缺乏症的成人和儿科患者中的药代动力学、止血疗效及安全性 Khayat, Claudia Djambas; El-Beshlawy, Amal; Meddeb, Balkis; Khelif, Abderrahim; Miesbach, Wolfgang; Adolf, Sonia; Boehm, Heike; Aigner, Silke; Abraha, Salomon; Bohlaender, Fabian; Schuettrumpf, Joerg 分享 收藏
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Predicting inhibitor development using a random peptide phage-display library approach in the SIPPET cohort Hassan, Shermarke; Baselli, Guido; Mollica, Luca; Rossi, Riccardo L.; Chand, Himani; El-Beshlawy, Amal; Elalfy, Mohsen; Ramanan, Vijay; Eshghi, Peyman; Karimi, Mehran; Palla, Roberta; Rosendaal, Frits R.; Peyvandi, Flora 分享 收藏
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Deferiprone for transfusional iron overload in sickle cell disease and other anemias: open-label study of up to 3 years Elalfy, Mohsen S.; Hamdy, Mona; El-Beshlawy, Amal; Ebeid, Fatma S. E.; Badr, Mohamed; Kanter, Julie; Inusa, Baba; Adly, Amira A. M.; Williams, Suzan; Kilinc, Yurdanur; Lee, David; Fradette, Caroline; Rozova, Anna; Temin, Noemi Toiber; Tricta, Fernando; Kwiatkowski, Janet L. 分享 收藏
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Transformative effect of a Humanitarian Program for individuals affected by rare diseases: building support systems and creating local expertise Verma, I. C.; El-Beshlawy, A.; Tylki-Szymanska, A.; Martins, A.; Duan, Y. -L.; Collin-Histed, T.; van der Linde, M. Schoneveld; Mansour, R.; Dung, V. C.; Mistry, Pramod K. 分享 收藏
Deferiprone vs deferoxamine for transfusional iron overload in SCD and other anemias: a randomized, open-label noninferiority study Kwiatkowski, Janet L.; Hamdy, Mona; El-Beshlawy, Amal; Ebeid, Fatma S. E.; Badr, Mohammed; Alshehri, Abdulrahman; Kanter, Julie; Inusa, Baba; Adly, Amira A. M.; Williams, Suzan; Kilinc, Yurdanur; Lee, David; Tricta, Fernando; Elalfy, Mohsen S. 分享 收藏
Risk of mortality from anemia and iron overload in nontransfusion-dependent β-thalassemia Musallam, Khaled M.; Vitrano, Angela; Meloni, Antonella; Pollina, Sebastiano Addario; Karimi, Mehran; El-Beshlawy, Amal; Hajipour, Mahmoud; Di Marco, Vito; Ansari, Saqib Hussain; Filosa, Aldo; Ricchi, Paolo; Ceci, Adriana; Daar, Shahina; Vlachaki, Efthymia; Singer, Sylvia Titi; Naserullah, Zaki A.; Pepe, Alessia; Scondotto, Salvatore; Dardanoni, Gabriella; Bonifazi, Fedele; Sankaran, Vijay G.; Vichinsky, Elliott; Taher, Ali T.; Maggio, Aurelio 分享 收藏
Performance of a clinical risk prediction model for inhibitor formation in severe haemophilia A Hassan, Shermarke; Palla, Roberta; Valsecchi, Carla; Garagiola, Isabella; El-Beshlawy, Amal; Elalfy, Mohsen; Ramanan, Vijay; Eshghi, Peyman; Karimi, Mehran; Gouw, Samantha Claudia; Mannucci, Pier Mannuccio; Rosendaal, Frits Richard; Peyvandi, Flora 分享 收藏
; ); ); ); Howard, Jo; Ataga, Kenneth, I; Brown, Robert C.; Achebe, Maureen; Nduba, Videlis; El-Beshlawy, Amal; Hassab, Hoda; Agodoa, Irene; Tonda, Margaret; Gray, Sarah; Lehrer-Graiwer, Joshua; Vichinsky, Elliott 分享 收藏
Survival and causes of death in 2,033 patients with non-transfusion-dependent β-thalassemia Musallam, Khaled M.; Vitrano, Angela; Meloni, Antonella; Pollina, Sebastiano Addario; Karimi, Mehran; El-Beshlawy, Amal; Hajipour, Mahmoud; Di Marco, Vito; Ansari, Saqib Hussain; Filosa, Aldo; Ricchi, Paolo; Ceci, Adriana; Daar, Shahina; Vlachaki, Efthymia; Singer, Sylvia Titi; Naserullah, Zaki A.; Pepe, Alessia; Scondotto, Salvatore; Dardanoni, Gabriella; Bonifazi, Fedele; Sankaran, Vijay G.; Vichinsky, Elliott; Taher, Ali T.; Maggio, Aurelio 分享 收藏
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A Phase 3 Randomized Trial of Voxelotor in Sickle Cell Disease Vichinsky, Elliott; Hoppe, Carolyn C.; Ataga, Kenneth I.; Ware, Russell E.; Nduba, Videlis; El-Beshlawy, Amal; Hassab, Hoda; Achebe, Maureen M.; Alkindi, Salam; Brown, R. Clark; Diuguid, David L.; Telfer, Paul; Tsitsikas, Dimitris A.; Elghandour, Ashraf; Gordeuk, Victor R.; Kanter, Julie; Abboud, Miguel R.; Lehrer-Graiwer, Joshua; Tonda, Margaret; Intondi, Allison; Tong, Barbara; Howard, Jo 分享 收藏
Role of factor VIII-binding capacity of endogenous von Willebrand factor in the development of factor VIII inhibitors in patients with severe hemophilia A Repesse, Yohann; Costa, Catherine; Palla, Roberta; Moshai, Elika Farrokhi; Borel-Derlon, Annie; D'Oiron, Roseline; Rothschild, Chantal; El-Beshlawy, Amal; Elalfy, Mohsen; Ramanan, Vijay; Eshghi, Peyman; Oldenburg, Johannes; Pavlova, Anna; Rosendaal, Frits R.; Peyvandi, Flora; Kaveri, Srinivas V.; Lacroix-Desmazes, Sebastien 分享 收藏
Long-term hematological, visceral, and growth outcomes in children with Gaucher disease type 3 treated with imiglucerase in the International Collaborative Gaucher Group Gaucher Registry El-Beshlawy, Amal; Tylki-Szymanska, Anna; Vellodi, Ashok; Belmatoug, Nadia; Grabowski, Gregory A.; Kolodny, Edwin H.; Batista, Julie L.; Cox, Gerald F.; Mistry, Pramod K. 分享 收藏
A Randomized Trial of Factor VIII and Neutralizing Antibodies in Hemophilia A Peyvandi, F.; Mannucci, P. M.; Garagiola, I.; El-Beshlawy, A.; Elalfy, M.; Ramanan, V.; Eshghi, P.; Hanagavadi, S.; Varadarajan, R.; Karimi, M.; Manglani, M. V.; Ross, C.; Young, G.; Seth, T.; Apte, S.; Nayak, D. M.; Santagostino, E.; Mancuso, M. E.; Sandoval Gonzalez, A. C.; Mahlangu, J. N.; Bonanad Boix, S.; Cerqueira, M.; Ewing, N. P.; Male, C.; Owaidah, T.; Soto Arellano, V.; Kobrinsky, N. L.; Majumdar, S.; Perez Garrido, R.; Sachdeva, A.; Simpson, M.; Thomas, M.; Zanon, E.; Antmen, B.; Kavakli, K.; Manco-Johnson, M. J.; Martinez, M.; Marzouka, E.; Mazzucconi, M. G.; Neme, D.; Palomo Bravo, A.; Paredes Aguilera, R.; Prezotti, A.; Schmitt, K.; Wicklund, B. M.; Zulfikar, B.; Rosendaal, F. R. 分享 收藏