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Long-term outcomes after unrelated donor transplantation for severe sickle cell disease on the BMT CTN 0601 trial BMT CTN 0601试验中严重镰状细胞病的无关供体移植后的长期结果 Eapen, Mary; Kou, Jianqun; Andreansky, Martin; Bhatia, Monica; Brochstein, Joel; Chaudhury, Sonali; Haight, Ann E.; Haines, Hilary; Jacobsohn, David; Jaroscak, Jennifer; Kasow, Kimberly A.; Krishnamurti, Lakshmanan; Levine, John E.; Leung, Kathryn; Margolis, David; Yu, Lolie C.; Horowitz, Mary M.; Kamani, Naynesh; Walters, Mark C.; Shenoy, Shalini 分享 收藏
Long-Term Immune Reconstitution in ADA-Deficient Patients Treated With Elapegademase: A Real-World Experience Murguia-Favela, Luis; Suresh, Sneha; Wright, Nicola A. M.; Alvi, Saima; Tehseen, Sarah; Hernandez-Trujillo, Vivian; Seroogy, Christine M.; Haddad, Elie; Nieves, Daime; Hershfield, Michael S.; Walter, Jolan E.; Pettiford, Leah; Kamani, Naynesh R.; Keller, Michael D.; Pham-Huy, Anne; Grunebaum, Eyal 分享 收藏
Granulocyte Colony-Stimulating Factor Is Safe and Well Tolerated following Allogeneic Transplantation in Patients with Sickle Cell Disease 镰状细胞病患者同种异体移植后粒细胞集落刺激因子安全且耐受性良好 Shah, Niketa C.; Bhoopatiraju, Sweta; Abraham, Allistair; Anderson, Eric; Andreansky, Martin; Bhatia, Monica; Chaudhury, Sonali; Cuvelier, Geoff D. E.; Godder, Kamar; Grimley, Michael; Hale, Gregory; Kamani, Naynesh; Jacobsohn, David; Ngwube, Alexander; Gilman, Andrew L.; Skiles, Jodi; Yu, Lolie C.; Shenoy, Shalini 分享 收藏
Subsequent neoplasms and late mortality in children undergoing allogeneic transplantation for nonmalignant diseases Kahn, Justine M.; Brazauskas, Ruta; Tecca, Heather R.; Bo-Subait, Stephanie; Buchbinder, David; Battiwala, Minoo; Flowers, Mary E. D.; Savani, Bipin N.; Phelan, Rachel; Broglie, Larisa; Abraham, Allistair A.; Keating, Amy K.; Daly, Andrew; Wirk, Baldeep; George, Biju; Alter, Blanche P.; Ustun, Celalettin; Freytes, Cesar O.; Beitinjaneh, Amer M.; Duncan, Christine; Copelan, Edward; Hildebrandt, Gerhard C.; Murthy, Hemant S.; Lazarus, Hillard M.; Auletta, Jeffery J.; Myers, Kasiani C.; Williams, Kirsten M.; Page, Kristin M.; Vrooman, Lynda M.; Norkin, Maxim; Byrne, Michael; Diaz, Miguel Angel; Kamani, Naynesh; Bhatt, Neel S.; Rezvani, Andrew; Farhadfar, Nosha; Mehta, Parinda A.; Hematti, Peiman; Shaw, Peter J.; Kamble, Rammurti T.; Schears, Raquel; Olsson, Richard F.; Hayashi, Robert J.; Gale, Robert Peter; Mayo, Samantha J.; Chhabra, Saurabh; Rotz, Seth J.; Badawy, Sherif M.; Ganguly, Siddhartha; Pavletic, Steven; Nishihori, Taiga; Prestidge, Tim; Agrawal, Vaibhav; Hogan, William J.; Inamoto, Yoshihiro; Shaw, Bronwen E.; Satwani, Prakash 分享 收藏
Bone marrow transplantation for adolescents and young adults with sickle cell disease: Results of a prospective multicenter pilot study Krishnamurti, Lakshmanan; Neuberg, Donna S.; Sullivan, Keith M.; Kamani, Naynesh R.; Abraham, Allistair; Campigotto, Federico; Zhang, Wandi; Dandoul, Thabat; De Castro, Laura; Parikh, Suhag; Bakshi, Nitya; Haight, Ann; Hassell, Kathryn L.; Loving, Rebekah; Rosenthal, Joseph; Smith, Shannon L.; Smith, Wally; Spearman, Marcus; Stevenson, Kristen; Wu, Catherine J.; Wiedl, Christina; Waller, Edmund K.; Walters, Mark C. 分享 收藏
Randomized controlled trial of individualized treatment summary and survivorship care plans for hematopoietic cell transplantation survivors Majhail, Navneet S.; Murphy, Elizabeth; Laud, Purushottam; Preussler, Jaime M.; Denzen, Ellen M.; Abetti, Beatrice; Adams, Alexia; Besser, RaeAnne; Burns, Linda J.; Cerny, Jan; Drexler, Rebecca; Hahn, Theresa; Idossa, Lensa; Jahagirdar, Balkrishna; Kamani, Naynesh; Loren, Alison; Mattila, Deborah; McGuirk, Joseph; Moore, Heather; Reynolds, Jana; Saber, Wael; Salazar, Lizette; Schatz, Barry; Stiff, Patrick; Wingard, John R.; Syrjala, Karen L.; Baker, K. Scott 分享 收藏
Successful matched sibling donor marrow transplantation following reduced intensity conditioning in children with hemoglobinopathies King, Allison A.; Kamani, Naynesh; Bunin, Nancy; Sahdev, Indira; Brochstein, Joel; Hayashi, Robert J.; Grimley, Michael; Abraham, Allistair; Dioguardi, Jacqueline; Chan, Ka Wah; Douglas, Dorothea; Adams, Roberta; Andreansky, Martin; Anderson, Eric; Gilman, Andrew; Chaudhury, Sonali; Yu, Lolie; Dalal, Jignesh; Hale, Gregory; Cuvelier, Geoff; Jain, Akshat; Krajewski, Jennifer; Gillio, Alfred; Kasow, Kimberly A.; Delgado, David; Hanson, Eric; Murray, Lisa; Shenoy, Shalini 分享 收藏
Hematopoietic stem cell transplantation in thalassemia major and sickle cell disease: indications and management recommendations from an international expert panel Angelucci, Emanuele; Matthes-Martin, Susanne; Baronciani, Donatella; Bernaudin, Francoise; Bonanomi, Sonia; Cappellini, Maria Domenica; Dalle, Jean-Hugues; Di Bartolomeo, Paolo; Diaz de Heredia, Cristina; Dickerhoff, Roswitha; Giardini, Claudio; Gluckman, Eliane; Hussein, Ayad Achmed; Kamani, Naynesh; Minkov, Milen; Locatelli, Franco; Rocha, Vanderson; Sedlacek, Petr; Smiers, Frans; Thuret, Isabelle; Yaniv, Isaac; Cavazzana, Marina; Peters, Christina 分享 收藏
Expansion of immunoglobulin-secreting cells and defects in B cell tolerance in Rag-dependent immunodeficiency Walter, Jolan E.; Rucci, Francesca; Patrizi, Laura; Recher, Mike; Regenass, Stephan; Paganini, Tiziana; Keszei, Marton; Pessach, Itai; Lang, Philipp A.; Poliani, Pietro Luigi; Giliani, Silvia; Al-Herz, Waleed; Cowan, Morton J.; Puck, Jennifer M.; Bleesing, Jack; Niehues, Tim; Schuetz, Catharina; Malech, Harry; DeRavin, Suk See; Facchetti, Fabio; Gennery, Andrew R.; Andersson, Emma; Kamani, Naynesh R.; Sekiguchi, JoAnn; Alenezi, Hamid M.; Chinen, Javier; Dbaibo, Ghassan; ElGhazali, Gehad; Fontana, Adriano; Pasic, Srdjan; Detre, Cynthia; Terhorst, Cox; Alt, Frederick W.; Notarangelo, Luigi D. 分享 收藏
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Allogeneic hematopoietic cell transplantation for primary immune deficiency diseases: Current status and critical needs Griffith, Linda M.; Cowan, Morton J.; Kohn, Donald B.; Notarangelo, Luigi D.; Puck, Jennifer M.; Schultz, Kirk R.; Buckley, Rebecca H.; Eapen, Mary; Kamani, Naynesh R.; O'Reilly, Richard J.; Parkman, Robertson; Roifman, Chaim M.; Sullivan, Kathleen E.; Filipovich, Alexandra H.; Fleisher, Thomas A.; Shearer, William T. 分享 收藏