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Paula R. Clemens

university of pittsburgh school of medicine

55H指数
235论文数
1.5W被引数
收录论文 88
发表时间
Adrenal insufficiency in individuals with Duchenne muscular dystrophy treated with glucocorticoids: Insights from the past, current challenges, and future directionsglucocorticoids治疗的患者中肾上腺功能不全:来自过去的见解、当前挑战和未来方向
err2026-09-22
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PREAI
errDavid R. Weber; Alexandra Ahmet; Kathi Kinnett; Maria-Elena Lautatzis; Hugh J. McMillan; Susan Apkon; Shipra Bansal; Robert W. Benjamin; Paula R. Clemens; Janet L. Crane; Melissa Fiscaletti; Carol Lam; Laura McAdam; Meilan M. Rutter; Nadia Merchant; Nat Nasomyont; Stefan Nicolau; Kim Phung; Nora Renthal; Mena Scavina; Julia Sorbara; Jaclyn Tamaroff; Cuixia Tian; Claire Wood; Tommaso Aversa; Luca Bello; Sabrina Corbetta; Francesca Cumbo; Luisa De Sanctis; Natascia Di Iorgi; Alberto Ferlin; Danilo Fintini; Eugenio Maria Mercuri; Chiara Panicucci; Gianluca Tornese; Rachel Schrader; Kathryn A. Selby; Aravindhan Veerapandiyan; Sze Choong Wong; Leanne M. Ward; Anne Marie Sbrocchi
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Prednisone, not vamorolone, suppresses novel serum bone and cartilage biomarkers associated with growth failure in children with Duchenne muscular dystrophy泼尼松,而非vamorolone,抑制与杜氏肌营养不良儿童生长迟缓相关的血清骨骼和软骨新型生物标志物
err2026-08-03
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errOAAI
errRebecca A. Tobin; Utkarsh J. Dang; Laura Hagerty; Leanne M. Ward; Raoul Rooman; Karl Heinz Konopka; Paula R. Clemens; Michela Guglieri; Jesse Damsker; Michael Ziemba; Yetrib Hathout; Eric P. Hoffman
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Adrenal Suppression in Duchenne Muscular Dystrophy: Management Strategies Incorporating Novel Steroid Vamorolone杜氏肌营养不良症中的肾上腺抑制:整合新型类固醇vamorolone的管理策略
err2026-02-01
err1
PREAI
errSbrocchi, Anne Marie; Kinnett, Kathi; Lautatzis, Maria-Elena; McMillan, Hugh J.; Selby, Kathryn A.; Veerapandiyan, Aravind; Weber, David R.; Apkon, Susan; Bharucha-Goebel, Diana X.; Bharill, Sonum; Bansal, Shipra; Clemens, Paula R.; Fiscaletti, Melissa; Halloun, Rana; Lam, Carol; Merchant, Nadia; McAdam, Laura; Nasomyont, Nat; Nicolau, Stefan; Ochoa Molina, Maria F.; Phung, Kim; Rutter, Meilan M.; Scavina, Mena; Surampudi, Prasanth N.; Tamaroff, Jaclyn; Tian, Cuixia; Ward, Leanne M.; Wood, Claire L.; Wong, Sze Choong; Ahmet, Alex
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Mineralocorticoid receptor antagonism of vamorolone: Evidence from LIONHEART and VISION-DMD clinical trialsde Vera A, Clemens PR, Dang UJ, Dutreix C, Gresko E, Guglieri M, et al. 醛固酮受体拮抗作用:来自LIONHEART和VISION-DMD临床试验的证据。Steroids. (2025) 223:109689. doi: 10.1016/j.steroids.2025.109689。
err2025-11-01
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errOAAI
errde Vera, Ana; Clemens, Paula R.; Dang, Utkarsh J.; Dutreix, Catherine; Gresko, Ekaterina; Guglieri, Michela; Hagerty, Laura; Hasham, Shabir; Damsker, Jesse; Hathout, Yetrib; Linden, Aki; Berglund, Anders; Tobin, Rebecca; Wahbi, Karim; Hoffman, Eric P.
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Exposure-response of serum biomarkers to vamorolone, a dissociative corticosteroidal anti-inflammatory drug, in 4-to <7-year childrenvamorolone(一种解离性皮质类固醇抗炎药)对4至<7岁儿童血清生物标志物的暴露-反应关系
err2025-11-01
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errOAAI
errMummidivarpu, Swati; Dang, Utkarsh J.; Ziemba, Michael; Hathout, Yetrib; Clemens, Paula R.; Damsker, Jesse; Hagerty, Laura; Jusko, William J.; Smith, Edward C.; Mah, Jean K.; Guglieri, Michela; Nevo, Yoram; Kuntz, Nancy; Mcdonald, Craig M.; Ryan, Monique M.; Castro, Diana; Finkel, Richard S.; Conklin, Laurie S.; Mccall, John M.; Nagaraju, Kanneboyina; Van Den Anker, John; Hoffman, Eric P.
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Efficacy and safety of avalglucosidase alfa in patients with late-onset Pompe disease after 145 weeks of treatment during the COMET trialavalglucosidase alfa在COMET试验中治疗晚期发作型庞贝病145周后的疗效与安全性
err2025-08-16
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errOAAI
errPriya S. Kishnani; Jordi Díaz-Manera; Sergey Illarioshkin; Ans T. van der Ploeg; Paula R. Clemens; John W. Day; Antonio Toscano; Hani Kushlaf; Shafeeq Ladha; Shahram Attarian; Gerson Carvalho; Anna Kostera-Pruszczyk; Sevim Erdem-Özdamar; Ozlem Goker-Alpan; Tahseen Mozaffar; Volker Straub; Mark Roberts; Kristina An Haack; Olivier Huynh-Ba; Swathi Tammireddy; Magali Periquet; Nathan Thibault; Tianyue Zhou; Mazen M. Dimachkie; Benedikt Schoser
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Switching Enzyme Replacement Therapy for Late-Onset Pompe Disease From Alglucosidase Alfa to Cipaglucosidase Alfa Plus Miglustat: Post Hoc Effect Size Analysis of PROPEL将晚期庞贝病糖苷酶替代疗法从阿糖苷酶alfa切换为西帕糖苷酶alfa联合米格鲁斯坦:PROPEL研究的后效分析
err2025-05-07
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errOAAI
errHani Kushlaf; Jordi Díaz-Manera; Drago Bratkovic; Barry J. Byrne; Kristl G. Claeys; Paula R. Clemens; Mazen M. Dimachkie; Priya S. Kishnani; Pascal Laforêt; Mark Roberts; Benedikt Schoser; Antonio Toscano; Jeff Castelli; Fred Holdbrook; Sheela Sitaraman Das; Mitchell Goldman; Tahseen Mozaffar; the PROPEL Study Group
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Association of DMD Gene Variant Classes With Motor Outcomes in a Drug Registration Clinical Trial Setting
err2025-04-01
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PREAI
errFang, Yuan; Dang, Utkarsh J.; Illei, Katherine I.; Clemens, Paula; Hoffman, Eric P.
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Analysis of human urinary extracellular vesicles reveals disordered renal metabolism in myotonic dystrophy type 1对人类尿液外泌体的分析揭示了强直性肌营养不良1型中的肾代谢紊乱
err2025-03-05
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errOAAI
errKumari, Preeti; Sullivan, Lauren M.; Li, Zhaozhi; Conquest, E. Parker; Cornforth, Elizabeth; Jayakumar, Rojashree; Hu, Ningyan; Sizemore, J. Alexander; Mckee, Brigham B.; Kitchen, Robert R.; Gonzalez-Perez, Paloma; Linville, Constance; Castro, Karla; Gutierrez, Hilda; Samaan, Soleil; Townsend, Elise L.; Darras, Basil T.; Rutkove, Seward B.; Iannaccone, Susan T.; Clemens, Paula R.; Puwanant, Araya; Das, Sudeshna
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A Parent Project Muscular Dystrophy-sponsored International Workshop Report on Endocrine and Bone Issues in Patients with Duchenne Muscular Dystrophy: An Ever-changing LandscapeParent Project Muscular Dystrophy资助的国际研讨会报告:杜氏肌营养不良症患者的内分泌和骨骼问题:一个不断变化的领域
err2025-01-26
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PREAI
errWard, Leanne M.; Weber, David R.; Wong, Sze Choong; Apkon, Susan; Clemens, Paula R.; Cripe, Linda H.; Mcmillan, Hugh J.; Mercuri, Eugenio; Phung, Kim; Renthal, Nora E.; Rutter, Meilan M.; Tian, Cuixia; Wood, Claire L.; Zeitler, Philip S.; Buccella, Filippo; Kinnett, Kathi; Furlong, Pat
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Safety and efficacy of viltolarsen in ambulatory and nonambulatory males with Duchenne muscular dystrophy
err2024-10-08
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errOAAI
errHarper, Amy D.; Topaloglu, Haluk; Mercuri, Eugenio; Suslov, Vasiliy; Wu, Liwen; Ayanoglu, Cigdem Y.; Tansey, Michael; Previtera, Michelle L.; Crozier, Robert A.; Magnus, Leslie; Clemens, Paula R.
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Adrenal Suppression From Vamorolone and Prednisone in Duchenne Muscular Dystrophy: Results From the Phase 2b Clinical Trial
err2024-08-04
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errOAAI
errAhmet, Alexandra; Tobin, Rebecca; Dang, Utkarsh J.; Rooman, Raoul; Guglieri, Michela; Clemens, Paula R.; Hoffman, Eric P.; Ward, Leanne M.
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Efficacy and Safety of Vamorolone Over 48 Weeks in Boys With Duchenne Muscular DystrophyVamorolone在Duchenne肌营养不良症男孩中48周的疗效和安全性
err2024-03-12
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errOAAI
errDang, Utkarsh J.; Damsker, Jesse M.; Guglieri, Michela; Clemens, Paula R.; Perlman, Seth J.; Smith, Edward C.; Horrocks, Iain; Finkel, Richard S.; Mah, Jean K.; Deconinck, Nicolas; Goemans, Nathalie M.; Haberlova, Jana; Straub, Volker; Mengle-Gaw, Laurel; Schwartz, Benjamin D.; Harper, Amy; Shieh, Perry B.; De Waele, Liesbeth; Castro, Diana; Yang, Michele L.; Ryan, Monique M.; McDonald, Craig M.; Tulinius, Mar; Webster, Richard I.; Mcmillan, Hugh J.; Kuntz, Nancy; Rao, Vamshi K.; Baranello, Giovanni; Spinty, Stefan; Childs, Anne-Marie; Sbrocchi, Annie M.; Selby, Kathryn A.; Monduy, Migvis; Nevo, Yoram; Vilchez, Juan J.; Nascimento-Osorio, Andres; Niks, Erik H.; De Groot, Imelda J. M.; Katsalouli, Marina; van den Anker, John N.; Ward, Leanne M.; Leinonen, Mika; D'Alessandro, Andrea L.; Hoffman, Eric P.
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Findings from the Longitudinal CINRG Becker Natural History Study
err2023-11-17
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errOAAI
errClemens, Paula R.; Gordish-Dressman, Heather; Niizawa, Gabriela; Gorni, Ksenija; Guglieri, Michela; Connolly, Anne M.; Wicklund, Matthew; Bertorini, Tulio; Mah, Jean; Thangarajh, Mathula; Smith, Edward C.; Kuntz, Nancy L.; McDonald, Craig M.; Henricson, Erik; Upadhyayula, S.; Byrne, Barry; Manousakis, Georgios; Harper, Amy; Iannaccone, Susan; Dang, Utkarsh J.
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Antigen-driven T cell-macrophage interactions mediate the interface between innate and adaptive immunity in histidyl-tRNA synthetase-induced myositis
err2023-09-22
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errOAAI
errReay, Daniel P.; Tabib, Tracy; Wang, Ying; Oriss, Timothy B.; Young, Nicholas A.; Lafyatis, Robert A.; Jarjour, Wael N.; Clemens, Paula R.; Ascherman, Dana P.
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Efficacy and Safety of Viltolarsen in Boys With Duchenne Muscular Dystrophy: Results From the Phase 2, Open-Label, 4-Year Extension Study
err2023-05-02
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errOAAI
errClemens, Paula R.; Rao, Vamshi K.; Connolly, Anne M.; Harper, Amy D.; Mah, Jean K.; McDonald, Craig M.; Smith, Edward C.; Zaidman, Craig M.; Nakagawa, Tomoyuki; Hoffman, Eric P.
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The Impact of Establishing a Diversity, Equity, and Inclusion Committee in a Single US Adult Neurology Residency Program
err2023-04-25
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PREAI
errRavishankar, Mathura; Fukuda, Keiko; Alzyoud, Lamees; Nidamanuri, Priya; Pollard, Rebecca; Van Cott, Anne; Clemens, Paula; Sadasivan, Alexandria; Pennell, Page; Ojha, Ajitesh
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