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Development of a novel gene editing lexicon for hemophilia: methodology and results 开发用于血友病的新型基因编辑词典: 方法和结果 Kessler, Craig M.; Valentino, Leonard A.; Thornburg, Courtney D.; Unzu, Carmen; Kay, Mark A.; Peyvandi, Flora; Smith, Penni; Miesbach, Wolfgang; Mckeown, William; Pierce, Glenn F.; Khair, Kate; Starcevic, Katarina; Pillai, Monisha; Jones, Micheala; Sindhurakar, Anil; Whyte, Lauren; Delwart, Virginie; Chiao, Megan; Gutstein, David E.; Antonino, Ilia; Hermans, Cedric; Pipe, Steven W. 分享 收藏
Operationalising a Haemophilia Gene Editing Lexicon for Practical Use 操作血友病基因编辑词典以供实际使用 Mckeown, William; Hermans, Cedric; Unzu, Carmen; Kay, Mark A.; Peyvandi, Flora; Smith, Penni; Miesbach, Wolfgang; Pierce, Glenn F.; Khair, Kate; Valentino, Leonard A.; Pipe, Steven W.; Pillai, Monisha; Jones, Micheala; Delwart, Virginie; Sindhurakar, Anil; Gutstein, David E.; Kessler, Craig M. 分享 收藏
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A novel gene editing lexicon strategy for the haemophilia community: Research plan for development and preliminary results 血友病社区的新型基因编辑词典策略: 开发和初步结果的研究计划 Hermans, Cedric; Valentino, Leonard A.; Thornburg, Courtney D.; Unzu, Carmen; Kay, Mark A.; Peyvandi, Flora; Smith, Penni; Miesbach, Wolfgang; Mckeown, William; Pierce, Glenn F.; Khair, Kate; Pipe, Steven W.; Starcevic, Katarina; Pillai, Monisha; Jones, Micheala; Chiao, Megan; Antonino, Ilia; Kessler, Craig 分享 收藏
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Real-world data in patients with congenital hemophilia and inhibitors: final data from the FEIBA Global Outcome (FEIBA GO) study Ettingshausen, Carmen Escuriola; Hermans, Cedric; Holme, Pal A.; Cid, Ana R. R.; Khair, Kate; Oldenburg, Johannes; Negrier, Claude; Botha, Jaco; Lelli, Aurelia; Windyga, Jerzy 分享 收藏
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Humanistic burden of problem joints for children and adults with haemophilia Burke, Tom; Rodriguez-Santana, Idaira; Chowdary, Pratima; Curtis, Randall; Khair, Kate; Laffan, Michael; Mclaughlin, Paul; Noone, Declan; O'Mahony, Brian; Pasi, John; Skinner, Mark; O'Hara, Jamie 分享 收藏
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