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Profiling of Anti-Signal-Recognition Particle Antibodies and Clinical Characteristics in South Korean Patients With Immune-Mediated Necrotizing Myopathy Kim, Soo-Hyun; Choi, Yunjung; Oh, Eun Kyoung; Nishino, Ichizo; Suzuki, Shigeaki; Suh, Bum Chun; Shin, Ha Young; Kim, Seung Woo; Yoon, Byeol-A; Oh, Seong-il; Kim, Yoo Hwan; Kim, Hyunjin; Lim, Young-Min; Baek, Seol-Hee; Shin, Je-Young; Seok, Hung Youl; Lee, Seung-Ah; Choi, Young-Chul; Park, Hyung Jun 分享 收藏
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COMET post hoc analysis: Efficacy of long-term avalglucosidase alfa in subgroups of participants with late-onset Pompe disease Toscano, Antonio; Kishnani, Priya; Dimachkie, Mazen M.; Sacconi, Sabrina; Van der Beek, Nadine; Roberts, Mark E.; Suwazono, Shugo; Choi, Young Chul; Sgobbi de Souza, Paulo Victor; Schoser, Benedikt; Armstrong, Nicole; Huynh-Ba, Olivier; Thibault, Nathan; Periquet, Magali; Diaz-Manera, Jordi 分享 收藏
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Clinical and Radiological Features of Korean Patients With Anti-HMGCR Myopathy Oh, Eun Kyoung; Lee, Seung-Ah; Lee, Hyun Joon; Cha, Yoon Jin; Kim, Sungjun; Lee, Hyung-Soo; Suh, Bum Chun; Shin, Ha Young; Kim, Seung Woo; Yoon, Byeol-A; Oh, Seong-il; Kim, Yoo Hwan; Cho, Joong-Yang; Cho, Jeong Hee; Kwon, Ki-Han; Choi, Young-Chul; Park, Hyung Jun 分享 收藏
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The avalglucosidase alfa phase 3 COMET trial in late-onset Pompe disease patients: Efficacy and safety results after 97 weeks Kishnani, Priya; Diaz-Manera, Jordi; Kushlaf, Hani; Ladha, Shafeeq; Mozaffar, Tahseen; Straub, Volker; Toscano, Antonio; van der Ploeg, Ans T.; Berger, Kenneth I.; Clemens, Paula R.; Chien, Yin-Hsiu; Day, John W.; Illarioshkin, Sergey; Roberts, Mark; Attarian, Shahram; Carvalho, Gerson; Choi, Young-Chul; Erdem-Ozdamar, Sevim; Goker-Alpan, Ozlem; Kostera-Pruszczyk, Anna; Haack, Kristina An; Thibault, Nathan; Zhou, Tianyue; Dimachkie, Mazen M.; Schoser, Benedikt 分享 收藏
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Efficacy and safety results of the avalglucosidase alfa phase 3 COMET trial in late-onset Pompe disease patients Kishnani, Priya S.; Attarian, Shahram; Borges, Joao Lindolfo; Bouhourd, Francoisee; Chien, Yin-Hsiu; Choi, Young-Chul; Clemens, Paula; Day, John; Diaz-Manera, Jordi; Erdem-Ozdamar, Sevim; Goker-Alpan, Ozlem; Illarioshkin, Sergey; Kostera-Pruszczyk, Anna; Kushlaf, Hani; Ladha, Shafeeq; Mozaffar, Tahseen; Roberts, Mark; Straub, Volker; Toscano, Antonio; van der Ploeg, Ans; Haack, Kristina An; Huynh-Ba, Olivier; Zhou, Tianyue; Dimachkie, Mazen; Schoser, Benedikt 分享 收藏
Nogo-A Is Critical for Pro-Inflammatory Gene Regulation in Myocytes and Macrophages Ullah, H. M. Arif; Elfadl, A. K.; Park, SunYoung; Kim, Yong Deuk; Chung, Myung-Jin; Son, Ji-Yoon; Yun, Hyun-Ho; Park, Jae-Min; Yim, Jae-Hyuk; Jung, Seung-Jun; Choi, Young-Chul; Shin, Jin-Hong; Kim, Dae-Seong; Park, Jin-Kyu; Jeong, Kyu-Shik 分享 收藏