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M K Javaid

rare disease collaborative network for adult rare bone diseases

75H指数
724论文数
2.0W被引数
收录论文 236
发表时间
Brittle Bone Society best practice management recommendations for adults with severe Osteogenesis Imperfecta (OI), including type III OI: a consensus statement from a multi-disciplinary severe OI working group英国脆骨病协会关于成人严重型成骨不全(包括III型成骨不全)的最佳管理实践建议:来自多学科严重型成骨不全工作组的一致性声明
err2026-09-08
err0
errOAAI
errKaiyang Song; Rohit Vijjhalwar; Christopher Coulson; Guirish Solanki; Adrian Gardner; Lisa Mills; Jacqui Clinch; Ishpinder Toor; Stuart Ralston; Susan Parekh; Mark Heathfield; Amaka Offiah; Meena Balasubramanian; Jenny Walsh; Ruth Kingshott; Davina Ford; Claire Hill; Jill Birch; Judith Bubbear; Sophie Barlow; Martyn Dudley; Helen Jenkins; Coreen Kelday; Patricia Osborne; Sally Harris; Jamie Abbott; Muhammad Kassim Javaid
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A narrative review on the therapeutic potential of stem cells in neurodegenerative diseases: advances, insights, and challenges干细胞在神经退行性疾病治疗潜力方面的叙事性综述:进展、见解与挑战
err2026-02-01
err0
PREAI
errPatel, Tirath; Henna, Fathimathul; Sharif, Iman; Javed, Inaya; Mustafa, Fatima; Sharif, Hannan; Nasir, Fatima; Javaid, Mirat; Usman, Samman Fatima; Hanani, Christopher; Anand, Nikhilesh
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Baseline Characteristics of the TOPaZ Study: Randomised Trial of Teriparatide and Zoledronic Acid Compared with Standard Care in Adults with Osteogenesis ImperfectaTOPaZ研究基线特征:特立帕肽和唑来膦酸与标准护理在成骨不全成人中的随机对照试验
err2025-11-08
err0
errOAAI
errJannie Dahl Hald; Christopher Weir; Catriona Keerie; Lorna Dewar; Morag MacLean; Lynsey Milne; Richard Keen; Jennifer Walsh; Kenneth Poole; Bente Langdahl; John R. Lindsay; Nazim Ghouri; Rosemary J Hollick; Terry Aspray; Rachel K. Crowley; Martine Cohen-Solal; Zaki Hassan-Smith; Stephen Tuck; Elizabeth Curtis; Nick Harvey; E. Marelise W. Eekhoff; Johannes Feenstra; Geeta Hampson; Mike Stone; Jane Turton; Prashanth Patel; Mashood Siddiqi; Robin Munro; Matthew Roy; Zoe Paskins; Deepa Narayanan; Ellen Malcolm; Muhammad Kassim Javaid; Patricia Osborne; Jonathan C. Y. Tang; Wayne Lam; David Moore; Holly A. Black; Andrew D. Duckworth; Navnit Makaram; Tianyu Guo; Gregor Stenhouse; Stuart H. Ralston
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Bridging the knowledge gap in rare bone disorders: insights from the APCO Asia-Pacific Rare Bone Disorders Engagement (ASPIRE) survey弥合罕见骨病领域的知识差距:APCO亚太罕见骨病参与(ASPIRE)调查的见解
err2025-10-13
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errOAAI
errManju Chandran; Muhammad Kassim Javaid; Tricia Newell; Satpreet Kaur; Roderick Clifton-Bligh; Craig F. Munns; Andrea Trombetti; Sanjay Kumar Bhadada; Peter R. Ebeling; Ambrish Mithal; Maria Luisa Brandi
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Developing a Standardised Dataset for Natural History Studies in Fibrous Dysplasia/McCune-Albright Syndrome
err2025-05-02
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errOAAI
errPriego Zurita, Ana Luisa; Bulaicon, Oana O.; Bryce, Jillian; Arrieta, Nerea; Caballero Campos, Magdalena; Cherenko, Mariya; Doxiadis, Gaby; Grasemann, Corinna; Javaid, M. Kassim; Mcdevitt, Helen; van der Meeren, Stijn W.; Ovejero Crespo, Diana; de Sanctis, Luisa; Seefried, Lothar; Verrijn Stuart, Annemarie A.; Tessaris, Daniele; de Witte, Pieter Bas; Chapurlat, Roland; Ahmed, S. Faisal; Appelman-Dijkstra, Natasha M.
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Current Practices in Monitoring Children and Adults With X-linked Hypophosphatemia: A Global Survey of Expert ExperienceX-连锁低磷酸盐血症儿童和成人监测的当前实践:一项全球专家经验调查
err2025-03-20
err1
errOAAI
errDalal S Ali; Farah Alsarraf; Hajar Abu Alrob; R Todd Alexander; Abdulrahman Almoulia; Natasha M Appelman-Dijkstra; Signe Sparre Beck-Nielsen; Martin Biosse-Duplan; Maria Luisa Brandi; Thomas O Carpenter; Catherine Chaussain; Martine Cohen-Solal; Rachel K Crowley; Karel Dandurand; Pablo Florenzano; Claudia Gagnon; Paul Goodyer; Chelsey Grimbly; Salma Hussein; Erik A Imel; Suzanne M Jan de Beur; Muhammad K Javaid; Anna Lehman; Willem F Lems; E Michael Lewiecki; Ciara McDonnell; Reza D Mirza; Emmett Morgante; Anthony A Portale; Yumie Rhee; Heide Siggelkow; Laura L Tosi; Leanne M Ward; Gordon Guyatt; Aliya A Khan
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Mobility and Quality of Life in Adults with Paediatric-Onset Hypophosphatasia Treated with Asfotase Alfa: Results from UK Managed Access Agreement
err2025-03-01
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errOAAI
errMoss, Katie E.; Keen, Richard; Fang, Shona; Zygouras, Alexandros; Javaid, Muhammad K.; Geberhiwot, Tarekegn; Poole, Kenneth E. S.; Selby, Peter; Walsh, Jennifer S.; Bubbear, Judith S.
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Long-term adherence to anti-osteoporosis medication and determinants of adherence in the population-based screening trial ROSE
err2025-02-24
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errOAAI
errPetersen, Tanja Gram; Rubin, Katrine Hass; Javaid, Muhammad Kassim; Hermann, Anne Pernille; Akesson, Kristina E.; Abrahamsen, Bo
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XLH Matters: an evolving programme to discuss new advances and share clinical experiences to improve patient outcomes
err2025-02-03
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errOAAI
errSeefried, Lothar; Aliberti, Ferdinando; Heier, Cathrine Alsaker; Arango-Sancho, Pedro; Biosse Duplan, Martin; Sakka, Sophia D.; Emma, Francesco; Gardiner, Oliver; Javaid, Muhammad Kassim; Ferreira-Santos, Rui M.; Raimann, Adalbert; Rak, Kristen; Bubbear, Judith S.; Cheung, Moira S.; Beck-Nielsen, Signe Sparre; Mindler, Gabriel T.; Linglart, Agnes
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Assessing and Managing Primary Hyperparathyroidism and Fracture Risk in England: A Survey of Medical Professionals
err2025-01-28
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errOAAI
errSong, Kaiyang; Vijjhalwar, Rohit; Aye, Mo; Comninos, Alexander N.; Schini, Marian; Abbas, Afroze; Gittoes, Neil; Javaid, Muhammad Kassim
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Secure: A Prospective Long-Term Observational Study in Patients with Monoclonal Gammopathy of Undetermined Significance安全:一项前瞻性长期观察研究,研究对象为意义未明的单克隆丙种球蛋白病患者
errBLOOD
IF23.1
err2024-11-05
err0
PREAI
errRamasamy, Karthik; Knight, Elizabeth; Byun, Sulgi; Heartin, Earnest; Garvey, Victoria; Basu, Supratik; Stones, Jacqueline; Oakes, Roderick; Killingsworth, Grace; Nicholls, Patricia; Mahmood, Samiya; Bowcock, Stella; Ryan, Rachel; Essex, Sarah; Alfred, Arun; Collier, Dawn; De Soysa, Lally; Bradley, Rachel; Thomas-Dewing, Rowena; Cawley, Kathryn; Kaczmarski, Richard; Al-Obaidi, Magda; Cubos, Freter; Bomken, Charlotte; Stern, Simon; Elonen, Tiina; Raymode, Parizade; Chathurani, Dinusha; Jenkins, Louise; Bygrave, Ceri; Consuegra, Roberto Garcia; Harrison, Wendy; Willis, Fenella; Brouwer, Richard; Koshiaris, Constantinos; Vallance, Grant; Gamble, Vicki; Javaid, Kassim; Sadler, Ross; Pratt, Guy
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Pregnancy vitamin D supplementation and offspring bone mineral density in childhood follow-up of a randomized controlled trial孕期补充维生素d与子代骨密度儿童随访的随机对照试验
err2024-11-01
err2
errOAAI
errMoon, Rebecca; D'Angelo, Stefania; Curtis, Elizabeth; Ward, Kate; Crozier, Sarah R.; Schoenmakers, Inez; Javaid, M. Kassim; Bishop, Nicholas; Godfrey, Keith M.; Cooper, Cyrus; Harvey, Nicholas
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A Rare Case of Checkpoint Inhibitor-induced Myasthenia Gravis and Myositis Presenting Separately
err2024-10-08
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PREAI
errSmith, Sydney; Shah, Anvay; Shah, Vishrut; Liu, Cynthia; Hoffer, Colton; Javaid, Muhammad; Schiopu, Elena; Ciuro, Jordan
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Setrusumab for the treatment of osteogenesis imperfecta: 12-month results from the phase 2b asteroid studySettrusumab用于治疗成骨不全症: 2b期小行星研究的12个月结果
err2024-07-16
err8
PREAI
errGlorieux, Francis H.; Langdahl, Bente; Chapurlat, Roland; De Beur, Suzanne Jan; Sutton, Vernon Reid; Poole, Kenneth E. S.; Dahir, Kathryn M.; Orwoll, Eric S.; Willie, Bettina M.; Mikolajewicz, Nicholas; Zimmermann, Elizabeth; Hosseinitabatabaei, Seyedmahdi; Ominsky, Michael S.; Saville, Chris; Clancy, James; Macinnon, Alastair; Mistry, Arun; Javaid, Muhammad K.
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HEALTH-RELATED QUALITY OF LIFE IN ANTENATAL WOMEN WITH RHEUMATIC DISEASES: INSIGHTS USING PROMIS INSTRUMENTS FROM THE COVAD 2 DATASET与妊娠相关的生命质量在患有风湿性疾病孕妇中的研究:利用PROMIS量表从COVAD 2数据集中获得的见解
err2024-06-01
err0
PREAI
errAbe, S.; Li, Y.; Maroufy, V.; Andreoli, L.; Ghosh, S.; Nikiphorou, E.; Javaid, M.; Gracia-Ramos, A. E.; Shaharir, S. S.; Toro-Gutierrez, C. E.; Dzifa, D.; Aggarwal, R.; Agarwal, V.; Gupta, L.
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Ten-year follow-up of fracture risk in a systematic populationbased screening program: the risk-strati fi ed osteoporosis strategy evaluation (ROSE) randomised trial基于人群的系统性筛查项目中骨折风险的10年随访: 风险分层骨质疏松症策略评估 (ROSE) 随机试验
err2024-05-01
err1
errOAAI
errPetersen, Tanja Gram; Abrahamsen, Bo; Heiberg, Mikkel; Rothmann, Mette Juel; Holmberg, Teresa; Gram, Jeppe; Bech, Mickael; Akesson, Kristina E.; Javaid, M. Kassim; Hermann, Anne Pernille; Rubin, Katrine Hass
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