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Longitudinal GGT trajectories identify prognostic phenotypes in paediatric primary sclerosing cholangitis 纵向GGT轨迹可识别儿童原发性硬化性胆管炎的预后表型 Denier, Daniela; Peng, Yiming (Emmett); Amin, Mansi; Aumar, Madeleine; Auth, Marcus; Fagundes, Eleonora Druve Tavares; El-Matary, Wael; Ferreira, Alexandre R.; Furuya, Katryn N.; Gupta, Nitika; Guthery, Stephen; Horslen, Simon; Jensen, M. Kyle; Kamath, Binita M.; Koot, Bart G. P.; Loomes, Kathleen M.; Mack, Cara; Martinez, Mercedes; Ovchinsky, Nadia; Papadopoulou, Alexandra; Perito, Emily R.; Sathya, Pushpa; Stevens, James P.; Tessier, M. Elizabeth; Valentino, Pamela; Deneau, Mark; Liu, Kuan; Ricciuto, Amanda 分享 收藏
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Transcriptional analysis of murine biliary atresia identifies macrophage heterogeneity and subset-specific macrophage functions Gromer, Kyle D.; Chen, Shang-Yang; Gadhvi, Gaurav; Feng, Liang; Shearn, Colin; Antala, Swati; Wechsler, Joshua B.; Cuda, Carla M.; Mack, Cara L.; Sokol, Ronald J.; Janssen, William J.; Green, Richard M.; Perlman, Harris; Winter, Deborah R.; Taylor, Sarah A. 分享 收藏
Increased serum GM-CSF at diagnosis of biliary atresia is associated with improved biliary drainage Taylor, Sarah A.; Harpavat, Sanjiv; Gromer, Kyle D.; Andreev, Victor; Loomes, Kathleen M.; Bezerra, Jorge A.; Jarasvaraparn, Chaowapong; Wang, Kasper; Horslen, Simon; Rosenthal, Philip; Teckman, Jeffrey; Valentino, Pamela L.; Ng, Vicky L.; Karpen, Saul J.; Sokol, Ronald J.; Alonso, Estella M.; Mack, Cara L. 分享 收藏
Biliary atresia Tam, Paul K. H.; Wells, Rebecca G.; Tang, Clara S. M.; Lui, Vincent C. H.; Hukkinen, Maria; Luque, Carlos D.; De Coppi, Paolo; Mack, Cara L.; Pakarinen, Mikko; Davenport, Mark 分享 收藏
Oral vancomycin is associated with improved inflammatory bowel disease clinical outcomes in primary sclerosing cholangitis-associated inflammatory bowel disease (PSC-IBD): A matched analysis from the Paediatric PSC Consortium Ricciuto, Amanda; Liu, Kuan; El-Matary, Wael; Amin, Mansi; Amir, Achiya Z.; Aumar, Madeleine; Auth, Marcus; Di Guglielmo, Matthew D.; Druve Tavares Fagundes, Eleonora; Rodrigues Ferreira, Alexandre; Furuya, Katryn N.; Gupta, Nitika; Guthery, Stephen; Horslen, Simon P.; Jensen, Kyle; Kamath, Binita M.; Kerkar, Nanda; Koot, B. G. P.; Laborda, Trevor J.; Lee, Christine K.; Loomes, Kathleen M.; Mack, Cara; Martinez, Mercedes; Montano-Loza, Aldo; Ovchinsky, Nadia; Papadopoulou, Alexandra; Perito, Emily R.; Sathya, Pushpa; Schwarz, Kathleen B.; Shah, Uzma; Shteyer, Eyal; Soufi, Nisreen; Stevens, James Patrick; Taylor, Amy; Tessier, M. Elizabeth; Valentino, Pamela; Woynarowski, Marek; Deneau, Mark 分享 收藏
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Interim results from an ongoing, open-label, single-arm trial of odevixibat in progressive familial intrahepatic cholestasis 正在进行的odevixibat治疗进行性家族性肝内胆汁淤积症的开放标签单臂试验的中期结果 Thompson, Richard J.; Artan, Reha; Baumann, Ulrich; Calvo, Pier Luigi; Czubkowski, Piotr; Dalgic, Buket; D'Antiga, Lorenzo; Di Giorgio, Angelo; Durmaz, Ozlem; Gonzales, Emmanuel; Grammatikopoulos, Tassos; Gupte, Girish; Hardikar, Winita; Houwen, Roderick H. J.; Kamath, Binita M.; Karpen, Saul J.; Lacaille, Florence; Lachaux, Alain; Lainka, Elke; Loomes, Kathleen M.; Mack, Cara L.; Mattsson, Jan P.; Mckiernan, Patrick; Ni, Quanhong; Ozen, Hasan; Rajwal, Sanjay R.; Roquelaure, Bertrand; Shteyer, Eyal; Sokal, Etienne; Sokol, Ronald J.; Soufi, Nisreen; Sturm, Ekkehard; Tessier, Mary Elizabeth; van der Woerd, Wendy L.; Verkade, Henkjan J.; Vittorio, Jennifer M.; Wallefors, Terese; Warholic, Natalie; Yu, Qifeng; Horn, Patrick; Kjems, Lise 分享 收藏
Cytomegalovirus in biliary atresia is associated with increased pretransplant death, but not decreased native liver survival Kemme, Sarah; Canniff, Jennifer D.; Feldman, Amy G.; Garth, Krystle M.; Li, Shaobing; Pan, Zhaoxing; Sokol, Ronald J.; Weinberg, Adriana; Mack, Cara L. 分享 收藏
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Odevixibat treatment in progressive familial intrahepatic cholestasis: a randomised, placebo-controlled, phase 3 trial Odevixibat治疗进行性家族性肝内胆汁淤积症: 一项随机,安慰剂对照,3期试验 Thompson, Richard J.; Arnell, Henrik; Artan, Reha; Baumann, Ulrich; Calvo, Pier Luigi; Czubkowski, Piotr; Dalgic, Buket; D'Antiga, Lorenzo; Durmaz, Ozlem; Fischler, Bjorn; Gonzales, Emmanuel; Grammatikopoulos, Tassos; Gupte, Girish; Hardikar, Winita; Houwen, Roderick H. J.; Kamath, Binita M.; Karpen, Saul J.; Kjems, Lise; Lacaille, Florence; Lachaux, Alain; Lainka, Elke; Mack, Cara L.; Mattsson, Jan P.; McKiernan, Patrick; Ozen, Hasan; Rajwal, Sanjay R.; Roquelaure, Bertrand; Shagrani, Mohammad; Shteyer, Eyal; Soufi, Nisreen; Sturm, Ekkehard; Tessier, Mary Elizabeth; Verkade, Henkjan J.; Horn, Patrick 分享 收藏
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Impact of long-term administration of maralixibat on children with cholestasis secondary to Alagille syndrome Shneider, Benjamin L.; Spino, Catherine A.; Kamath, Binita M.; Magee, John C.; Ignacio, Rosalinda, V; Huang, Suiyuan; Horslen, Simon P.; Molleston, Jean P.; Miethke, Alexander G.; Kohli, Rohit; Leung, Daniel H.; Jensen, M. Kyle; Loomes, Kathleen M.; Karpen, Saul J.; Mack, Cara; Rosenthal, Philip; Squires, Robert H.; Baker, Alastair; Rajwal, Sanjay; Kelly, Deirdre; Sokol, Ronald J.; Thompson, Richard J. 分享 收藏
Maralixibat for the treatment of PFIC: Long-term, IBAT inhibition in an open-label, Phase 2 study Maralixibat治疗PFIC: 开放标签,2期研究中的长期IBAT抑制 Loomes, Kathleen M.; Squires, Robert H.; Kelly, Deirdre; Rajwal, Sanjay; Soufi, Nisreen; Lachaux, Alain; Jankowska, Irena; Mack, Cara; Setchell, Kenneth D. R.; Karthikeyan, Palaniswamy; Kennedy, Ciara; Dorenbaum, Alejandro; Desai, Nirav K.; Garner, Will; Jaecklin, Thomas; Vig, Pamela; Miethke, Alexander; Thompson, Richard J. 分享 收藏
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