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Impact of Fidanacogene Elaparvovec Gene Therapy on Joint Health in Adults With Haemophilia B: Results From a Phase 3 Study Fidanacogene Elaparvovec基因疗法对血友病B成人患者关节健康的影响:一项3期研究的结果 Matino, Davide; Frenzel, Laurent; Antmen, Ali Bulent; Astermark, Jan; Cerqueira, Monica H.; Cuker, Adam; Katsarou-Fasouli, Olga; Kavakli, Kaan; Ozelo, Margareth C.; P'ng, Stephanie; Wang, Jiaan-der; Agathon, Delphine; Biondo, Francesca; Klaus, Pascal; McKay, John; Rupon, Jeremy; Sun, Pengling; Wilcox, Lisa J.; Plonski, Frank 分享 收藏
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Outcomes and management of invasive procedures in participants with hemophilia A post gene therapy: a post hoc analysis of the GENEr8-1 phase III trial Quon, Doris V.; Wang, Jiaan-Der; Wang, Michael; Pepperell, Dominic; Park, Young-Shil; Kenet, Gili; Mahlangu, Johnny; Khoo, Teh-Liane; Robinson, Tara M.; Chavele, Konstantia-Maria; Pipe, Steven W. 分享 收藏
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Recapitulating the immune system of hemophilia A patients with inhibitors using immunodeficient mice Chou, Sheng-Chieh; Yen, Ching-Tzu; Yang, Yung-Li; Chen, Shu-Huey; Wang, Jiaan-Der; Fan, Meng -Ni; Chen, Li -Fu; Yu, I-Shing; Tsai, Dong-Yan; Lin, Kuo-, I; Tao, Mi -Hua; Wu, Jui-ching; Lin, Shu-Wha 分享 收藏
Health-related quality of life following valoctocogene roxaparvovec gene therapy for severe hemophilia A in the phase 3 trial GENEr8-1 在3期试验GENEr8-1中,valocologene roxaparvovec基因治疗严重血友病A后的健康相关生活质量 O'Mahony, Brian; Dunn, Amy L.; Leavitt, Andrew D.; Peyvandi, Flora; Ozelo, Margareth C.; Mahlangu, Johnny; Peerlinck, Kathelijne; Wang, Jiaan-Der; Lowe, Gillian C.; Tan, Chee Wee; Giermasz, Adam; Tran, Huyen; Khoo, Teh -Liane; Cockrell, Erin; Pepperell, Dominic; Chambost, Herve; Lopez Fernandez, Maria Fernanda; Kazmi, Rashid; Majerus, Elaine; Skinner, Mark W.; Klamroth, Robert; Quinn, Jennifer; Yu, Hua; Wong, Wing Yen; Robinson, Tara M.; Pipe, Steven W. 分享 收藏
DHA alleviated hepatic and adipose inflammation with increased adipocyte browning in high-fat diet-induced obese mice Lin, Shih-Yi; Wang, Ya-Yu; Pan, Pin-Ho; Wang, Jiaan-Der; Yang, Ching-Ping; Chen, Wen-Ying; Kuan, Yu-Hsiang; Liao, Su-Lan; Lo, Yu-Li; Chang, Yih-Hsin; Chen, Chun-Jung 分享 收藏
Efficacy, safety and cost of emicizumab prophylaxis in haemophilia A patients with inhibitors: A nationwide observational study in Taiwan emicizumab预防使用抑制剂的a型血友病患者的疗效,安全性和成本: 台湾的一项全国性观察性研究 Shen, Ming-Ching; Chou, Sheng-Chieh; Chiou, Shyh-Shin; Lin, Pei-Chin; Chen, Yeu-Chin; Lin, Hsuan-Yu; Lee, Yang-Cheng; Huang, Cih-En; Weng, Te-Fu; Huang, Ting-Huan; Chung, Chih-Yuan; Chen, Jiann-Shiuh; Chen, Shu-Huey; Cheng, Shin-Nan; Hsiao, Chih-Cheng; Huang, Yen-Min; Chen, Shih-Hsiang; Yu, Yuan-Bin; Lin, Shih-Chiang; Lin, Ching-Yeh; Peng, Ching-Tien; Wang, Jiaan-Der 分享 收藏
NMDA receptor inhibitor MK801 alleviated pro-inflammatory polarization of BV-2 microglia cells Wu, Chih-Cheng; Tzeng, Chung-Yuh; Chang, Cheng-Yi; Wang, Jiaan-Der; Chen, Yu-Fang; Chen, Wen-Ying; Kuan, Yu-Hsiang; Liao, Su-Lan; Wang, Wen-Yi; Chen, Chun-Jung 分享 收藏
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