未登录Adults With Acid Sphingomyelinase Deficiency Have Sustained Improvements in Clinical Outcomes With up to 5 Years of Olipudase Alfa Enzyme Replacement Therapy: ASCEND Trial Final Results成人鞘磷脂酶缺乏症患者经Olipudase Alfa酶替代疗法治疗5年后临床结局持续改善:ASCEND试验最终结果
Wasserstein, Melissa P.; Hollak, Carla E.; Barbato, Antonio; Gallagher, Renata C.; Giugliani, Roberto; Guelbert, Norberto Bernardo; Hennermann, Julia B.; Ikezoe, Takayuki; Lachmann, Robin; Lidove, Olivier; Mabe, Paulina; Mengel, Eugen; Scarpa, Maurizio; Senates, Ebubekir; Tchan, Michel; Thurberg, Beth L.; Villarrubia, Jesus; Armstrong, Nicole M.; Bhushan, Shashi; Kim, Yong; Kumar, Monica
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收藏Assisting the Diagnosis of Cirrhosis in Chronic Hepatitis C Patients Based on Machine Learning Algorithms: A Novel Non-Invasive Approach基于机器学习算法协助诊断慢性丙型肝炎患者肝硬化:一种新颖的无创方法
Dirican, Emre; Bal, Tayibe; Onlen, Yusuf; Sarigul, Figen; User, Ulku; Sari, Nagehan Didem; Kurtaran, Behice; Senates, Ebubekir; Gunduz, Alper; Zerdali, Esra; Karsen, Hasan; Batirel, Ayse; Karaali, Ridvan; Guner, Hatice Rahmet; Yamazhan, Tansu; Kose, Sukran; Erben, Nurettin; Ince, Nevin Koc; Koksal, Iftihar; Oztoprak, Nefise; Yoruk, Gulsen; Komur, Suheyla; Kaya, Sibel Yildiz; Bozkurt, Ilkay; Gunal, Ozgur; Yildiz, Ilknur Esen; Inan, Dilara; Barut, Sener; Namiduru, Mustafa; Tosun, Selma; Turker, Kamuran; Sener, Alper; Hizel, Kenan; Baykam, Nurcan; Duygu, Fazilet; Bodur, Hurrem; Can, Guray; Gul, Hanefi Cem; Tartar, Ayse Sagmak; Celebi, Guven; Sunnetcioglu, Mahmut; Karabay, Oguz; Karaosmanoglu, Hayat Kumbasar; Sirmatel, Fatma; Tabak, Omer Fehmi
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收藏Final results of the ASCEND trial: Continued or sustained improvements in hepatosplenomegaly, respiratory outcomes, and lipid profile after 4 years of olipudase alfa enzyme replacement therapy in adults with acid sphingomyelinase deficiency
Wasserstein, Melissa; Gallagher, Renata C.; Barbato, Antonio; Guigliani, Roberto; Guelbert, Norberto; Hennermann, Julia B.; Ikezoe, Takayuki; Lachmann, Robin; Lidove, Olivier; Mabe, Paulina; Mengel, Eugen; Scarpa, Maurizio; Senates, Ebubekir; Tchan, Michel; Villarrubia, Jesus; Thurberg, Beth L.; Armstrong, Nicole M.; Srivastav, Shruti; Wisniewska, Urszula; Kumar, Monica
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收藏Continued improvement in disease manifestations of acid sphingomyelinase deficiency for adults with up to 2 years of olipudase alfa treatment: open-label extension of the ASCEND trial
Wasserstein, Melissa P.; Lachmann, Robin; Hollak, Carla; Barbato, Antonio; Gallagher, Renata C.; Giugliani, Roberto; Guelbert, Norberto Bernardo; Hennermann, Julia B.; Ikezoe, Takayuki; Lidove, Olivier; Mabe, Paulina; Mengel, Eugen; Scarpa, Maurizio; Senates, Ebubekir; Tchan, Michel; Villarrubia, Jesus; Thurberg, Beth L.; Yarramaneni, Abhimanyu; Armstrong, Nicole M.; Kim, Yong; Kumar, Monica
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收藏Continued improvement in adults with acid sphingomyelinase deficiency after 2 years of olipudase alfa in the ASCEND placebo-controlled trial
Wasserstein, Melissa; Barbato, Antonio; Gallagher, Renata; Giugliani, Roberto; Guelbert, Norberto; Hennermann, Julia; Hollak, Carla; Ikezoe, Takayuki; Lachmann, Robin; Lidove, Olivier; Mabe, Paulina; Mengel, Eugen; Scarpa, Maurizio; Senates, Ebubekir; Tchan, Michel; Villarrubia, Jesus; Thurberg, Beth; Yarramaneni, Abhimanyu; Rawlings, Andreea; Kim, Yong; Kumar, Monica
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收藏Two-year results of the ASCEND trial of olipudase alfa adults with chronic acid sphingomyelinase deficiency show parallel improvements in former placebo patients and further improvement in continuing olipudase alfa patients
Wasserstein, Melissa P.; Barbato, Antonio; Gallagher, Renata C.; Giugliani, Roberto; Guelbert, Norberto B.; Hennermann, Julia B.; Hollak, Carla; Ikezoe, Takayuki; Lachmann, Robin; Lidove, Olivier; Mabe, Paulina; Mengel, Eugen; Scarpa, Maurizio; Senates, Ebubekir; Tchan, Michel; Villarrubia, Jesus; Thurberg, Beth L.; Yarramaneni, Abhimanyu; Rawling, Andreea M.; Kim, Yong; Kumar, Monica
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收藏Adults with chronic acid sphingomyelinase deficiency show significant visceral, pulmonary, and hematologic improvements after enzyme replacement therapy with olipudase-alfa: 1-year results of the ASCEND placebo-controlled trial
Wasserstein, Melissa; Arash-Kaps, Laila; Barbato, Antonio; Gallagher, Renata C.; Giugliani, Roberto; Guelbert, Norberto B.; Hollak, Carla; Ikezoe, Takayuki; Lachmann, Robin; Lidove, Oliver; Mabe, Paulina; Mengel, Eugen; Scarpa, Maurizio; Senates, Ebubekir; Tchan, Michel; Villarrubia, Jesus; Chen, Yixin; Fraser, Patricia A.; Thurberg, Beth L.; Zaher, Atef; Kumar, Monica
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收藏Impaired Gallbladder Motility and Increased Gallbladder Wall Thickness in Patients with Nonalcoholic Fatty Liver Disease
Colak, Yasar; Bozbey, Gulcin; Erim, Tolga; Caklili, Ozge Telci; Ulasoglu, Celal; Senates, Ebubekir; Mutlu, Hasan Huseyin; Mesci, Banu; Dogan, Mehmet Sait; Tasan, Guralp; Enc, Feruze Yilmaz; Tuncer, Ilyas
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收藏Serum osteopontin levels as a predictor of portal inflammation in patients with nonalcoholic fatty liver disease
Yilmaz, Yusuf; Ozturk, Oguzhan; Alandab, Yesim Ozen; Senates, Ebubekir; Colak, Yasar; Doganay, Hamdi Levent; Coskunpinar, Ender; Oltulu, Yasemin Musteri; Eren, Fatih; Atug, Ozlen; Tuncer, Ilyas; Imeryuz, Nese
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收藏Assessment of endothelial function in patients with nonalcoholic fatty liver disease
Colak, Yasar; Senates, Ebubekir; Yesil, Atakan; Yilmaz, Yusuf; Ozturk, Oguzhan; Doganay, Levent; Coskunpinar, Ender; Kahraman, Ozlem Timirci; Mesci, Banu; Ulasoglu, Celal; Tuncer, Ilyas
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收藏Circulating vaspin levels and epicardial adipose tissue thickness are associated with impaired coronary flow reserve in patients with nonalcoholic fatty liver disease
Yilmaz, Yusuf; Kurt, Ramazan; Gurdal, Ahmet; Alahdab, Yesim Ozen; Yonal, Oya; Senates, Ebubekir; Polat, Nihat; Eren, Fatih; Imeryuz, Nese; Oflaz, Huseyin
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