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Efficacy and safety of mitapivat in adults with transfusion-dependent α-thalassaemia or β-thalassaemia (ENERGIZE-T): a double-blind, randomised, multicentre, placebo-controlled, phase 3trial 米塔匹泛在依赖输血的α-地中海贫血或β-地中海贫血成人中的有效性和安全性(ENERGIZE-T):一项双盲、随机、多中心、安慰剂对照、III期临床试验 Cappellini, Maria Domenica; Sheth, Sujit; Taher, Ali; Al-Samkari, Hanny; Antmen, Ali Bulent; Beneitez, David; Cannas, Giovanna; Coates, Thomas; Czapla, Lauren; Dahlin, Jayme L.; Estepp, Jeremie H.; Feenstra, Elizabeth; Georgiev, Pencho; Gheuens, Sarah; Price, Gavrielle M.; Glenthoj, Andreas; Musallam, Khaled M.; Osman, Kareem; Porter, John B.; Shao, Hui; Uhlig, Katrin; Beers, Eduard J. van; Viprakasit, Vip; Kuo, Kevin H. M.; Kattamis, Antonis 分享 收藏
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Prospective collection of bleeding rate and factor usage in participants with hemophilia A and B in a noninvestigational product study 在非研究性产品研究中对血友病A和B患者出血率和因子使用情况进行前瞻性收集 Kavakli, Kaan; Frenzel, Laurent; Antmen, Ali Bulent; Alzahrani, Hazzaa; Matino, Davide; Leavitt, Andrew D.; Ozelo, Margareth C.; Astermark, Jan; Park, Young-Shil; Klamroth, Robert; Cuker, Adam; Konkle, Barbara A.; McKay, John; Agathon, Delphine; Tseng, Li-Jung; Resa, Maria de los Angeles; Healy, Jasmine; Wilcox, Lisa J.; Plonski, Frank 分享 收藏
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Impact of Fidanacogene Elaparvovec Gene Therapy on Joint Health in Adults With Haemophilia B: Results From a Phase 3 Study Fidanacogene Elaparvovec基因疗法对血友病B成人患者关节健康的影响:一项3期研究的结果 Matino, Davide; Frenzel, Laurent; Antmen, Ali Bulent; Astermark, Jan; Cerqueira, Monica H.; Cuker, Adam; Katsarou-Fasouli, Olga; Kavakli, Kaan; Ozelo, Margareth C.; P'ng, Stephanie; Wang, Jiaan-der; Agathon, Delphine; Biondo, Francesca; Klaus, Pascal; McKay, John; Rupon, Jeremy; Sun, Pengling; Wilcox, Lisa J.; Plonski, Frank 分享 收藏
Effect of genetic mutations on outcomes of stem cell transplantation in children with hemophagocytic lymphohistiocytosis 遗传突变对噬血细胞性淋巴组织细胞增多症儿童干细胞移植结局的影响 Ozturk, Gulyuz; Yesilipek, Mehmet Akif; Akcay, Arzu; Uygun, Vedat; Ozek, Gulcihan; Karasu, Gulsun; Yilmaz, Ebru; Yenigurbuz, Fatma Demir; Ozturkmen, Seda; Aksoylar, Serap; Bozkaya, Ikbal Ok; Yalcin, Koray; Aksoy, Basak Adakli; Unal, Ekrem; Akinci, Burcu; Daloglu, Hayriye; Karagun, Barbaros Sahin; Kansoy, Savas; Ozbek, Namik; Ince, Elif; Demir, Haci Ahmet; Gundogdu, Muge; Malbora, Baris; Karakukcu, Musa; Elli, Murat; Akyay, Arzu; Gunes, Adalet Meral; Akbayram, Sinan; Sarper, Nazan; Del Castello, Buket Erer; Hazar, Volkan; Antmen, Bulent 分享 收藏
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Ruxolitinib in treatment-naive or corticosteroid-refractory paediatric patients with chronic graft-versus-host disease (REACH5): interim analysis of a single-arm, multicentre, phase 2 study Locatelli, Franco; Antmen, Bulent; Kang, Hyoung Jin; Koh, Katsuyoshi; Takahashi, Yoshiyuki; Kupesiz, Alphan; Matos, Maria Gabriela A. Dias; Chopra, Yogi; Bhat, Sunil; Im, Ho Joon; Guengoer, Tayfun; Lu, Meng-Yao; Stefanelli, Tommaso; Rosko, Christine; St Pierre, Annie; Burock, Karin; Smith, Yvonne; Sinclair, Karen; Diaz-de-Heredia, Cristina 分享 收藏
Gene therapy in haemophilia: literature review and regional perspectives for Turkey Kavakli, Kaan; Antmen, Bulent; Okan, Vahap; Sahin, Fahri; Aytac, Selin; Balkan, Can; Berber, Ergul; Kaya, Zuhre; Kupesiz, Alphan; Zulfikar, Bulent 分享 收藏
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Different Kinetics and Risk Factors for Isolated Extramedullary Relapse after Allogeneic Hematopoietic Stem Cell Transplantation in Children with Acute Leukemia 儿童急性白血病异基因造血干细胞移植后孤立性髓外复发的不同动力学及危险因素 Hazar, Volkan; Ozturk, Gulyuz; Yalcin, Koray; Uygun, Vedat; Aksoylar, Serap; Kupesiz, A.; Bozkaya, Ikbal Ok; Karagun, Barbaros Sahin; Bozkurt, Ceyhun; Ileri, Talia; Atay, Didem; Kocak, Ulker; Karasu, Gulsun Tezcan; Yesilipek, Akif; Gokce, Muge; Kansoy, Savas; Kintrup, Gulen Tuysuz; Karakukcu, Musa; Okur, Fatma Visal; Ertem, Mehmet; Kaya, Zuhre; Gursel, Orhan; Yaman, Yontem; Ozbek, Namik; Antmen, Bulent; Tufekci, Ozlem; Albayrak, Canan; Aksoy, Basak Adakli; Sezgin, Gulay; Albayrak, Davut; Evim, Melike Sezgin; Zengin, Emine; Pekpak, Esra 分享 收藏
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Stem cell transplantation for congenital dyserythropoietic anemia: an analysis from the European Society for Blood and Marrow Transplantation Miano, Maurizio; Eikema, Dirk-Jan; Aljurf, Mahmoud; van't Veer, Pieter J.; Ozturk, Gulyuz; Wolfl, Matthias; Smiers, Frans; Schulz, Angsar; Socie, Gerard; Vettenranta, Kim; Diaz de Heredia, Cristina; Zecca, Marco; Maertens, Johan; Rovira, Montserrat; Sierra, Jorge; Uckan-Cetinkaya, Duygu; Skorobogatova, Elena; Antmen, Ali Bulent; Dalle, Jean-Hugues; Markiewicz, Miroslaw; Hamladji, Rose Marie; Kitra-Roussou, Vassiliki; La Nasa, Giorgio; Krivan, Gergely; Al-Seiraihy, Amal; Giardino, Stefano; Risitano, Antonio Maria; de Latour, Regis Peffault; Dufour, Carlo 分享 收藏
A Randomized Trial of Factor VIII and Neutralizing Antibodies in Hemophilia A Peyvandi, F.; Mannucci, P. M.; Garagiola, I.; El-Beshlawy, A.; Elalfy, M.; Ramanan, V.; Eshghi, P.; Hanagavadi, S.; Varadarajan, R.; Karimi, M.; Manglani, M. V.; Ross, C.; Young, G.; Seth, T.; Apte, S.; Nayak, D. M.; Santagostino, E.; Mancuso, M. E.; Sandoval Gonzalez, A. C.; Mahlangu, J. N.; Bonanad Boix, S.; Cerqueira, M.; Ewing, N. P.; Male, C.; Owaidah, T.; Soto Arellano, V.; Kobrinsky, N. L.; Majumdar, S.; Perez Garrido, R.; Sachdeva, A.; Simpson, M.; Thomas, M.; Zanon, E.; Antmen, B.; Kavakli, K.; Manco-Johnson, M. J.; Martinez, M.; Marzouka, E.; Mazzucconi, M. G.; Neme, D.; Palomo Bravo, A.; Paredes Aguilera, R.; Prezotti, A.; Schmitt, K.; Wicklund, B. M.; Zulfikar, B.; Rosendaal, F. R. 分享 收藏
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Health-related quality of life in patients with haemophilia and inhibitors on prophylaxis with anti-inhibitor complex concentrate: results from the Pro-FEIBA study Gringeri, A.; Leissinger, C.; Cortesi, P. A.; Jo, H.; Fusco, F.; Riva, S.; Antmen, B.; Berntorp, E.; Biasoli, C.; Carpenter, S.; Kavakli, K.; Morfini, M.; Negrier, C.; Rocino, A.; Schramm, W.; Windyga, J.; Zulfikar, B.; Mantovani, L. G. 分享 收藏