未登录Long-term safety and efficacy of lecanemab in early Alzheimer's disease: Results from the clarity AD open-label extension study利卡奈玛单抗在早期阿尔茨海默病中的长期安全性与有效性:来自Clarity AD开放标签扩展研究的结果
Van Dyck, Christopher H.; Sperling, Reisa; Johnson, Keith; Dhadda, Shobha; Kanekiyo, Michio; Li, David; Gee, Michelle; Hersch, Steven; Irizarry, Michael; Kramer, Lynn
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收藏A natural history study to track brain and spinal cord changes in individuals with Friedreich's ataxia: TRACK-FA study protocol ( vol 17 ,e0269649 , 2022)一项追踪弗里德赖希共济失调症患者脑部和脊髓变化的自然病史研究:TRACK-FA研究方案(卷17,e0269649,2022)
Georgiou-Karistianis, Nellie; Corben, Louise A.; Reetz, Kathrin; Adanyeguh, Isaac M.; Corti, Manuela; Deelchand, Dinesh K.; Delatycki, Martin B.; Dogan, Imis; Evans, Rebecca; Farmer, Jennifer; Franca, Marcondes C.; Gaetz, William; Harding, Ian H.; Harris, Karen S.; Hersch, Steven; Joules, Richard; Joers, James J.; Krishnan, Michelle L.; Lax, Michelle; Lock, Eric F.; Lynch, David; Mareci, Thomas; Gamage, Sahan Muthuhetti; Pandolfo, Massimo; Papoutsi, Marina; Rezende, Thiago J. R.; Roberts, Timothy P. L.; Rosenberg, Jens T.; Romanzetti, Sandro; Schulz, Jorg B.; Schilling, Traci; Schwarz, Adam J.; Subramony, Sub; Yao, Bert; Zicha, Stephen; Lenglet, Christophe; Henry, Pierre-Gilles
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收藏A natural history study to track brain and spinal cord changes in individuals with Friedreich's ataxia: TRACK-FA study protocol (vol 17, e0269649, 2022)一项追踪弗里德赖希共济失调症患者脑和脊髓变化的自然史研究:TRACK-FA研究方案(卷17,e0269649,2022)
Georgiou-Karistianis, Nellie; Corben, Louise A.; Reetz, Kathrin; Adanyeguh, Isaac M.; Corti, Manuela; Deelchand, Dinesh K.; Delatycki, Martin B.; Dogan, Imis; Evans, Rebecca; Farmer, Jennifer; Franca, Marcondes C.; Gaetz, William; Harding, Ian H.; Harris, Karen S.; Hersch, Steven; Joules, Richard; Joers, James J.; Krishnan, Michelle L.; Lax, Michelle; Lock, Eric F.; Lynch, David; Mareci, Thomas; Gamage, Sahan Muthuhetti; Pandolfo, Massimo; Papoutsi, Marina; Rezende, Thiago J. R.; Roberts, Timothy P. L.; Rosenberg, Jens T.; Romanzetti, Sandro; Schulz, Joerg B.; Schilling, Traci; Schwarz, Adam J.; Subramony, Sub; Yao, Bert; Zicha, Stephen; Lenglet, Christophe; Henry, Pierre-Gilles
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收藏Updated safety results from phase 3 lecanemab study in early Alzheimer's disease (vol 16, 105, 2024)
Honig, Lawrence S.; Sabbagh, Marwan N.; van Dyck, Christopher H.; Sperling, Reisa A.; Hersch, Steven; Matta, Andre; Giorgi, Luigi; Gee, Michelle; Kanekiyo, Michio; Li, David; Purcell, Derk; Dhadda, Shobha; Irizarry, Michael; Kramer, Lynn
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收藏Updated safety results from phase 3 lecanemab study in early Alzheimer's disease早期阿尔茨海默病3期lecanemab研究的最新安全性结果
Honig, Lawrence S.; Sabbagh, Marwan N.; van Dyck, Christopher H.; Sperling, Reisa A.; Hersch, Steven; Matta, Andre; Giorgi, Luigi; Gee, Michelle; Kanekiyo, Michio; Li, David; Purcell, Derk; Dhadda, Shobha; Irizarry, Michael; Kramer, Lynn
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收藏Lecanemab Clarity AD: Quality-of-Life Results from a Randomized, Double-Blind Phase 3 Trial in Early Alzheimer's DiseaseLecanemab Clarity AD: 早期阿尔茨海默病随机双盲3期试验的生活质量结果
Cohen, Sharon; van Dyck, C. H.; Gee, M.; Doherty, T.; Kanekiyo, M.; Dhadda, S.; Li, D.; Hersch, S.; Irizarry, M.; Kramer, L. D.
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收藏Safety and Tolerability of SRX246, a Vasopressin 1a Antagonist, in Irritable Huntington's Disease Patients-A Randomized Phase 2 Clinical Trial加压素1a拮抗剂SRX246在易激惹亨廷顿舞蹈病患者中的安全性和耐受性-一项随机2期临床试验
Brownstein, Michael J.; Simon, Neal G.; Long, Jeffrey D.; Yankey, Jon; Maibach, Hilda T.; Cudkowicz, Merit; Coffey, Christopher; Conwit, Robin A.; Lungu, Codrin; Anderson, Karen E.; Hersch, Steven M.; Ecklund, Dixie J.; Damiano, Eve M.; Itzkowitz, Debra E.; Lu, Shifang; Chase, Marianne K.; Shefner, Jeremy M.; McGarry, Andrew; Thornell, Brenda; Gladden, Catherine; Costigan, Michele; O'Suilleabhain, Padraig; Marshall, Frederick J.; Chesire, Amy M.; Deritis, Paul; Adams, Jamie L.; Hedera, Peter; Lowen, Kelly; Rosas, H. Diana; Hiller, Amie L.; Quinn, Joseph; Keith, Kellie; Duker, Andrew P.; Gruenwald, Christina; Molloy, Angela; Jacob, Cara; Factor, Stewart; Sperin, Elaine; Bega, Danny; Brown, Zsazsa R.; Seeberger, Lauren C.; Sung, Victor W.; Benge, Melanie; Kostyk, Sandra K.; Daley, Allison M.; Perlman, Susan; Suski, Valerie; Conlon, Patricia; Barrett, Matthew J.; Lowenhaupt, Stephanie; Quigg, Mark; Perlmutter, Joel S.; Wright, Brenton A.; Most, Elaine; Schwartz, Guy J.; Lamb, Jessica; Chuang, Rosalind S.; Singer, Carlos; Marder, Karen; Moran, Joyce A.; Singleton, John R.; Zorn, Meghan; Wall, Paola V.; Dubinsky, Richard M.; Gray, Carolyn; Drazinic, Carolyn
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收藏Motor, cognitive, and functional declines contribute to a single progressive factor in early HD
Schobel, Scott A.; Palermo, Giuseppe; Auinger, Peggy; Long, Jeffrey D.; Ma, Shiyang; Khwaja, Omar S.; Trundell, Dylan; Cudkowicz, Merit; Hersch, Steven; Sampaio, Cristina; Dorsey, E. Ray; Leavitt, Blair R.; Kieburtz, Karl D.; Sevigny, Jeffrey J.; Langbehn, Douglas R.; Tabrizi, Sarah J.
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收藏KEAP1-modifying small molecule reveals muted NRF2 signaling responses in neural stem cells from Huntington's disease patients
Quinti, Luisa; Naidu, Sharadha Dayalan; Trager, Ulrike; Chen, Xiqun; Kegel-Gleason, Kimberly; Lleres, David; Connolly, Colum; Chopra, Vanita; Low, Cho; Moniot, Sebastien; Sapp, Ellen; Tousley, Adelaide R.; Vodicka, Petr; Van Kanegan, Michael J.; Kaltenbach, Linda S.; Crawford, Lisa A.; Fuszard, Matthew; Higgins, Maureen; Miller, James R. C.; Farmer, Ruth E.; Potluri, Vijay; Samajdar, Susanta; Meisel, Lisa; Zhang, Ningzhe; Snyder, Andrew; Stein, Ross; Hersch, Steven M.; Ellerby, Lisa M.; Weerapana, Eranthie; Schwarzschild, Michael A.; Steegborn, Clemens; Leavitt, Blair R.; Degterev, Alexei; Tabrizi, Sarah J.; Lo, Donald C.; DiFiglia, Marian; Thompson, Leslie M.; Dinkova-Kostova, Albena T.; Kazantsev, Aleksey G.
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