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J

John B. Porter

university college london hospitals

76H指数
707论文数
2.1W被引数
收录论文 121
发表时间
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Efficacy and safety of luspatercept in non-transfusion-dependent β-thalassemia: long-term results from the BEYOND studyluspaterecpt 在非输血依赖性β-地中海贫血中的有效性和安全性:BEYOND研究的长期能力结果
err2025-09-01
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errAli T. Taher; Vip Viprakasit; Antonis Kattamis; Silverio Perrotta; Paolo Ricchi; John B. Porter; Thomas D. Coates; Gian Luca Forni; Khaled M. Musallam; Oriana Esposito; Richard Pilot; Wen-Ling Kuo; Yinzhi Lai; Marta Reverte; Richard Wei; Luciana Moro Bueno; Maria Domenica Cappellini
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TIF Guidelines for the Management of Transfusion-Dependent β-Thalassemia输血依赖性β-地中海贫血管理指南
err2025-03-05
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errMusallam, Khaled M.; Cappellini, Maria Domenica; Porter, John B.; Farmakis, Dimitrios; Eleftheriou, Androulla; Angastiniotis, Michael
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Mitapivat improves ineffective erythropoiesis and iron overload in adult patients with pyruvate kinase deficiency
err2024-05-20
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errvan Beers, Eduard J.; Al-Samkari, Hanny; Grace, Rachael F.; Barcellini, Wilma; Glenthoj, Andreas; DiBacco, Melissa; Wind-Rotolo, Megan; Xu, Rengyi; Beynon, Vanessa; Patel, Parija; Porter, John B.; Kuo, Kevin H. M.
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Luspatercept stimulates erythropoiesis, increases iron utilization, and redistributes body iron in transfusion-dependent thalassemia
err2023-10-02
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errGarbowski, Maciej W.; Ugidos, Manuel; Risueno, Alberto; Shetty, Jeevan K.; Schwickart, Martin; Hermine, Olivier; Porter, John B.; Thakurta, Anjan; Vodala, Sadanand
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SLN124, a GalNAc conjugated 19-mer siRNA targeting tmprss6, reduces plasma iron and increases hepcidin levels of healthy volunteers
err2023-07-27
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errPorter, John B.; Scrimgeour, Alison; Martinez, Alberto; James, Leo; Aleku, Manuela; Wilson, Rosamund; Muckenthaler, Martina; Boyce, Malcolm; Wilkes, Denise; Schaeper, Ute; Campion, Giles V.
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Modified-release hydrocortisone is associated with lower plasma renin activity in patients with salt-wasting congenital adrenal hyperplasia
err2023-01-19
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errTschaidse, Lea; Reisch, Nicole; Arlt, Wiebke; de la Perriere, Aude Brac; Hirschberg, Angelica Linden; Juul, Anders; Mallappa, Ashwini; Merke, Deborah P.; Newell-Price, John D. C.; Perry, Colin G.; Prete, Alessandro; Rees, D. Aled; Stikkelbroeck, Nike M. M. L.; Touraine, Philippe A.; Coope, Helen; Porter, John; Ross, Richard John M.; Quinkler, Marcus
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Early-onset reduced bone mineral density in patients with pyruvate kinase deficiency
err2023-01-09
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errAl-Samkari, Hanny; Grace, Rachael F.; Glenthoj, Andreas; Andres, Oliver; Barcellini, Wilma; Galacteros, Frederic; Kuo, Kevin H. M.; Layton, D. Mark; Morado Arias, Marta; Viprakasit, Vip; Dong, Yan; Tai, Feng; Hawkins, Peter; Gheuens, Sarah; Morales-Arias, Jaime; Gilroy, Keely S.; Porter, John B.; van Beers, Eduard J.
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Effects of green tea extract treatment on erythropoiesis and iron parameters in iron-overloaded β-thalassemic mice
err2022-12-23
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errSettakorn, Kornvipa; Kongkarnka, Sarawut; Chompupoung, Anchan; Svasti, Saovaros; Fucharoen, Suthat; Porter, John B.; Srichairatanakool, Somdet; Koonyosying, Pimpisid
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Untreated Anemia in Nontransfusion-dependent β-thalassemia: Time to Sound the Alarm
err2022-12-01
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errMusallam, Khaled M. T.; Taher, Ali T.; Cappellini, Maria Domenica; Hermine, Olivier; Kuo, Kevin H. M.; Sheth, Sujit; Viprakasit, Vip B.; Porter, John B.
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Luspatercept for the treatment of anaemia in non-transfusion-dependent β-thalassaemia (BEYOND): a phase 2, randomised, double-blind, multicentre, placebo-controlled trial
err2022-10-01
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errTaher, Ali T.; Cappellini, Maria Domenica; Kattamis, Antonis; Voskaridou, Ersi; Perrotta, Silverio; Piga, Antonio G.; Filosa, Aldo; Porter, John B.; Coates, Thomas D.; Forni, Gian Luca; Thompson, Alexis A.; Tartaglione, Immacolata; Musallam, Khaled M.; Backstrom, Jay T.; Esposito, Oriana; Giuseppi, Ana Carolina; Kuo, Wen-Ling; Miteva, Dimana; Lord-Bessen, Jennifer; Yucel, Aylin; Zinger, Tatiana; Shetty, Jeevan K.; Viprakasit, Vip
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Mitapivat in adult patients with pyruvate kinase deficiency receiving regular transfusions (ACTIVATE-T): a multicentre, open-label, single-arm, phase 3 trial
err2022-10-01
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errGlenthoj, Andreas; van Beers, Eduard J.; Al-Samkari, Hanny; Viprakasit, Vip; Kuo, Kevin H. M.; Galacteros, Frederic; Chonat, Satheesh; Porter, John; Zagadailov, Erin; Xu, Rengyi; Oluyadi, Abdulafeez; Hawkins, Peter; Gheuens, Sarah; Beynon, Vanessa; Barcellini, Wilma
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2021 Thalassaemia International Federation Guidelines for the Management of Transfusion-dependent Thalassemia
err2022-08-01
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errFarmakis, Dimitrios; Porter, John; Taher, Ali; Cappellini, Maria Domenica; Angastiniotis, Michael; Eleftheriou, Androulla
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An open-label, multicenter, efficacy, and safety study of deferasirox in iron-overloaded patients with non-transfusion-dependent thalassemia (THETIS): 5-year results
err2022-05-27
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errLai, Yong-Rong; Cappellini, Maria Domenica; Aydinok, Yesim; Porter, John; Karakas, Zeynep; Viprakasit, Vip; Siritanaratkul, Noppadol; Kattamis, Antonis; Liu, Rongrong; Izquierdo, Miguel; Lasher, Janet; Govindaraju, Sameera; Taher, Ali
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Betibeglogene Autotemcel Gene Therapy for Non-β0/β0 Genotype β-ThalassemiaBetibeglogene Autotemcel基因治疗非 β0/β0基因型 β 地中海贫血
err2022-02-03
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errLocatelli, Franco; Thompson, Alexis A.; Kwiatkowski, Janet L.; Porter, John B.; Thrasher, Adrian J.; Hongeng, Suradej; Sauer, Martin G.; Thuret, Isabelle; Lal, Ashutosh; Algeri, Mattia; Schneiderman, Jennifer; Olson, Timothy S.; Carpenter, Ben; Amrolia, Persis J.; Anurathapan, Usanarat; Schambach, Axel; Chabannon, Christian; Schmidt, Manfred; Labik, Ivan; Elliot, Heidi; Guo, Ruiting; Asmal, Mohammed; Colvin, Richard A.; Walters, Mark C.
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Iron status influences the response of cord blood megakaryocyte progenitors to eltrombopag in vitro
err2021-12-30
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errLiu, Zhi-Jian; Deschmann, Emoke; Ramsey, Haley E.; Feldman, Henry A.; Psaila, Bethan; Cooper, Nichola; Vlachodimitropoulou, Evangelia; Porter, John; Bussel, James; Georgieff, Michael; Sola-Visner, Martha
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An oral lipidic native testosterone formulation that is absorbed independent of food
err2021-11-01
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errNewell-Price, John; Huatan, Hiep; Quirke, Jo; Porter, John; Daniel, Eleni; Mumdzic, Enis; Voet, Bernard; Keevil, Brian; Whitaker, Martin J.; Ross, Richard J.
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