arrow
返回
F

Frank W.G. Leebeek

Erasmus University Medical Center

72H指数
598论文数
2.0W被引数
收录论文 339
发表时间
Risk of thrombosis and bleeding following CAR T-cell therapy: Insights from the Dutch “Follow that CAR!” registryCAR T细胞疗法后的血栓和出血风险:来自荷兰“Follow that CAR!”登记研究的见解
err2026-07-28
err0
errOAAI
errAmica K. Ko; Pim G. N. J. Mutsaers; Lukas M. van Kleij; Amária Vledder; Elise R. A. Pennings; Anne M. Spanjaart; Janneke W. de Boer; Kylie Keijzer; Astrid M. P. Demandt; Jaap A. van Doesum; Suzanne van Dorp; Margot Jak; Maria T. Kuipers; Tom van Meerten; Marjolein W. M. van der Poel; Joost S. P. Vermaat; Frank W. G. Leebeek; Marie J. Kersten; Mandy N. Lauw
err分享
err收藏
Allele-selective Disruption of Pathogenic VWF Variants in Type 2 Von Willebrand Disease using CRISPR/Cas9利用CRISPR/Cas9对2型范可尼贫血中致病性VWF变异体进行等位基因选择性破坏
err2025-12-22
err0
errOAAI
errIsabel Bär; Stijn A. Groten; Alastair Barraclough; Petra E. Bürgisser; Calvin van Kwawegen; Peter J. Lenting; Iris van Moort; Jeroen C.J. Eikenboom; Frank W.G. Leebeek; Jan Voorberg; Maartje van den Biggelaar; Ruben Bierings
err分享
err收藏
Final Analysis of a Study of Etranacogene Dezaparvovec for Hemophilia BEtranacogene Dezaparvovec治疗血友病B的研究最终分析
err2025-12-01
err2
PREAI
errPipe, Steven W.; Miesbach, Wolfgang; Recht, Michael; Leebeek, Frank W. G.; Key, Nigel S.; Castaman, Giancarlo; Lattimore, Susan; Coppens, Michiel; Le Quellec, Sandra; Mahajan, Vaibhav; Gill, Sean; Drelich, Douglass; Monahan, Paul E.
err分享
err收藏
Correction: Rewriting the script: gene therapy and genome editing for von Willebrand Disease更正:重写脚本:基因治疗和基因组编辑在von Willebrand Disease中的应用
err2025-11-07
err0
errOAAI
errAlastair Barraclough†; Isabel Bär†; Tirsa van Duijl; Karin Fijnvandraat; Jeroen C. J. Eikenboom; Frank W. G. Leebeek; Ruben Bierings; Jan Voorberg; Despoina Trasanidou†
err分享
err收藏
err分享
err收藏
Large deletions in the F8 gene predict immune tolerance induction failure in people with severe hemophilia AF8基因中的大片段缺失可预测严重血友病A患者免疫耐受诱导失败。
err2025-10-10
err0
errOAAI
errIlja Oomen; Amal Abdi; Linda Broer; Ricardo M. Camelo; Fábia M.R.A. Callado; Luany E.M. Carvalho; Ilenia L. Calcaterra; Manuel Carcao; Giancarlo Castaman; Jeroen C.J. Eikenboom; Kathelijn Fischer; Vivian K.B. Franco; Judy Geissler; Taco W. Kuijpers; Frank W.G. Leebeek; David Lillicrap; Cláudia S. Lorenzato; Maria Elisa Mancuso; Davide Matino; Matteo N.D. Di Minno; Aomei Mo; Alex B. Mohseny; Sietse Q. Nagelkerke; Johannes Oldenburg; Suely Meireles Rezende; Georges-Etienne Rivard; Natalia Rydz; Saskia E.M. Schols; Michael W.T. Tanck; Jan Voorberg; Karin Fijnvandraat; Samantha C. Gouw
err分享
err收藏
Sex differences in outcomes of vitamin K antagonist treatment in patients with a mechanical heart valve: a Dutch population-based cohort study维生素K拮抗剂治疗在机械心脏瓣膜患者中的结局性别差异:一项荷兰基于人群的队列研究
err2025-10-08
err0
errOAAI
errEva K. Kempers; Chantal Visser; Jaap Seelig; Qingui Chen; Henk J. Adriaansen; Maarten J. Beinema; Arina J. ten Cate-Hoek; Laura M. Faber; Charlotte E.A. Dronkers; Melchior C. Nierman; Roger K. Schindhelm; Nynke M. Wiersma; Alexander D.M. Stork; Frederikus A. Klok; Frank W.G. Leebeek; Ron Pisters; Suzanne C. Cannegieter; Raffaele De Caterina; Martin E.W. Hemels; Hugo ten Cate; Maryam Kavousi; Marieke J.H.A. Kruip
err分享
err收藏
Rewriting the script: gene therapy and genome editing for von Willebrand Disease改写脚本:基因治疗和基因组编辑用于冯·维勒布兰德病
err2025-09-23
err0
errOAAI
errAlastair Barraclough†; Isabel Bär†; Tirsa van Duijl; Karin Fijnvandraat; Jeroen C. J. Eikenboom; Frank W. G. Leebeek; Ruben Bierings; Jan Voorberg; Despoina Trasanidou†
err分享
err收藏
A novel cause of type 1 Von Willebrand Disease: impaired exocytosis of Weibel-Palade bodies due to biallelic MADD variants1型血管性血友病的一种新型病因:由于双等位基因MADD变异导致Weibel-Palade小体的外排障碍
errBlood
IF23.1
err2025-07-17
err0
PREAI
errSophie Hordijk; Stijn A. Groten; Petra E. Bürgisser; Sebastiaan N. J. Laan; Georg Christoph Korenke; Tomáš Honzík; Diane Beysen; Frank W. G. Leebeek; Paul A. Skehel; Maartje van den Biggelaar; Tom Carter; Ruben Bierings
err分享
err收藏
von Willebrand disease-specific defects and proteomic signatures in endothelial colony–forming cells血管性血友病特异性缺陷和内皮集落形成细胞的蛋白质组学特征
err2025-05-06
err0
errOAAI
errSebastiaan N.J. Laan; Stijn Groten; Richard J. Dirven; Petra E. Bürgisser; Frank W.G. Leebeek; Iris van Moort; Maartje van den Biggelaar; Ruben Bierings; Jeroen Eikenboom
err分享
err收藏
Completion of phase 2b trial of etranacogene dezaparvovec gene therapy in patients with hemophilia B over 5 years完成etranacogene dezaparvovec基因疗法在5年以上血友病B患者中的2b期试验。
err2025-04-08
err0
errOAAI
errAnnette von Drygalski; Esteban Gomez; Adam Giermasz; Giancarlo Castaman; Nigel S. Key; Susan U. Lattimore; Frank W. G. Leebeek; Wolfgang A. Miesbach; Michael Recht; Paul E. Monahan; Sandra Le Quellec; Steven W. Pipe
err分享
err收藏
Sexuality and bleeding in von Willebrand disease
err2025-02-01
err0
errOAAI
errvan Kwawegen, Calvin B.; Pastoor, Hester; Eikenboom, Jeroen; Fijnvandraat, Karin; Ypma, Paula; Heubel-Moenen, Floor C. J. I.; van Galen, Karin P. M.; Mauser-Bunschoten, Evelien P.; Meijer, Karina; Schols, Saskia E. M.; Cnossen, Marjon H.; van der Bom, Johanna G.; de Meris, Joke; Atiq, Ferdows; Kruip, Marieke J. H. A.; Leebeek, Frank W. G.
err分享
err收藏
Replacement therapy in pregnant women with von Willebrand disease during delivery: Factor levels and pharmacokinetics妊娠期患者分娩时伴有冯·维勒布兰德病时的替代疗法:因子水平和药代动力学
err2025-01-03
err0
errOAAI
errAl Arashi, Wala; Cloesmeijer, Michael E.; Leebeek, Frank W. G.; Duvekot, Johannes J.; Kruip, Marieke J. H. A.; Mathot, Ron A. A.; Cnossen, Marjon H.
err分享
err收藏
err分享
err收藏
Adeno-associated virus-based gene therapy for hemophilia- addressing the gaps基于腺相关病毒的血友病基因治疗-解决差距
err2025-01-01
err0
errOAAI
errMiesbach, Wolfgang; Batty, Paul; Chowdary, Pratima; Fong, Sylvia; Kaczmarek, Radoslaw; Leebeek, Frank W. G.; Long, Brian; Mahlangu, Johnny; Makris, Mike; Pierce, Glenn F.; Pipe, Steven W.; Srivastava, Alok; Voorberg, Jan; Peyvandi, Flora
err分享
err收藏
Genetic variants, thrombocytopenia, and clinical phenotype of type 2B von Willebrand disease: a median 16-year follow-up study2B型血管性血友病的遗传变异、血小板减少和临床表型: 一项中位16年随访研究
err2024-12-01
err0
errOAAI
errvan Kwawegen, Calvin B.; Atiq, Ferdows; Endenburg, Dara; Fijnvandraat, Karin; van Galen, Karin P. M.; Cnossen, Marjon H.; Schols, Saskia E. M.; Kruip, Marieke J. H. A.; van Heerde, Waander L.; de Meris, Joke; van der Bom, Johanna G.; Eikenboom, Jeroen; Meijer, Karina; Leebeek, Frank W. G.
err分享
err收藏
Patient-reported data on the severity of Von Willebrand disease患者报告的关于血管性血友病严重程度的数据
err2024-10-15
err0
errOAAI
errvan Kwawegen, Calvin B.; Fijnvandraat, Karin; Kruip, Marieke J. H. A.; de Meris, Joke; Schols, Saskia E. M.; Meijer, Karina; van der Bom, Johanna G.; Cnossen, Marjon H.; van Galen, Karin P. M.; Atiq, Ferdows; Eikenboom, Jeroen; Leebeek, Frank W. G.
err分享
err收藏