未登录Exploring erythroid cell transcriptomics to understand regulation of fetal hemoglobin expression for advanced sickle cell disease treatment探索红系细胞转录组学以理解胎儿血红蛋白表达调控,用于先进镰状细胞病治疗
Nkya, Siana; Nzunda, Collin; Kaywanga, Frida; Karim, Salmaan; Solomon, David; Saukiwa, Emmanuel; Christopher, Heavenlight; Ngowi, Doreen; Johansen, Julieth; Urio, Florence; Mgaya, Josephine; Chamba, Clara; Hashim, Fadya; Ambrose, Emmanuela E.; Acquah, Solomon Ofori; Chimusa, Emile R.; Makani, Julie
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收藏Caregivers' beliefs about hydroxyurea influence its usage among children with sickle cell disease: a cross-sectional study in Dar-es-Salaam, Tanzania照护者对羟基脲的信念影响其在患有镰状细胞病儿童中的使用:坦桑尼亚达累斯萨拉姆的一项横断面研究
Ally, Mwashungi; Kakoko, Deodatus; Swai, Calvin; Omsland, Tone Kristin; Moen, Kare; Metta, Emmy; Yonazi, Mbonea; Jonathan, Agnes; Makani, Julie; Mmbaga, Elia John; Leshabari, Melkizedeck; Balandya, Emmanuel
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收藏Scientific Advancements in Gene Therapies: Opportunities for Global Regulatory Convergence
Olaghere, Jimi; Williams, David A.; Farrar, Jeremy; Buening, Hildegard; Calhoun, Cecelia; Ho, Tony; Inamdar, Maneesha S.; Liu, David; Makani, Julie; Nyarko, Kwasi; Ruiz, Sol; Tisdale, John; Mccune, Joseph M.; Boadi, Esther; Reagan Udall Fn FDA
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收藏Strengthening advanced therapy for sickle cell disease in Africa: experience from sickle cell disease centre in Dar es Salaam, Tanzania
Bukini, Daima; Rifai, Aisha; Kanza, Collin; Luoga, Fredrick; Maingu, Deogratius; Kassim, Kassim; Mashaka, Jennifer; Kisali, Eka Patricia; Karim, Salmaan; Alimohamed, Mohamed Zahir; Manongi, Janeth; Lema, Winfrida; Chuwa, Harrison; Konteh, Sisawo; Urio, Florence; Minja, Irene Kida; Balandya, Emmanuel; Moshi, Grace; Makani, Julie; Muhimbili Sickle Cell Programme
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收藏The epidemiology of very severe anaemia in sickle cell disease in Tanzania: a prospective cohort study坦桑尼亚镰状细胞病严重贫血的流行病学: 一项前瞻性队列研究
Makani, Julie; Masamu, Upendo; Tluway, Furahini; Sangeda, Raphael Z.; Soka, Deogratius; Osati, Elisha; Kindole, Christine; Cox, Sharon E.; Mgaya, Josephine; Shayo, Sigfrid C.; Makubi, Abel; Balandya, Emmanuel; Mmbando, Bruno P.
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收藏Hydroxyurea mobile directly observed therapy versus standard monitoring in patients with sickle cell anemia: a phase 2 randomized trial
Sasi, Philip; Makubi, Abel; Sangeda, Raphael Z.; Ngaeje, Mariam Y.; Mmbando, Bruno P.; Soka, Joseph; Rosano, Caterina; Magesa, Alex S.; Cox, Sharon E.; Makani, Julie; Novelli, Enrico M.
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收藏The Ugandan sickle Pan-African research consortium registry: design, development, and lessons
Nsubuga, Mike; Mutegeki, Henry; Jjingo, Daudi; Munube, Deogratias; Namazzi, Ruth; Opoka, Robert; Kasirye, Philip; Ndeezi, Grace; Hume, Heather; Mupere, Ezekiel; Kebirungi, Grace; Birungi, Isaac; Morrice, Jack; Jonas, Mario; Nembaware, Victoria; Wonkam, Ambroise; Makani, Julie; Kiguli, Sarah
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收藏The translational gap for gene therapies in low- and middle-income countries
Doxzen, Kevin W.; Adair, Jennifer E.; Fonseca Bazzo, Yris Maria; Bukini, Daima; Cornetta, Kenneth; Dalal, Varsha; Guerino-Cunha, Renato Luiz; Hongeng, Suradej; Jotwani, Geeta; Kityo-Mutuluuza, Cissy; Lakshmanan, Krishnamurti; Mahlangu, Johnny; Makani, Julie; Mathews, Vikram; Ozelo, Margareth C.; Rangarajan, Savita; Scholefield, Janine; Silva Junior, Joao Batista; Mccune, Joseph M.
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收藏The genetic dissection of fetal haemoglobin persistence in sickle cell disease in Nigeria
Ojewunmi, Oyesola O.; Adeyemo, Titilope A.; Oyetunji, Ajoke, I; Inyang, Bassey; Akinrindoye, Afolashade; Mkumbe, Baraka S.; Gardner, Kate; Rooks, Helen; Brewin, John; Patel, Hamel; Lee, Sang Hyuck; Chung, Raymond; Rashkin, Sara; Kang, Guolian; Chianumba, Reuben; Sangeda, Raphael; Mwita, Liberata; Isa, Hezekiah; Agumadu, Uche-Nnebe; Ekong, Rosemary; Faruk, Jamilu A.; Jamoh, Bello Y.; Adebiyi, Niyi M.; Umar, Ismail A.; Hassan, Abdulaziz; Grace, Christopher; Goel, Anuj; Inusa, Baba P. D.; Falchi, Mario; Nkya, Siana; Makani, Julie; Ahmad, Hafsat R.; Nnodu, Obiageli; Strouboulis, John; Menzel, Stephan
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收藏Clonal selection of hematopoietic stem cells after gene therapy for sickle cell disease
Chapman, Michael Spencer; Cull, Alyssa H.; Ciuculescu, Marioara F.; Esrick, Erica B.; Mitchell, Emily; Jung, Hyunchul; O'Neill, Laura; Roberts, Kirsty; Fabre, Margarete A.; Williams, Nicholas; Nangalia, Jyoti; Quinton, Joanne; Fox, James M.; Pellin, Danilo; Makani, Julie; Armant, Myriam; Williams, David A.; Campbell, Peter J.; Kent, David G.
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收藏Caught between pity, explicit bias, and discrimination: a qualitative study on the impact of stigma on the quality of life of persons living with sickle cell disease in three African countries
Munung, Nchangwi Syntia; Treadwell, Marsha; Kamga, Karen Kengne; Dennis-Antwi, Jemima; Anie, Kofi; Bukini, Daima; Makani, Julie; Wonkam, Ambroise
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