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Zinc finger nuclease-mediated gene editing in hematopoietic stem cells results in reactivation of fetal hemoglobin in sickle cell disease Lessard, Samuel; Rimmele, Pauline; Ling, Hui; Moran, Kevin; Vieira, Benjamin; Lin, Yi-Dong; Rajani, Gaurav Manohar; Hong, Vu; Reik, Andreas; Boismenu, Richard; Hsu, Ben; Chen, Michael; Cockroft, Bettina M.; Uchida, Naoya; Tisdale, John; Alavi, Asif; Krishnamurti, Lakshmanan; Abedi, Mehrdad; Galeon, Isobelle; Reiner, David; Wang, Lin; Ramezi, Anne; Rendo, Pablo; Walters, Mark C.; Levasseur, Dana; Peters, Robert; Harris, Timothy; Hicks, Alexandra 分享 收藏
Reproductive Health Assessment and Reports of Fertility Counseling in Pediatric and Adolescent Patients with Sickle Cell Disease After Hematopoietic Cell Transplantation George, Sobenna A.; Veludhandi, Anirudh; Xiang, Yijin; Liu, Katie; Stenger, Elizabeth; Arnold, Staci D.; Mehta, Akanksha; Schirmer, David A.; Spencer, Jessica B.; Guilcher, Gregory M. T.; Bhatia, Monica; Abraham, Allistair; Gomez-Lobo, Veronica; Krishnamurti, Lakshmanan; Meacham, Lillian R. 分享 收藏
Long-term quality of life after hematopoietic cell transplant for sickle cell disease in childhood: A STELLAR interim analysis Arnold, Staci D.; Bakshi, Nitya; Ross, Diana; Smith, Crystal; Sinha, Cynthia; Veludhandi, Anirudh; Dutreuil, Valerie; Bai, Shasha; Meacham, Lillian R.; Guilcher, Greg; Bhatia, Monica; Abraham, Allistair; Kasow, Kimberly A.; Haight, Ann; El Rassi, Fuad; Stenger, Elizabeth; Lipscomb, Joseph; Krishnamurti, Lakshmanan 分享 收藏
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The translational gap for gene therapies in low- and middle-income countries Doxzen, Kevin W.; Adair, Jennifer E.; Fonseca Bazzo, Yris Maria; Bukini, Daima; Cornetta, Kenneth; Dalal, Varsha; Guerino-Cunha, Renato Luiz; Hongeng, Suradej; Jotwani, Geeta; Kityo-Mutuluuza, Cissy; Lakshmanan, Krishnamurti; Mahlangu, Johnny; Makani, Julie; Mathews, Vikram; Ozelo, Margareth C.; Rangarajan, Savita; Scholefield, Janine; Silva Junior, Joao Batista; Mccune, Joseph M. 分享 收藏
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Long-term outcomes after unrelated donor transplantation for severe sickle cell disease on the BMT CTN 0601 trial BMT CTN 0601试验中严重镰状细胞病的无关供体移植后的长期结果 Eapen, Mary; Kou, Jianqun; Andreansky, Martin; Bhatia, Monica; Brochstein, Joel; Chaudhury, Sonali; Haight, Ann E.; Haines, Hilary; Jacobsohn, David; Jaroscak, Jennifer; Kasow, Kimberly A.; Krishnamurti, Lakshmanan; Levine, John E.; Leung, Kathryn; Margolis, David; Yu, Lolie C.; Horowitz, Mary M.; Kamani, Naynesh; Walters, Mark C.; Shenoy, Shalini 分享 收藏
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