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Frank J. T. Staal

Leiden University

70H指数
300论文数
1.8W被引数
收录论文 117
发表时间
RAG1 lentiviral gene therapy restores T cell development of RAG1-SCID patient cells in artificial thymic organoids.RAG1慢病毒基因疗法在人工胸腺类器官中恢复了RAG1-SCID患者细胞的T细胞发育。
err2025-08-21
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errXiaolin Meng; Janine E. Melsen; Rosalie van der Holst; Bas de Mooij; Sandra Vloemans; Marja van Eggermond; Dagmar Berghuis; Arjan C. Lankester; Sander de Kivit; Karin Pike-Overzet; Anton W. Langerak; Frank J. T. Staal; Lisa M. Ott de Bruin; Kirsten Canté-Barrett
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European Society for Immunodeficiencies guidelines for the management of patients with congenital athymia
err2024-12-01
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errKreins, Alexandra Y.; Dhalla, Fatima; Flinn, Aisling M.; Howley, Evey; Ekwall, Olov; Villa, Anna; Staal, Frank J. T.; Anderson, Graham; Gennery, Andrew R.; Hollander, Georg A.; Davies, E. Graham
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Gene therapy strategies for RAG1 deficiency: Challenges and breakthroughs
err2024-12-01
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errGilioli, Giorgio; Lankester, Arjan C.; de Kivit, Sander; Staal, Frank J. T.; de Bruin, Lisa M. Ott
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Utilizing epigenetic regulators to improve HSC-based lentiviral gene therapy
err2024-09-16
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errTajer, Parisa; Karakaslar, Emin Onur; Cante-Barrett, Kirsten; Naber, Brigitta A. E.; Vloemans, Sandra A.; van Eggermond, Marja C. J. A.; van der Hoorn, Marie-Louise; van den Akker, Erik; Pike-Overzet, Karin; Staal, Frank J. T.
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Restoration of T and B Cell Differentiation after RAG1 Gene Transfer in Human RAG1 Defective Hematopoietic Stem Cells
err2024-07-05
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errSorel, Natael; Diaz-Pascual, Francisco; Bessot, Boris; Sadek, Hanem; Mollet, Chloe; Chouteau, Myriam; Zahn, Marco; Gil-Farina, Irene; Tajer, Parisa; van Eggermond, Marja; Berghuis, Dagmar; Lankester, Arjan C.; Andre, Isabelle; Gabriel, Richard; Cavazzana, Marina; Pike-Overzet, Kasrin; Staal, Frank J. T.; Lagresle-Peyrou, Chantal
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Newborn Screening Today and Tomorrow: A Brief Report from the International Primary Immunodeficiencies Congress新生儿筛查的今天和明天: 国际原发性免疫缺陷大会的简要报告
err2024-04-05
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errSolis, Leire; Van Coillie, Samya; Bonham, James R.; Hauck, Fabian; Hammarstrom, Lennart; Staal, Frank J. T.; Lim, Bruce; Pergent, Martine; Prevot, Johan
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Partial correction of immunodeficiency by lentiviral vector gene therapy in mouse models carrying Rag1 hypomorphic mutations
err2023-11-13
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errCastiello, Maria Carmina; Di Verniere, Martina; Draghici, Elena; Fontana, Elena; Penna, Sara; Sereni, Lucia; Zecchillo, Alessandra; Minuta, Denise; Uva, Paolo; Zahn, Marco; Gil-Farina, Irene; Annoni, Andrea; Iaia, Silvia; Ott de Bruin, Lisa M.; Notarangelo, Luigi D.; Pike-Overzet, Karin; Staal, Frank J. T.; Villa, Anna; Capo, Valentina
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Immune subset-committed proliferating cells populate the human foetal intestine throughout the second trimester of gestation
err2023-03-10
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errGuo, Nannan; Li, Na; Jia, Li; Jiang, Qinyue; Schreurs, Mette; van Unen, Vincent; Lopes, Susana M. Chuva de Sousa; Vloemans, Alexandra A.; Eggermont, Jeroen; Lelieveldt, Boudewijn; Staal, Frank J. T.; de Miranda, Noel F. C. C.; Pascutti, M. Fernanda; Koning, Frits
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Single-cell immune profiling reveals thymus-seeding populations, T cell commitment, and multilineage development in the human thymus
err2022-11-25
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errCordes, Martijn; Cante-Barrett, Kirsten; van den Akker, Erik B.; Moretti, Federico A.; Kielbasa, Szymon M.; Vloemans, Sandra A.; Garcia-Perez, Laura; Teodosio, Cristina; van Dongen, Jacques J. M.; Pike-Overzet, Karin; Reinders, Marcel J. T.; Staal, Frank J. T.
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Immune Determinants of Viral Clearance in Hospitalised COVID-19 Patients: Reduced Circulating Naive CD4+T Cell Counts Correspond with Delayed Viral Clearance
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err2022-09-02
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errZlei, Mihaela; Sidorov, Igor A.; Joosten, Simone A.; Heemskerk, Mirjam H. M.; Myeni, Sebenzile K.; Pothast, Cilia R.; de Brouwer, Caroline S.; Boomaars-van der Zanden, A. Linda; van Meijgaarden, Krista E.; Morales, Shessy T.; Wessels, Els; Janse, Jacqueline J.; Goeman, Jelle J.; Cobbaert, Christa M.; Kroes, Aloys C. M.; Cannegieter, Suzanne C.; Roestenberg, Meta; Visser, Leonardus G.; Kikkert, Marjolein; Feltkamp, Mariet C. W.; Arbous, Sesmu M.; Staal, Frank J. T.; Ottenhoff, Tom H. M.; van Dongen, Jacques J. M.; Roukens, Anna H. E.; de Vries, Jutte J. C.
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Axin2/Conductin Is Required for Normal Haematopoiesis and T Lymphopoiesis
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err2022-08-28
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errde Roo, Jolanda J. D.; Chhatta, Amiet; Garcia-Perez, Laura; Naber, Brigitta A. E.; Vloemans, Sandra A.; Salvatori, Daniela C. F.; Pike-Overzet, Karin; Mikkers, Harald; Staal, Frank J. T.
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The EHA Research Roadmap: Hematopoietic Stem Cells and Allotransplantation
err2022-05-01
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errFibbe, Willem; Bernardi, Rosa; Charbord, Pierre; Krause, Daniela; Lo Celso, Cristina; Mendez-Ferrer, Simon; Mummery, Christine; Oostendorp, Robert; Raaijmakers, Marc; Socie, Gerard; Staal, Frank; Bacigalupo, Andrea
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Stem Cell-Based Disease Models for Inborn Errors of Immunity
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err2021-12-30
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errZbinden, Aline; Cante-Barrett, Kirsten; Pike-Overzet, Karin; Staal, Frank J. T.
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Prolonged activation of nasal immune cell populations and development of tissue-resident SARS-CoV-2-specific CD8+ T cell responses following COVID-19
err2021-12-22
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errRoukens, Anna H. E.; Pothast, Cilia R.; Koenig, Marion; Huisman, Wesley; Dalebout, Tim; Tak, Tamar; Azimi, Shohreh; Kruize, Yvonne; Hagedoorn, Renate S.; Zlei, Mihaela; Staal, Frank J. T.; de Bie, Fenna J.; van Dongen, Jacques J. M.; Arbous, Sesmu M.; Zhang, Jaimie L. H.; Verheij, Maaike; Prins, Corine; van der Does, Anne M.; Hiemstra, Pieter S.; de Vries, Jutte J. C.; Janse, Jacqueline J.; Roestenberg, Meta; Myeni, Sebenzile K.; Kikkert, Marjolein; Yazdanbakhsh, Maria; Heemskerk, Mirjam H. M.; Smits, Hermelijn H.; Jochems, Simon P.
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Predicting genotoxicity of viral vectors for stem cell gene therapy using gene expression-based machine learning使用基于基因表达的机器学习预测用于干细胞基因治疗的病毒载体的遗传毒性
err2021-12-01
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errSchwarzer, Adrian; Talbot, Steven R.; Selich, Anton; Morgan, Michael; Schott, Juliane W.; Dittrich-Breiholz, Oliver; Bastone, Antonella L.; Weigel, Bettina; Ha, Teng Cheong; Dziadek, Violetta; Gijsbers, Rik; Thrasher, Adrian J.; Staal, Frank J. T.; Gaspar, Hubert B.; Modlich, Ute; Schambach, Axel; Rothe, Michael
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The Route of Early T Cell Development: Crosstalk between Epigenetic and Transcription Factors
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err2021-04-30
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errChiara, Veronica Della; Daxinger, Lucia; Staal, Frank J. T.
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Combining Mobilizing Agents with Busulfan to Reduce Chemotherapy-Based Conditioning for Hematopoietic Stem Cell Transplantation
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IF5.2
err2021-04-30
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errGarcia-Perez, Laura; van Roon, Lieke; Schilham, Marco W.; Lankester, Arjan C.; Pike-Overzet, Karin; Staal, Frank J. T.
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