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Bone Health Screening in Persons With Bleeding Disorders: A Survey of United States Haemophilia Treatment Centres Citla-Sridhar, Divyaswathi; Ahuja, Sanjay; Sidonio, Robert; Chitlur, Meera; Sharathkumar, Anjali; Tobase, Patricia; Acharya, Suchitra; Isaac, Daniel; Kulkarni, Roshni; Johnson, Marilyn Manco 分享 收藏
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Recombinant von Willebrand factor and tranexamic acid for heavy menstrual bleeding in patients with mild and moderate von Willebrand disease in the USA (VWDMin): a phase 3, open-label, randomised, crossover trial Ragni, Margaret, V; Rothenberger, Scott; Feldman, Robert; Nance, Danielle; Leavitt, Andrew; Malec, Lynn; Kulkarni, Roshni; Sidonio Jr, Robert; Kraut, Eric; Lasky, Joseph; Pruthi, Rajiv; Angelini, Dana; Philipp, Claire; Hwang, Nina; Wheeler, Allison P.; Seaman, Craig; Machin, Nicoletta; Xavier, Frederico; Meyer, Michael; Bellissimo, Daniel; Humphreys, Gregory; Smith, Kenneth J.; Merricks, Elizabeth P.; Nichols, Timothy C.; Ivanco, Dana; Vehec, Deborah; Koerbel, Glory; Althouse, Andrew D. 分享 收藏
Prophylaxis with a recombinant factor VIII Fc in hemophilia A: long-term follow-up on joint health, efficacy, and safety from phase 3 studies in children and adults 重组因子VIII Fc预防血友病a: 儿童和成人3期研究关节健康、疗效和安全性的长期随访 Konkle, Barbara A.; Oldenburg, Johannes; Pasi, John; Kulkarni, Roshni; Nolan, Beatrice; Mahlangu, Johnny; Young, Guy; Brown, Simon A.; Pabinger, Ingrid; Shapiro, Amy; Negrier, Claude; Blanchette, Victor; Ragni, Margaret, V; Dumont, Jennifer; Lethagen, Stefan 分享 收藏
Post hoc longitudinal assessment of the efficacy and safety of recombinant factor IX Fc fusion protein in hemophilia B Shapiro, Amy D.; Kulkarni, Roshni; Ragni, Margaret V.; Chambost, Herve; Mahlangu, Johnny; Oldenburg, Johannes; Nolan, Beatrice; Ozelo, Margareth C.; Foster, Meredith C.; Willemze, Annemieke; Barnowski, Christopher; Jain, Nisha; Winding, Bent; Dumont, Jennifer; Lethagen, Stefan; Barnes, Chris; Pasi, K. John 分享 收藏
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Efanesoctocog Alfa Prophylaxis for Patients with Severe Hemophilia A von Drygalski, Annette; Chowdary, Pratima; Kulkarni, Roshni; Susen, Sophie; Konkle, Barbara A.; Oldenburg, Johannes; Matino, Davide; Klamroth, Robert; Weyand, Angela C.; Jimenez-Yuste, Victor; Nogami, Keiji; Poloskey, Stacey; Winding, Bent; Willemze, Annemieke; Knobe, Karin 分享 收藏
Depression and anxiety in persons with Von Willebrand disease 血管性血友病患者的抑郁和焦虑 Roberts, Jonathan C. C.; Kulkarni, Roshni; Kouides, Peter A. A.; Sidonio Jr, Robert F. F.; Carpenter, Shannon L. L.; Konkle, Barbara A. A.; Wu, Joanne; Ullman, Megan M. M.; Curtis, Randall; Baker, Judith R. R.; Crook, Nicole; Nichol, Michael B. B. 分享 收藏
Quality of life in a large multinational haemophilia B cohort (The B-Natural study) - Unmet needs remain Berntorp, Erik; LeBeau, Petra; Ragni, Margaret, V; Borhany, Munira; Abajas, Yasmina L.; Tarantino, Michael D.; Holstein, Katharina; Croteau, Stacy E.; Liesner, Raina; Tarango, Cristina; Carvalho, Manuela; McGuinn, Catherine; Funding, Eva; Kempton, Christine L.; Bidlingmaier, Christoph; Cohen, Alice; Oldenburg, Johannes; Kearney, Susan; Knoll, Christine; Kuriakose, Philip; Acharya, Suchitra; Reiss, Ulrike M.; Kulkarni, Roshni; Witkop, Michelle; Lethagen, Stefan; Krouse, Rebecca; Shapiro, Amy D.; Astermark, Jan 分享 收藏
Whole-exome analysis of adolescents with low VWF and heavy menstrual bleeding identifies novel genetic associations 对低VWF水平且伴有重度月经出血的青少年进行全外显子组分析,鉴定了新的遗传关联。 Sadler, Brooke; Minard, Charles G.; Haller, Gabe; Gurnett, Christina A.; O'Brien, Sarah H.; Wheeler, Allison; Jain, Shilpa; Sharma, Mutka; Zia, Ayesha; Kulkarni, Roshni; Mullins, Eric; Ragni, Margaret, V; Sidonio, Robert; Dietrich, Jennifer E.; Kouides, Peter A.; Di Paola, Jorge; Srivaths, Lakshmi 分享 收藏
A new hemophilia carrier nomenclature to define hemophilia in women and girls: Communication from the SSC of the ISTH 一种新的血友病携带者命名法,用于定义妇女和女孩的血友病: 来自ISTH SSC的交流 van Galen, Karin P. M.; d'Oiron, Roseline; James, Paula; Abdul-Kadir, Rezan; Kouides, Peter A.; Kulkarni, Roshni; Mahlangu, Johnny N.; Othman, Maha; Peyvandi, Flora; Rotellini, Dawn; Winikoff, Rochelle; Sidonio, Robert F. 分享 收藏
Characteristics, complications, and sites of bleeding among infants and toddlers less than 2 years of age with VWD 患有VWD的2岁以下婴幼儿的特征,并发症和出血部位 Dupervil, Brandi; Abe, Karon; O'Brien, Sarah H.; Oakley, Meredith; Kulkarni, Roshni; Thornburg, Courtney D.; Byams, Vanessa R.; Soucie, J. Michael 分享 收藏
Women and girls with haemophilia and bleeding tendencies: Outcomes related to menstruation, pregnancy, surgery and other bleeding episodes from a retrospective chart review Chaudhury, Ateefa; Sidonio, Robert, Jr.; Jain, Nisha; Tsao, Elisa; Tymoszczuk, Justyna; Oviedo Ovando, Mariana; Kulkarni, Roshni 分享 收藏
Natural history study of factor IX deficiency with focus on treatment and complications (B-Natural) 因子IX缺乏症的自然史研究,重点是治疗和并发症 (B-自然) Shapiro, Amy D.; Ragni, Margaret V.; Borhany, Munira; Abajas, Yasmina L.; Tarantino, Michael D.; Holstein, Katharina; Croteau, Stacy E.; Liesner, Riana; Tarango, Cristina; Carvalho, Manuela; McGuinn, Catherine; Funding, Eva; Kempton, Christine L.; Bidlingmaier, Christoph; Cohen, Alice; Oldenburg, Johannes; Kearney, Susan; Knoll, Christine; Kuriakose, Philip; Acharya, Suchitra; Reiss, Ulrike M.; Kulkarni, Roshni; Witkop, Michelle; Lethagen, Stefan; Donfield, Sharyne; LeBeau, Petra; Berntorp, Erik; Astermark, Jan 分享 收藏
BIVV001 Fusion Protein as Factor VIII Replacement Therapy for Hemophilia A BIVV001融合蛋白作为血友病A的因子VIII替代疗法 Konkle, Barbara A.; Shapiro, Amy D.; Quon, Doris V.; Staber, Janice M.; Kulkarni, Roshni; Ragni, Margaret V.; Chhabra, Ekta S.; Poloskey, Stacey; Rice, Kara; Katragadda, Suresh; Fruebis, Joachim; Benson, Craig C. 分享 收藏
The spectrum and severity of bleeding in adolescents with low von Willebrand factor-associated heavy menstrual bleeding Srivaths, Lakshmi; Minard, Charles G.; O'Brien, Sarah H.; Wheeler, Allison P.; Mullins, Eric; Sharma, Mukta; Sidonio, Robert; Jain, Shilpa; Zia, Ayesha; Ragni, Margaret, V; Kulkarni, Roshni; Dietrich, Jennifer E.; Kouides, Peter A. 分享 收藏