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Hospital-Based Careers in Pediatric Hematology-Oncology: The State of the Field and Future Needs 儿科血液肿瘤学领域的医院内职业:现状与未来需求 Sohal, Ambika; Freedman, Jason L.; Aller, Steven; Cobb, Carmen; Davis, Matt; Degar, Barbara; De Vela, Gabriel; Graul-conroy, Amanda; Hu, Zhongbo; Jacobsohn, David; Mazzone, Subha; Porea, Tim; Ray, Andrew; Schuback, Heather L.; Slone, Jeremy S.; Spencer, Christina; Styres, Courtney; Neufeld, Ellis J.; Fromme, H. Barrett; Johnson, Liza-marie 分享 收藏
Taking Care of the Caregivers: A Quality-of-Life Measure for the Parents of Children With Transfusion-Dependent 关爱护理者:一项针对输血依赖儿童父母的生存质量评估 Klaassen, Robert J.; Khelifi, Rania S.; Barrowman, Nicholas; Merelles-Pulcini, Manuela; Vichinsky, Elliott P.; Kirby-Allen, Melanie; Neufeld, Ellis J.; Kwiatkowski, Janet L.; Wu, John; Young, Nancy L. 分享 收藏
Genetic variants in canonical Wnt signaling pathway associated with pediatric immune thrombocytopenia Kim, Taylor Olmsted; Geris, Jennifer M.; Flanagan, Jonathan M.; Grace, Rachael F.; Lambert, Michele P.; O'Farrell, Candelaria; Rose, Melissa J.; Shimano, Kristin A.; Niss, Omar; Neunert, Cindy; Nakano, Taizo A.; MacMath, Derek; Dinu, Bogdan; Kirk, Susan E.; Neufeld, Ellis J.; Despotovic, Jenny M.; Scheurer, Michael E.; Grimes, Amanda B. 分享 收藏
Genetic ablation of the CDP/Cux protein C terminus results in hair cycle defects and reduced male fertility Luong, MX; van der Meijden, CM; Xing, DX; Hesselton, R; Monuki, ES; Jones, SN; Lian, JB; Stein, JL; Stein, GS; Neufeld, EJ; van Wijnen, AJ 分享 收藏
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Simoctocog Alfa (Nuwiq) in Previously Untreated Patients with Severe Haemophilia A: Final Results of the NuProtect Study Simococog Alfa (Nuwiq) 在先前未经治疗的严重血友病A患者中: NuProtect研究的最终结果 Liesner, Ri J.; Abraham, Aby; Altisent, Carmen; Belletrutti, Mark J.; Carcao, Manuel; Carvalho, Manuela; Chambost, Herve; Chan, Anthony K. C.; Dubey, Leonid; Ducore, Jonathan; Gattens, Michael; Gresele, Paolo; Gruel, Yves; Guillet, Benoit; Jimenez-Yuste, Victor; Kitanovski, Lidija; Klukowska, Anna; Lohade, Sunil; Mancuso, Maria Elisa; Oldenburg, Johannes; Pavlova, Anna; Pollio, Berardino; Sigaud, Marianne; Vdovin, Vladimir; Vilchevska, Kateryna; Wu, John K. M.; Jansen, Martina; Belyanskaya, Larisa; Walter, Olaf; Knaub, Sigurd; Neufeld, Ellis J. 分享 收藏
A Phase 3 Trial of Luspatercept in Patients with Transfusion-Dependent β-Thalassemia Luspatercept在输血依赖性 β-地中海贫血患者中的3期试验 Cappellini, M. D.; Viprakasit, V.; Taher, A. T.; Georgiev, P.; Kuo, K. H. M.; Coates, T.; Voskaridou, E.; Liew, H. -K.; Pazgal-Kobrowski, I.; Forni, G. L.; Perrotta, S.; Khelif, A.; Lal, A.; Kattamis, A.; Vlachaki, E.; Origa, R.; Aydinok, Y.; Bejaoui, M.; Ho, P. J.; Chew, L. -P.; Bee, P. -C.; Lim, S. -M.; Lu, M. -Y.; Tantiworawit, A.; Ganeva, P.; Gercheva, L.; Shah, F.; Neufeld, E. J.; Thompson, A.; Laadem, A.; Shetty, J. K.; Zou, J.; Zhang, J.; Miteva, D.; Zinger, T.; Linde, P. G.; Sherman, M. L.; Hermine, O.; Porter, J.; Piga, A. 分享 收藏
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Second-line treatments in children with immune thrombocytopenia: Effect on platelet count and patient-centered outcomes 儿童免疫性血小板减少症的二线治疗: 对血小板计数和以患者为中心的结果的影响 Grace, Rachael F.; Shimano, Kristin A.; Bhat, Rukhmi; Neunert, Cindy; Bussel, James B.; Klaassen, Robert J.; Lambert, Michele P.; Rothman, Jennifer A.; Breakey, Vicky R.; Hege, Kerry; Bennett, Carolyn M.; Rose, Melissa J.; Haley, Kristina M.; Buchanan, George R.; Geddis, Amy; Lorenzana, Adonis; Jeng, Michael; Pastore, Yves D.; Crary, Shelley E.; Neier, Michelle; Neufeld, Ellis J.; Neu, Nolan; Forbes, Peter W.; Despotovic, Jenny M. 分享 收藏
Regional variation and cost implications of prescribed extended half-life factor concentrates among US Haemophilia Treatment Centres for patients with moderate and severe haemophilia Croteau, Stacy E.; Cheng, Dunlei; Cohen, Alice J.; Holmes, Chris E.; Malec, Lynn M.; Silvey, Michael; Thornburg, Courtney D.; Wheeler, Allison P.; Kouides, Peter A.; Raffini, Leslie J.; Neufeld, Ellis J. 分享 收藏
Prevalence and management of iron overload in pyruvate kinase deficiency: report from the Pyruvate Kinase Deficiency Natural History Study van Beers, Eduard J.; van Straaten, Stephanie; Morton, D. Holmes; Barcellini, Wilma; Eber, Stefan W.; Glader, Bertil; Yaish, Hassan M.; Chonat, Satheesh; Kwiatkowski, Janet L.; Rothman, Jennifer A.; Sharma, Mukta; Neufeld, Ellis J.; Sheth, Sujit; Despotovic, Jenny M.; Kollmar, Nina; Pospisilova, Dagmar; Knoll, Christine M.; Kuo, Kevin; Pastore, Yves D.; Thompson, Alexis A.; Newburger, Peter E.; Ravindranath, Yaddanapudi; Wang, Winfred C.; Wlodarski, Marcin W.; Wang, Heng; Holzhauer, Susanne; Breakey, Vicky R.; Verhovsek, Madeleine; Kunz, Joachim; McNaull, Melissa A.; Rose, Melissa J.; Bradeen, Heather A.; Addonizio, Kathryn; Li, Anran; Al-Sayegh, Hasan; London, Wendy B.; Grace, Rachael F. 分享 收藏
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Performing and interpreting individual pharmacokinetic profiles in patients with Hemophilia A or B: Rationale and general considerations Iorio, Alfonso; Edginton, Andrea N.; Blanchette, Victor; Blatny, Jan; Boban, Ana; Cnossen, Marjon; Collins, Peter; Croteau, Stacy E.; Fischer, Katheljin; Hart, Daniel P.; Ito, Shinya; Korth-Bradley, Joan; Lethagen, Stefan; Lillicrap, David; Makris, Mike; Mathot, Ron; Morfini, Massimo; Neufeld, Ellis J.; Spears, Jeffrey 分享 收藏
Focusing in on use of pharmacokinetic profiles in routine hemophilia care Croteau, Stacy E.; Callaghan, Michael U.; Davis, Joanna; Dunn, Amy L.; Guerrera, Michael; Khan, Osman; Neufeld, Ellis J.; Raffini, Leslie J.; Recht, Michael; Wang, Michael; Iorio, Alfonso 分享 收藏
Physician decision making in selection of second-line treatments in immune thrombocytopenia in children 儿童免疫性血小板减少症二线治疗的医师决策选择 Grace, Rachael F.; Despotovic, Jenny M.; Bennett, Carolyn M.; Bussel, James B.; Neier, Michelle; Neunert, Cindy; Crary, Shelley E.; Pastore, Yves D.; Klaassen, Robert J.; Rothman, Jennifer A.; Hege, Kerry; Breakey, Vicky R.; Rose, Melissa J.; Shimano, Kristin A.; Buchanan, George R.; Geddis, Amy; Haley, Kristina M.; Lorenzana, Adonis; Thompson, Alexis; Jeng, Michael; Neufeld, Ellis J.; Brown, Travis; Forbes, Peter W.; Lambert, Michele P. 分享 收藏
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Rituximab for treatment of inhibitors in haemophilia A A Phase II Study Leissinger, Cindy; Josephson, Cassandra D.; Granger, Suzanne; Konkle, Barbara A.; Kruse-Jarres, Rebecca; Ragni, Margaret V.; Journeycake, Janna M.; Valentino, Leonard; Key, Nigel S.; Gill, Joan C.; McCrae, Keith R.; Neufeld, Ellis J.; Manno, Catherine; Raffini, Leslie; Saxena, Kapil; Torres, Marcela; Marder, Victor; Bennett, Carolyn M.; Assmann, Susan F. 分享 收藏
Safety and pharmacokinetics of the oral iron chelator SP-420 in -thalassemia Taher, Ali T.; Saliba, Antoine N.; Kuo, Kevin H.; Giardina, Patricia J.; Cohen, Alan R.; Neufeld, Ellis J.; Aydinok, Yesim; Kwiatkowski, Janet L.; Jeglinski, Brenda I.; Pietropaolo, Keith; Berk, Gregory; Viprakasit, Vip 分享 收藏