Gurung, Sonam; Timmermand, Oskar Vilhelmsson; Perocheau, Dany; Gil-Martinez, Ana Luisa; Minnion, Magdalena; Touramanidou, Loukia; Fang, Sherry; Messina, Martina; Khalil, Youssef; Spiewak, Justyna; Barber, Abigail R.; Edwards, Richard S.; Pinto, Patricia Lipari; Finn, Patrick F.; Cavedon, Alex; Siddiqui, Summar; Rice, Lisa; Martini, Paolo G. V.; Ridout, Deborah; Heywood, Wendy; Hargreaves, Ian; Heales, Simon; Mills, Philippa B.; Waddington, Simon N.; Gissen, Paul; Eaton, Simon; Ryten, Mina; Feelisch, Martin; Frassetto, Andrea; Witney, Timothy H.; Baruteau, Julien

Systemic gene therapy rescues retinal dysfunction and hearing loss in a model of Norrie disease

EMBO MOLECULAR MEDICINE

IF8.3

2023-08-296

OAAI

Dopamine Transporter Deficiency Syndrome (DTDS): Expanding the Clinical Phenotype and Precision Medicine Approaches

CELLS

IF5.2

2023-06-285

OAAI

Gene Therapy for Dopamine Dyshomeostasis: From Parkinson's to Primary Neurotransmitter Diseases

MOVEMENT DISORDERS

IF7.6

2023-05-055

OAAI

Genomic investigations of unexplained acute hepatitis in children

Nature

IF48.5

2023-03-300

OAAI

Sofia Morfopoulou; Sarah Buddle; Oscar Enrique Torres Montaguth; Laura Atkinson; José Afonso Guerra-Assunção; Mahdi Moradi Marjaneh; Riccardo Zennezini Chiozzi; Nathaniel Storey; Luis Campos; J. Ciaran Hutchinson; John R. Counsell; Gabriele Pollara; Sunando Roy; Cristina Venturini; Juan F. Antinao Diaz; Ala’a Siam; Luke J. Tappouni; Zeinab Asgarian; Joanne Ng; Killian S. Hanlon; Alexander Lennon; Andrew McArdle; Agata Czap; Joshua Rosenheim; Catarina Andrade; Glenn Anderson; Jack C. D. Lee; Rachel Williams; Charlotte A. Williams; Helena Tutill; Nadua Bayzid; Luz Marina Martin Bernal; Hannah Macpherson; Kylie-Ann Montgomery; Catherine Moore; Kate Templeton; Claire Neill; Matt Holden; Rory Gunson; Samantha J. Shepherd; Priyen Shah; Samantha Cooray; Marie Voice; Michael Steele; Colin Fink; Thomas E. Whittaker; Giorgia Santilli; Paul Gissen; Benedikt B. Kaufer; Jana Reich; Julien Andreani; Peter Simmonds; Dimah K. Alrabiah; Sergi Castellano; Primrose Chikowore; Miranda Odam; Tommy Rampling; Catherine Houlihan; Katja Hoschler; Tiina Talts; Cristina Celma; Suam Gonzalez; Eileen Gallagher; Ruth Simmons; Conall Watson; Sema Mandal; Maria Zambon; Meera Chand; James Hatcher; Surjo De; Kenneth Baillie; Malcolm Gracie Semple; Joanne Martin; Ines Ushiro-Lumb; Mahdad Noursadeghi; Maesha Deheragoda; Nedim Hadzic; Tassos Grammatikopoulos; Rachel Brown; Chayarani Kelgeri; Konstantinos Thalassinos; Simon N. Waddington; Thomas S. Jacques; Emma Thomson; Michael Levin; Julianne R. Brown; Judith Breuer

Microfluidic production of nanogels as alternative triple transfection reagents for the manufacture of adeno-associated virus vectors

NANOSCALE

IF5.1

2023-01-015

In Vitro and In Vivo Evaluation of Human Adenovirus Type 49 as a Vector for Therapeutic Applications

人49型腺病毒作为治疗应用载体的体内外评价

VIRUSES-BASEL

IF3.5

2021-07-285

OAAI

Gene therapy restores dopamine transporter expression and ameliorates pathology in iPSC and mouse models of infantile parkinsonism

SCIENCE TRANSLATIONAL MEDICINE

IF14.6

2021-05-1922

Ng, Joanne; Barral, Serena; Barrigon, Carmen De la Fuente; Lignani, Gabriele; Erdem, Fatma A.; Wallings, Rebecca; Privolizzi, Riccardo; Rossignoli, Giada; Alrashidi, Haya; Heasman, Sonja; Meyer, Esther; Ngoh, Adeline; Pope, Simon; Karda, Rajvinder; Perocheau, Dany; Baruteau, Julien; Suff, Natalie; Diaz, Juan Antinao; Schorge, Stephanie; Vowles, Jane; Marshall, Lucy R.; Cowley, Sally A.; Sucic, Sonja; Freissmuth, Michael; Counsell, John R.; Wade-Martins, Richard; Heales, Simon J. R.; Rahim, Ahad A.; Bencze, Maximilien; Waddington, Simon N.; Kurian, Manju A.

Simon N. Waddington

个人简介

教育背景

工作经历

荣誉奖项

研究方向