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S

Simon N. Waddington

university college london

54H指数
394论文数
1.1W被引数
收录论文 118
发表时间
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Safety and efficacy analysis of in vivo lentiviral gene therapy in pre-clinical ARC syndrome models在ARC综合征动物模型中体内慢病毒基因治疗的安全性与有效性分析
errNature Communications
IF15.7
err2026-06-19
err0
errOAAI
errClaudiu A. Cozmescu; Mina Nazari; Loukia Touramanidou; Sonam Gurung; Dany Perocheau; Neil Sebire; Yi-Ting Hu; Sian Goldsworthy; Jemima J. Burden; Youssef Khalil; Ivan Doykov; John R. Counsell; Rajvinder Karda; Sergi Castellano; Philippa Mills; Peter Clayton; Wendy Heywood; Dale Moulding; Simon N. Waddington; Julien Baruteau; Giandomenico Turchiano; Paul Gissen
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Contaminating plasmid sequences and disrupted vector genomes in the liver following adeno-associated virus gene therapy腺相关病毒基因治疗后肝脏中污染的质粒序列和破坏的载体基因组
errNature Medicine
IF50
err2026-01-16
err0
errOAAI
errSarah Buddle; Li-An K. Brown; Sofia Morfopoulou; Oscar Enrique Torres Montaguth; Mariacristina Scoto; Vanessa Herder; Anil Dhawan; Julianne R. Brown; Laura Atkinson; Angelika Kopec; Dee Davis; Nathaniel Storey; Luis Campos; Neil Sebire; Hannah Macpherson; Jasmaine Lee; Richard Orton; Giovanni Baranello; Patawee Asamaphan; Georgios Ilia; Rajvinder Karda; Holly Belfield; John Counsell; Simon N. Waddington; Emma C. Thomson; Francesco Muntoni; Judith Breuer
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Genetic therapies for neurological diseases神经疾病的基因疗法
errPharmacological Reviews
IF17.3
err2025-10-03
err0
errOAAI
errAhad A. Rahim; Manju A. Kurian; Haiyan Zhou; Ross Ferguson; Sarah J. Tabrizi; Gabriele Lignani; Kristian Aquilina; Simon N. Waddington
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Modeling Ascending Vaginal Infection, Preterm Birth, and Neonatal Morbidity in Mice小鼠中上行性阴道感染、早产及新生儿发病率的建模
errJOVE-JOURNAL OF VISUALIZED EXPERIMENTS
IF1
err2025-10-01
err0
PREAI
errBoyle, Ashley K.; Tetorou, Konstantina; Hristova, Mariya; Waddington, Simon N.; Peebles, Donald; Suff, Natalie
err分享
err收藏
Genetic therapies for movement disorders - current status运动障碍的基因疗法 - 当前状态
errJOURNAL OF NEUROLOGY
IF4.6
err2025-02-22
err0
errOAAI
errSartorelli, J.; Ng, J.; Rahim, A. A.; Waddington, S. N.; Kurian, M. A.
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Unifying biology of neurodegeneration in lysosomal storage diseases溶酶体贮积症中神经退行性病变的统一生物学
errJOURNAL OF INHERITED METABOLIC DISEASE
IF3.8
err2025-01-17
err0
errOAAI
errLudlaim, Anna M.; Waddington, Simon N.; Mckay, Tristan R.
err分享
err收藏
Ascending Vaginal Infection in Mice Induces Preterm Birth and Neonatal Morbidity小鼠上行性阴道感染可导致早产及新生儿疾病发病率升高
errAMERICAN JOURNAL OF PATHOLOGY
IF3.6
err2025-01-01
err0
errOAAI
errBoyle, AK; Tetorou, K; Suff, N; Beecroft, L; Mazzaschi, M; Karda, R; Hristova, M; Waddington, SN; Peebles, D
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Macrophage Inhibitor Clodronate Enhances Liver Transduction of Lentiviral but Not Adeno-Associated Viral Vectors or mRNA Lipid Nanoparticles in Neonatal and Juvenile Mice巨噬细胞抑制剂氯膦酸钠增强新生和幼年小鼠慢病毒而不是腺相关病毒载体或mRNA脂质纳米颗粒的肝脏转导
errCELLS
IF5.2
err2024-11-29
err0
errOAAI
errTouramanidou, Loukia; Gurung, Sonam; Cozmescu, Claudiu A.; Perocheau, Dany; Moulding, Dale; Finn, Patrick F.; Frassetto, Andrea; Waddington, Simon N.; Gissen, Paul; Baruteau, Julien
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Human HPSE2 gene transfer ameliorates bladder pathophysiology in a mutant mouse model of urofacial syndrome
errELIFE
IF0
err2024-07-11
err2
errOAAI
errLopes, Filipa M.; Grenier, Celine; Jarvis, Benjamin W.; Al Mahdy, Sara; Lene-McKay, Adrian; Gurney, Alison M.; Newman, William G.; Waddington, Simon N.; Woolf, Adrian S.; Roberts, Neil A.
err分享
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AAV-mediated expression of mouse or human GLDC normalises metabolic biomarkers in a GLDC-deficient mouse model of Non-Ketotic Hyperglycinemia
errMOLECULAR GENETICS AND METABOLISM
IF3.5
err2024-07-01
err1
errOAAI
errLeung, Kit-Yi; Santos, Chloe; De Castro, Sandra C. P.; Diaz, Diana Gold; Copp, Andrew J.; Waddington, Simon; Greene, Nicholas D. E.
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Dysregulated Wnt and NFAT signaling in a Parkinson's disease LRRK2 G2019S knock-in model帕金森病LRRK2 G2019S敲入模型中Wnt和NFAT信号的失调
errSCIENTIFIC REPORTS
IF3.9
err2024-05-29
err5
errOAAI
errWetzel, Andrea; Lei, Si Hang; Liu, Tiansheng; Hughes, Michael P.; Peng, Yunan; McKay, Tristan; Waddington, Simon N.; Granno, Simone; Rahim, Ahad A.; Harvey, Kirsten
err分享
err收藏
Comparison of different promoters to improve AAV vector-mediated gene therapy for neuronopathic Gaucher disease
errHUMAN MOLECULAR GENETICS
IF3.2
err2024-05-16
err1
errOAAI
errMassaro, Giulia; Geard, Amy F.; Nelvagal, Hemanth R.; Gore, Katrina; Clemo, Nadine K.; Waddington, Simon N.; Rahim, Ahad A.
err分享
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mRNA therapy corrects defective glutathione metabolism and restores ureagenesis in preclinical argininosuccinic aciduria
errSCIENCE TRANSLATIONAL MEDICINE
IF14.6
err2024-01-10
err8
errOAAI
errGurung, Sonam; Timmermand, Oskar Vilhelmsson; Perocheau, Dany; Gil-Martinez, Ana Luisa; Minnion, Magdalena; Touramanidou, Loukia; Fang, Sherry; Messina, Martina; Khalil, Youssef; Spiewak, Justyna; Barber, Abigail R.; Edwards, Richard S.; Pinto, Patricia Lipari; Finn, Patrick F.; Cavedon, Alex; Siddiqui, Summar; Rice, Lisa; Martini, Paolo G. V.; Ridout, Deborah; Heywood, Wendy; Hargreaves, Ian; Heales, Simon; Mills, Philippa B.; Waddington, Simon N.; Gissen, Paul; Eaton, Simon; Ryten, Mina; Feelisch, Martin; Frassetto, Andrea; Witney, Timothy H.; Baruteau, Julien
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Systemic gene therapy rescues retinal dysfunction and hearing loss in a model of Norrie disease
errEMBO MOLECULAR MEDICINE
IF8.3
err2023-08-29
err6
errOAAI
errPauzuolyte, Valda; Patel, Aara; Wawrzynski, James R.; Ingham, Neil J.; Leong, Yeh Chwan; Karda, Rajvinder; Bitner-Glindzicz, Maria; Berger, Wolfgang; Waddington, Simon N.; Steel, Karen P.; Sowden, Jane C.
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Dopamine Transporter Deficiency Syndrome (DTDS): Expanding the Clinical Phenotype and Precision Medicine Approaches
errCELLS
IF5.2
err2023-06-28
err5
errOAAI
errNg, Joanne; Barral, Serena; Waddington, Simon N.; Kurian, Manju A.
err分享
err收藏
Gene Therapy for Dopamine Dyshomeostasis: From Parkinson's to Primary Neurotransmitter Diseases
errMOVEMENT DISORDERS
IF7.6
err2023-05-05
err5
errOAAI
errNg, Joanne; Barral, Serena; Waddington, Simon N.; Kurian, Manju A.
err分享
err收藏
Microfluidic production of nanogels as alternative triple transfection reagents for the manufacture of adeno-associated virus vectors
errNANOSCALE
IF5.1
err2023-01-01
err5
errOAAI
errWhiteley, Zoe; Massaro, Giulia; Gkogkos, Georgios; Gavriilidis, Asterios; Waddington, Simon N.; Rahim, Ahad A.; Craig, Duncan Q. M.
err分享
err收藏
In Vitro and In Vivo Evaluation of Human Adenovirus Type 49 as a Vector for Therapeutic Applications人49型腺病毒作为治疗应用载体的体内外评价
errVIRUSES-BASEL
IF3.5
err2021-07-28
err5
errOAAI
errBates, Emily A.; Counsell, John R.; Alizert, Sophie; Baker, Alexander T.; Suff, Natalie; Boyle, Ashley; Bradshaw, Angela C.; Waddington, Simon N.; Nicklin, Stuart A.; Baker, Andrew H.; Parker, Alan L.
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err收藏
Gene therapy restores dopamine transporter expression and ameliorates pathology in iPSC and mouse models of infantile parkinsonism
errSCIENCE TRANSLATIONAL MEDICINE
IF14.6
err2021-05-19
err22
errOAAI
errNg, Joanne; Barral, Serena; Barrigon, Carmen De la Fuente; Lignani, Gabriele; Erdem, Fatma A.; Wallings, Rebecca; Privolizzi, Riccardo; Rossignoli, Giada; Alrashidi, Haya; Heasman, Sonja; Meyer, Esther; Ngoh, Adeline; Pope, Simon; Karda, Rajvinder; Perocheau, Dany; Baruteau, Julien; Suff, Natalie; Diaz, Juan Antinao; Schorge, Stephanie; Vowles, Jane; Marshall, Lucy R.; Cowley, Sally A.; Sucic, Sonja; Freissmuth, Michael; Counsell, John R.; Wade-Martins, Richard; Heales, Simon J. R.; Rahim, Ahad A.; Bencze, Maximilien; Waddington, Simon N.; Kurian, Manju A.
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Beclin-1-mediated activation of autophagy improves proximal and distal urea cycle disorders
errEMBO MOLECULAR MEDICINE
IF8.3
err2020-12-28
err19
errOAAI
errSoria, Leandro R.; Gurung, Sonam; De Sabbata, Giulia; Perocheau, Dany P.; De Angelis, Angela; Bruno, Gemma; Polishchuk, Elena; Paris, Debora; Cuomo, Paola; Motta, Andrea; Orford, Michael; Khalil, Youssef; Eaton, Simon; Mills, Philippa B.; Waddington, Simon N.; Settembre, Carmine; Muro, Andres F.; Baruteau, Julien; Brunetti-Pierri, Nicola
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研究方向

暂时未获取到该数据
合作学者
合作期刊
N
Nico van Rooijen
H 指数: 165 · 论文数: 1.0K
R
Roderick T. Bronson
H 指数: 164 · 论文数: 1.1K
A
Anthony H.V. Schapira
H 指数: 127 · 论文数: 902
A
A. David Edwards
H 指数: 113 · 论文数: 824
C
Christof von Kalle
H 指数: 110 · 论文数: 602
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