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The Use of Durable Medical Equipment in COURAGE-ALS, a Phase 3, Multicentre, Randomized Clinical Trial for ALS COURAGE-ALS试验中耐用医疗设备的使用:一项针对ALS的III期、多中心、随机临床试验 Rudnicki, Stacy A.; Giacomelli, Elisa; Herder, Katherine; Ingre, Caroline; Kupfer, Stuart; Malik, Fady I.; Meng, Lisa; Paganoni, Sabrina; Schellenberg, Kerri; Scirocco, Erica; Simkins, Tyrell; Wei, Jenny; Shefner, Jeremy M. 分享 收藏
Pridopidine treatment in ALS: subgroup analyses from the HEALEY ALS Platform trial 普利多匹定治疗ALS: 来自HEALEY ALS平台试验的亚组分析 Geva, Michal; Goldberg, Y. Paul; Leitner, Melanie L.; Cruz-Herranz, Andres; Hand, Randal; Chen, Kelly; Gershoni Emek, Noga; Tan, Andrew M.; Paganoni, Sabrina; Berry, James D.; Macklin, Eric A.; Shefner, Jeremy M.; Cudkowicz, Merit E.; Hayden, Michael R. 分享 收藏
Participant, site personnel and sponsor perspectives on decentralized trial features in COURAGE-ALS: a randomized clinical trial 参与者、研究现场人员及申办方对于COURAGE-ALS试验中分散化试验特征的观点:一项随机临床试验 Rudnicki, Stacy A.; Gebrehiwet, Paulos; Kupfer, Stuart; Malik, Fady I.; Meng, Lisa; Simkins, Tyrell; Wei, Jenny; Wolff, Andrew A.; Shefner, Jeremy M. 分享 收藏
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Reldesemtiv in Amyotrophic Lateral Sclerosis: Results From the COURAGE-ALS Randomized Clinical Trial 利德尔西米夫在肌萎缩侧索硬化症中的应用:COURAGE-ALS随机临床试验的结果 Shefner, Jeremy M.; Cudkowicz, Merit E.; Genge, Angela; Hardiman, Orla; Al-Chalabi, Ammar; Andrews, Jinsy A.; Chio, Adriano; Corcia, Philippe; Couratier, Philippe; de Carvalho, Mamede; Heiman-Patterson, Terry; Henderson, Robert D.; Ingre, Caroline; Johnston, Wendy; Ludolph, Albert; Maragakis, Nicholas J.; Miller, Timothy M.; Mora, Jesus S.; Petri, Susanne; Simmons, Zachary; van den Berg, Leonard H.; Zinman, Lorne; Kupfer, Stuart; Malik, Fady I.; Meng, Lisa; Simkins, Tyrell J.; Wei, Jenny; Wolff, Andrew A.; Rudnicki, Stacy A.; COURAGE ALS Study Grp 分享 收藏
Efficacy and Safety of Zilucoplan in Amyotrophic Lateral Sclerosis, A Randomized Clinical Trial Zilucoplan治疗肌萎缩侧索硬化症的疗效与安全性:一项随机临床试验 Paganoni, Sabrina; Fournier, Christina N.; Macklin, Eric A.; Chibnik, Lori B.; Quintana, Melanie; Saville, Benjamin R.; Detry, Michelle A.; Vestrucci, Matteo; Marion, Joe; Mcglothlin, Anna; Ajroud-Driss, Senda; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A.; Yu, Hong; Sherman, Alexander V.; Shefner, Jeremy M.; Hall, Meghan; Kittle, Gale; Berry, James D.; Babu, Suma; Andrews, Jinsy; Dagostino, Derek; Tustison, Eric; Giacomelli, Elisa; Scirocco, Erica; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H.; Shroff, Sheetal; Felice, Kevin; Maragakis, Nicholas J.; Simmons, Zachary; Miller, Timothy M.; Olney, Nicholas; Weiss, Michael D.; Goutman, Stephen A.; Fernandes, Joseph Americo; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura A.; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S.; Arcila-Londono, Ximena; Jackson, Carlayne E.; Ladha, Shafeeq; Heiman-Patterson, Terry; Caress, James B.; Swenson, Andrea; Peltier, Amanda; Lewis, Richard; Fee, Dominic; Elliott, Matthew; Kasarskis, Edward J.; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; Mcilduff, Courtney; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A.; Cohen, Jeffrey A.; Benatar, Michael; Jones, Vovanti; Glass, Jonathan; Shah, Jaimin; Beydoun, Said R.; Wymer, James P.; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L.; Martinez-Thompson, Jennifer; Harvey, Brittany; Patel, Shital; Mahoney, Paul; Duda, Petra W.; Cudkowicz, Merit E. 分享 收藏
Guidance for clinical management of pathogenic variant carriers at elevated genetic risk for ALS/FTD ALS/FTD遗传风险升高的致病性变异携带者的临床管理指南 Benatar, Michael; Heiman-Patterson, Terry D.; Cooper-Knock, Johnathan; Brickman, Daniel; Casaletto, Kaitlin B.; Goutman, Stephen A.; Vinceti, Marco; Dratch, Laynie; Arias, Jalayne J.; Swidler, Jean; Turner, Martin R.; Shefner, Jeremy; Westeneng, Henk-Jan; van den Berg, Leonard H.; Al-Chalabi, Ammar 分享 收藏
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The Miami Framework for ALS and related neurodegenerative disorders: an integrated view of phenotype and biology (May, 10.1038/s41582-024-00961-z, 2024) Benatar, Michael; Wuu, Joanne; Huey, Edward D.; Mcmillan, Corey T.; Petersen, Ronald C.; Postuma, Ronald; McHutchison, Caroline; Dratch, Laynie; Arias, Jalayne J.; Crawley, Anita; Houlden, Henry; McDermott, Michael P.; Cai, Xueya; Thakur, Neil; Boxer, Adam; Rosen, Howard; Boeve, Bradley F.; Dacks, Penny; Cosentino, Stephanie; Abrahams, Sharon; Shneider, Neil; Lingor, Paul; Shefner, Jeremy; Andersen, Peter M.; Al-Chalabi, Ammar; Turner, Martin R. 分享 收藏
The Miami Framework for ALS and related neurodegenerative disorders: an integrated view of phenotype and biology Benatar, Michael; Wuu, Joanne; Huey, Edward D.; Mcmillan, Corey T.; Petersen, Ronald C.; Postuma, Ronald; Mchutchison, Caroline; Dratch, Laynie; Arias, Jalayne J.; Crawley, Anita; Houlden, Henry; McDermott, Michael P.; Cai, Xueya; Thakur, Neil; Boxer, Adam; Rosen, Howard; Boeve, Bradley F.; Dacks, Penny; Cosentino, Stephanie; Abrahams, Sharon; Shneider, Neil; Lingor, Paul; Shefner, Jeremy; Andersen, Peter M.; Al-Chalabi, Ammar; Turner, Martin R.; Allred, Peggy; Appel, Stanley; Benatar, David; Berry, James; Bradbury, Meg; Bruijn, Lucie; Buczyner, Jennifer; Carberry, Nathan; Caress, James; Champney, Thomas; Dave, Kuldip; Fradette, Stephanie; Granit, Volkan; Grignon, Anne-Laure; Gubitz, Amelie; Harms, Matthew; Heiman-Patterson, Terry; Hesterlee, Sharon; Lawrence, Karen; Lewis, Travis; Levy, Oren; Lingor, Paul; Mozaffar, Tahseen; Stanislaw, Christine; Thompson, Alexander; Uspenskay, Olga; Weydt, Patrick; Zinman, Lorne 分享 收藏
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Skeletal muscle in amyotrophic lateral sclerosis Shefner, Jeremy M.; Musaro, Antonio; Ngo, Shyuan T.; Lunetta, Christian; Steyn, Frederik J.; Robitaille, Richard; De Carvalho, Mamede; Rutkove, Seward; Ludolph, Albert C.; Dupuis, Luc 分享 收藏
Evidence for Survival Benefit in ALS with CNM-Au8 Treatment Across Three Study Populations Berry, James; Maragakis, Nicholas; Paganoni, Sabrina; Quintana, Melanie; Macklin, Eric; Saville, Benjamin; Andrews, Jinsy; Shefner, Jeremy; Detry, Michelle; Menon, Parvathi; Huynh, William; Mahoney, Colin; Stommel, Elijah; Hall, Meghan; Connolly, Mariah; Kittle, Gale; Chase, Marianne; Sherman, Alexander; Yu, Hong; Pothier, Lindsay; Drake, Kristin; Chibnik, Lori; Bind, Marie-Abele; Vestrucci, Matteo; Glanzman, Robert; Hotchkin, Michael; Vucic, Steve; Kiernan, Matthew; Cudkowicz, Merit 分享 收藏
Results from the first four regimens of the HEALEY ALS Platform Trial Paganoni, Sabrina; Berry, James; Quintana, Melanie; Macklin, Eric; Saville, Benjamin; Andrews, Jinsy; Shefner, Jeremy; Fournier, Christina; Babu, Suma; Maragakis, Nicholas; Oskarsson, Bjorn; Detry, Michelle; Chase, Marianne; Sherman, Alex; Yu, Hong; Pothier, Lindsay; Drake, Kristin; Chibnik, Lori; Bind, Marie-Abele; Vestrucci, Matteo; McGlothlin, Anna; Marion, Joseph; Duda, Petra; Harvey, Brittany; Qureshi, Irfan; Donohue, Mary; Granit, Volkan; Grossman, Katheryn; Glanzman, Robert; Hotchkin, Michael; Goldberg, Y. Paul; Leitner, Melanie; Hayden, Michael; Cudkowicz, Merit 分享 收藏
Interim Safety Profile From the Feasibility Study of the BrainGate Neural Interface System 来自BrainGate神经接口系统可行性研究的临时安全性概况 Rubin, Daniel B.; Ajiboye, A. Bolu; Barefoot, Laurie; Bowker, Marguerite; Cash, Sydney S.; Chen, David; Donoghue, John P.; Eskandar, Emad N.; Friehs, Gerhard; Grant, Carol; Henderson, Jaimie M.; Kirsch, Robert F.; Marujo, Rose; Masood, Maryam; Mernoff, Stephen T.; Miller, Jonathan P.; Mukand, Jon A.; Penn, Richard D.; Shefner, Jeremy; Shenoy, Krishna V.; Simeral, John D.; Sweet, Jennifer A.; Walter, Benjamin L.; Williams, Ziv M.; Hochberg, Leigh R. 分享 收藏
Effect of sodium phenylbutyrate/taurursodiol on tracheostomy/ventilation-free survival and hospitalisation in amyotrophic lateral sclerosis: long-term results from the CENTAUR trial Paganoni, Sabrina; Hendrix, Suzanne; Dickson, Samuel P.; Knowlton, Newman; Berry, James D.; Elliott, Michael A.; Maiser, Samuel; Karam, Chafic; Caress, James B.; Owegi, Margaret Ayo; Quick, Adam; Wymer, James; Goutman, Stephen A.; Heitzman, Daragh; Heiman-Patterson, Terry D.; Jackson, Carlayne; Quinn, Colin; Rothstein, Jeffrey D.; Kasarskis, Edward J.; Katz, Jonathan; Jenkins, Liberty; Ladha, Shafeeq S.; Miller, Timothy M.; Scelsa, Stephen N.; Vu, Tuan H.; Fournier, Christina; Johnson, Kristin M.; Swenson, Andrea; Goyal, Namita; Pattee, Gary L.; Babu, Suma; Chase, Marianne; Dagostino, Derek; Hall, Meghan; Kittle, Gale; Eydinov, Mathew; Ostrow, Joseph; Pothier, Lindsay; Randall, Rebecca; Shefner, Jeremy M.; Sherman, Alexander, V; Tustison, Eric; Vigneswaran, Prasha; Yu, Hong; Cohen, Joshua; Klee, Justin; Tanzi, Rudolph; Gilbert, Walter; Yeramian, Patrick; Cudkowicz, Merit 分享 收藏
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