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Long-Term Safety and Efficacy of Gene Therapy for Adenosine Deaminase Deficiency 腺苷脱氨酶缺乏症的基因治疗长期安全性与有效性 Booth, Claire; Masiuk, Katelyn; Vazouras, Konstantinos; Fernandes, Augustine; Xu-Bayford, Jinhua; Campo Fernandez, Beatriz; Roy, Sohini; Curio-Penny, Beatrice; Arnold, Jordyn; Terrazas, Dayna; Reid, Jack; Gilmour, Kimberly C.; Adams, Stuart; Alvarez Mediavilla, Elena; Mhaldien, Lana; O'Toole, Grainne; Ahmed, Rima; Garabedian, Elizabeth; Malech, Harry; De Ravin, Suk See; Moore, Theodore B.; De Oliveira, Satiro; Pellin, Danilo; Lin, Tsai-Yu; Dang, Thao Thi; Cornetta, Kenneth; Hershfield, Michael S.; Hara, Havinder; Thrasher, Adrian J.; Gaspar, H. Bobby; Kohn, Donald B. 分享 收藏
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Bioinformatic Analysis of the Genetic Basis of Differential Adeno-Associated Virus Production Capability of 293 Variants 293变体中腺相关病毒生产能力差异的遗传基础生物信息学分析 Herzog, Christopher R.; Zhang, Junping; Feng, Xiaomin; Dang, Thao Thi; Yu, Xiangping; Huang, Jie; Fang, Fang; Gao, Hongyu; Yu, Xuhong; Wang, Yue; Han, Renzhi; Liu, Yulong; Cornetta, Kenneth; Xiao, Weidong; Xu, Weihong 分享 收藏
The translational gap for gene therapies in low- and middle-income countries Doxzen, Kevin W.; Adair, Jennifer E.; Fonseca Bazzo, Yris Maria; Bukini, Daima; Cornetta, Kenneth; Dalal, Varsha; Guerino-Cunha, Renato Luiz; Hongeng, Suradej; Jotwani, Geeta; Kityo-Mutuluuza, Cissy; Lakshmanan, Krishnamurti; Mahlangu, Johnny; Makani, Julie; Mathews, Vikram; Ozelo, Margareth C.; Rangarajan, Savita; Scholefield, Janine; Silva Junior, Joao Batista; Mccune, Joseph M. 分享 收藏
Implementation of a gene therapy education initiative by the ASGCT and Muhimbili University of Health and Allied Sciences Cornetta, Kenneth; Kay, Samantha; Urio, Florence; Minja, Irene Kida; Mbugi, Erasto; Mgaya, Josephine; Mselle, Teddy; Nkya, Siana; Alimohamed, Mohamed Zahir; Ndaki, Kinuma; Bonamino, Martin; Koya, Richard C.; Shah, Lesha D.; Mahlangu, Johnny; Drago, Daniela; Rangarajan, Savita; Jayandharan, Giridhara Rao 分享 收藏
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Replication competent retrovirus testing (RCR) in the National Gene Vector Biorepository: No evidence of RCR in 1,595 post-treatment peripheral blood samples obtained from 60 clinical trials Cornetta, Kenneth; Yao, Jing; House, Kimberley; Duffy, Lisa; Adusumilli, Prasad S.; Beyer, Rachel; Booth, Claire; Brenner, Malcolm; Curran, Kevin; Grilley, Bambi; Heslop, Helen; Hinrichs, Christian S.; Kaplan, Rosandra N.; Kiem, Hans-Peter; Kochenderfer, James; Kohn, Donald B.; Mailankody, Sham; Norberg, Scott M.; O'Cearbhaill, Roisin E.; Pappas, Jennifer; Park, Jae; Ramos, Carlos; Ribas, Antonio; Riviere, Isabelle; Rosenberg, Steven A.; Sauter, Craig; Shah, Nirali N.; Slovin, Susan F.; Thrasher, Adrian; Williams, David A.; Lin, Tsai-Yu 分享 收藏
Gene therapy access: Global challenges, opportunities, and views from Brazil, South Africa, and India Cornetta, Kenneth; Bonamino, Martin; Mahlangu, Johnny; Mingozzi, Federico; Rangarajan, Savita; Rao, Jayandharan 分享 收藏
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Electroceutical fabric lowers zeta potential and eradicates coronavirus infectivity upon contact Ghatak, Subhadip; Khona, Dolly K.; Sen, Abhishek; Huang, Kaixiang; Jagdale, Gargi; Singh, Kanhaiya; Gopalakrishnan, Vinoj; Cornetta, Kenneth G.; Roy, Sashwati; Khanna, Savita; Baker, Lane A.; Sen, Chandan K. 分享 收藏
Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency 自体慢病毒基因治疗腺苷脱氨酶缺乏症 Kohn, D. B.; Booth, C.; Shaw, K. L.; Xu-Bayford, J.; Garabedian, E.; Trevisan, V.; Carbonaro-Sarracino, D. A.; Soni, K.; Terrazas, D.; Snell, K.; Ikeda, A.; Leon-Rico, D.; Moore, T. B.; Buckland, K. F.; Shah, A. J.; Gilmour, K. C.; De Oliveira, S.; Rivat, C.; Crooks, G. M.; Izotova, N.; Tse, J.; Adams, S.; Shupien, S.; Ricketts, H.; Davila, A.; Uzowuru, C.; Icreverzi, A.; Barman, P.; Fernandez, B. Campo; Hollis, R. P.; Coronel, M.; Yu, A.; Chun, K. M.; Casas, C. E.; Zhang, R.; Arduini, S.; Lynn, F.; Kudari, M.; Spezzi, A.; Zahn, M.; Heimke, R.; Labik, I.; Parrott, R.; Buckley, R. H.; Reeves, L.; Cornetta, K.; Sokolic, R.; Hershfield, M.; Schmidt, M.; Candotti, F.; Malech, H. L.; Thrasher, A. J.; Gaspar, H. B. 分享 收藏
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Transitioning from development to commercial: risk-based guidance for critical materials management in cell therapies Scott, Michael; Clarke, Dominic; Lipsitz, Yonatan; Brandwein, Harvey; Allickson, Julie; Alzebdeh, Dalia; Aleksic, Sasha; Kraft, Crystal; Lhu, Lexan; Cornetta, Kenneth 分享 收藏
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IND-Enabling Studies for a Clinical Trial to Genetically Program a Persistent CancerTargeted Immune System Puig-Saus, Cristina; Parisi, Giulia; Garcia-Diaz, Angel; Krystofinski, Paige E.; Sandoval, Salemiz; Zhang, Ruixue; Champhekar, Ameya S.; McCabe, James; Cheung-Lau, Gardenia C.; Truong, Nhat A.; Vega-Crespo, Agustin; Komenan, Marie Desiles S.; Pang, Jia; Macabali, Mignonette H.; Saco, Justin D.; Goodwin, Jeffrey L.; Bolon, Brad; Seet, Christopher S.; Montel-Hagen, Amelie; Crooks, Gay M.; Hollis, Roger P.; Campo-Fernandez, Beatriz; Bischof, Daniela; Cornetta, Kenneth; Gschweng, Eric H.; Adelson, Celia; Nguyen, Alexander; Yang, Lili; Witte, Owen N.; Baltimore, David; Comin-Anduix, Begonya; Kohn, Donald B.; Wang, Xiaoyan; Cabrera, Paula; Kaplan-Lefko, Paula J.; Berent-Maoz, Beata; Ribas, Antoni 分享 收藏
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Absence of Replication-Competent Lentivirus in the Clinic: Analysis of Infused T Cell Products 临床中缺乏具有复制能力的慢病毒: 输注T细胞产物的分析 Cornetta, Kenneth; Duffy, Lisa; Turtle, Cameron J.; Jensen, Michael; Forman, Stephen; Binder-Scholl, Gwendolyn; Fry, Terry; Chew, Anne; Maloney, David G.; June, Carl H. 分享 收藏