未登录 Circulatory CCL2 distinguishes Duchenne muscular dystrophy dogs 循环CCL2区分Duchenne肌营养不良的狗 Perez-Lopez, Dennis O.; Burke, Matthew J.; Hakim, Chady H.; Teixeira, James A.; Han, Jin; Yue, Yongping; Ren, Zewei; Sun, Jianguo; Chen, Shi-jie; Herzog, Roland W.; Yao, Gang; Duan, Dongsheng 分享 收藏
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Dwarf Open Reading Frame (DWORF) Gene Therapy Ameliorated Duchenne Muscular Dystrophy Cardiomyopathy in Aged mdx Mice 矮人开放阅读框 (DWORF) 基因治疗改善老年mdx小鼠的杜氏肌营养不良性心肌病 Morales, Emily D.; Yue, Yongping; Watkins, Thais B.; Han, Jin; Pan, Xiufang; Gibson, Aaron M.; Hu, Bryan; Brito-Estrada, Omar; Yao, Gang; Makarewich, Catherine A.; Babu, Gopal J.; Duan, Dongsheng 分享 收藏
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Cas9-specific immune responses compromise local and systemic AAV CRISPR therapy in multiple dystrophic canine models Hakim, Chady H.; Kumar, Sandeep R. P.; Perez-Lopez, Dennis O.; Wasala, Nalinda B.; Zhang, Dong; Yue, Yongping; Teixeira, James; Pan, Xiufang; Zhang, Keqing; Million, Emily D.; Nelson, Christopher E.; Metzger, Samantha; Han, Jin; Louderman, Jacqueline A.; Schmidt, Florian; Feng, Feng; Grimm, Dirk; Smith, Bruce F.; Yao, Gang; Yang, N. Nora; Gersbach, Charles A.; Chen, Shi-jie; Herzog, Roland W.; Duan, Dongsheng 分享 收藏
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AAV9 Edits Muscle Stem Cells in Normal and Dystrophic Adult Mice Nance, Michael E.; Shi, Ruicheng; Hakim, Chady H.; Wasala, Nalinda B.; Yue, Yongping; Pan, Xiufang; Zhang, Tracy; Robinson, Carolyn A.; Duan, Sean X.; Yao, Gang; Yang, N. Nora; Chen, Shi-jie; Wagner, Kathryn R.; Gersbach, Charles A.; Duan, Dongsheng 分享 收藏
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Alterations in the expression of Hs1-associated protein X-1 in the rat retina after optic nerve crush Cui, Ling; He, Wen-Jing; Xu, Fan; Jiang, Li; Lv, Ming-Liang; Huang, Hui; Xu, Ji-Ping; Wu, Yu; Zhong, Hai-Bin; Zhang, Shao-Yang; Chen, Li-Fei; Shen, Chao-Lan; Yao, Gang; Li, Li; Li, Min; Zeng, Si-Ming 分享 收藏
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Enzyme replacement therapy delays pupillary light reflex deficits in a canine model of late infantile neuronal ceroid lipofuscinosis Whiting, Rebecca E. H.; Narfstroem, Kristina; Yao, Gang; Pearce, Jacqueline W.; Coates, Joan R.; Castaner, Leilani J.; Jensen, Cheryl A.; Dougherty, Brittanie N.; Vuillemenot, Brian R.; Kennedy, Derek; O'Neill, Charles A.; Katz, Martin L. 分享 收藏
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