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Gene therapy in advanced metachromatic leukodystrophy: tempering expectations

delete2024-11-28
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D
Daphne H. Schoenmakers *
S
Shanice Beerepoot
L
Laura Adang
M
Marije A B C Asbreuk
C
Caroline G. Bergner
A
Annette Bley
J
Jaap Jan Boelens
V
Valeria Calbi
A
Alejandra Darling
E
Erik A. Eklund
Á
Ángeles García Cazorla
S
Sabine Grønborg
S
Samuel Groeschel
P
Peter M. van Hasselt
C
Carla E. M. Hollak
C
Claire Horgan
S
Simon Jones
T
Tom de Koning
L
Lucia Laugwitz
C
Caroline A. Lindemans
P
Pascal Martin
F
Fanny Mochel
A
Andreas Øberg
D
Dipak Ram
C
Caroline Sevin
L
Lüdger Schöls
A
Ayelet Zerem
N
Nicole I. Wolf
F
Francesca Fumagalli
DOI:10.1093/procel/pwae065delete
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Abstract

Abstract

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Keywords:
CELL TRANSPLANTATION
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Journal

Protein and Cell cover
Protein and Cell
IF:
12.8
Papers:
1.6K
Citations:
8.6K

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