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Amyloid-Journal of Protein Folding Disorders

IF7.4
Papers1437
Citations2448
Journal Papers 2521
Publication Date
Emerging therapies and translational tools for drug development in systemic amyloidosis: insights from the International Society of Amyloidosis Scientific Workshop
delete2026-10-05
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deleteGareth J. Morgan; Angela Dispenzieri; Jing Fu; Richard M. Giadone; Jeffery W. Kelly; Suzanne Lentzsch; Mathew S. Maurer; Stefano Ricagno; Christophe Sirac; Ashutosh D. Wechalekar
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Cryo-EM reveals untwisted and non-periodic twist fibrils in ex vivo type B ATTRv-V30M fibrils
delete2026-09-30
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deleteShumaila  Afrin; Maria del Carmen Fernandez-Ramirez; Binh An Nguyen; Saylor Schreiber; Barbara Kluve-Beckerman; Lorena Saelices
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Frailty is a mortality risk factor in tafamidis-treated patients with transthyretin cardiac amyloidosis
delete2026-09-10
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deleteAmaury Broussier; Amira Zaroui; Mounira Kharoubi; Silvia Oghina; Charlotte Lafont; Marie Laurent; Nina Liu; Nathalie Marie-Nelly; Jean-Philippe David; Emmanuel Teiger; Sylvie Bastuji Garin; Thibaud Damy
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Sodium-glucose cotransporter-2 inhibitor therapy and body composition analysis in transthyretin amyloid cardiomyopathy: a prospective, feasibility pilot study
delete2026-09-08
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deleteAni Nalbandian; Sergio Teruya; Dia Smiley; Stephen Helmke; Hirad Yarmohammadi; Margaret Cuomo; Jeffeny De Los Santos; Kimberly Mateo Collado; Maxine Ashby-Thompson; Wen W. Yu; Alfonsina Mirabal Santos; Carlos Rodriguez; Denisse Santana Del Rosario; Elissa Driggin; Helene Maltz; Utpal Pajvani; Jai Radhakrishnan; Jonathan Barasch; Dympna Gallagher; Mathew S. Maurer
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Liver stiffness in AL amyloidosis: interest in diagnosis and prognosis
delete2026-09-06
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deletePaul Carrier; Véronique Loustaud-Ratti; Jean-François Cadranel; Céline Rigaud; Bienvenue Randrianarivo; David Lavergne; Laurent Alric; Aurore Baron; Eric Nguyen Khac; Arnaud Pauwels; Louis Bettan; Xavier Causse; Honoré Zougmoure; Abdelali El Kharrazi; Marilyne Debette-Gratien; Anne Cypierre; Murielle Roussel; Arnaud Jaccard
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Susceptibility and screening approaches in systemic amyloidosis: expert perspectives from the International Society of Amyloidosis (ISA)
delete2026-09-04
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deleteTaxiarchis Kourelis; Raymond Comenzo; Andrea Cortese; Justin L. Grodin; Martha Grogan; Paolo Milani; Frederick L. Ruberg; Yoshiki Sekijima; Lukas D. Weberling; Efstathios Kastritis; Kevin M. Alexander
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Gastric amyloid pathology and mucosal denervation in ATTRv amyloidosis: insights from patients, mice, and gut microenvironment profiles
delete2026-08-29
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deleteHsueh-Wen Hsueh; Ping-Hao Yang; Ping-Huei Tseng; Ti-Yen Yeh; Hao-Chia Hsu; Chieh‐Chang Chen; Chia-Lang Hsu; Ya‐Yin Cheng; Tsai-Wei Ting; Cheng-Chen Lin; Hui-Fang Ke; Ching-Hua Kuo; Chi‐Chao Chao; Koping Chang; Sung‐Tsang Hsieh
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Clinical significance of gastric food residue in gastrointestinal hereditary transthyretin amyloidosis
delete2026-08-04
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PREAI
deleteTakuma Okamura; Yugo Iwaya; Nagaaki Katoh; Yoshiki Sekijima; Hiroyoshi Ota; Tadanobu Nagaya
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Diagnostic utility of deep excisional skin biopsy including abdominal fat for transthyretin cardiac amyloidosis
delete2026-07-30
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deleteKohei Honda; Ikoi Omatsu; Tetsuhiro Yamano; Hironobu Naiki; Ayano Maruyama; Yukiko Morinaga; Noriyuki Tanaka; Aya Miyagawa-Hayashino
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Fewer gastrointestinal events with vutrisiran versus placebo in patients with transthyretin amyloidosis with cardiomyopathy: analysis from the phase 3 HELIOS-B study
delete2026-07-17
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deleteMarcus A. Urey; Quan M. Bui; Laura Obici; Jonas Wixner; Erwan Donal; Hiroaki Kitaoka; Ainara Lozano-Bahamonde; Shaun Bender; Katherine L. Boyle; Emre Aldinc; Caroline Morbach
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Progressive leptomeningeal involvement on gadolinium-enhanced FLAIR MRI in hereditary transthyretin amyloidosis with the V30M (p.V50M) mutation
delete2026-07-17
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deleteYohei Misumi; Toshiya Nomura; Tomoaki Taguchi; Shiori Yamakawa; Hiroyuki Uetani; Masayoshi Tasaki; Konen Obayashi; Taro Yamashita; Toshinori Hirai; Yukio Ando; Mitsuharu Ueda
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Guidelines for the management of hereditary ATTR amyloidosis 2026
delete2026-07-09
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deleteYoshiki Sekijima; Mitsuharu Ueda; John L. Berk; Laura Obici; Ronald M. Witteles; Violaine Planté-Bordeneuve; Markus Weiler; Marianna Fontana; Márcia Waddington Cruz; Teresa Coelho; Bo-Göran Ericzon; Pablo Garcia-Pavia; João Beirão; Jonas Wixner; Luísa Lobato; Yukio Ando; Giampaolo Merlini; Mathew S. Maurer
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Hepatic multimodal phenotyping in AL amyloidosis with cardiac involvement: the D-Amy-LIPHE study
delete2026-07-06
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deleteAnna Sessa; Amira Zaroui; Margaux Charles; Stefano Caruso; Julien Calderaro; Jeremy Augustin; Mounira Kharoubi; François Lemonnier; Karim Belhadj; Xue Shaodian; Sébastien Mulé; Emmanuel Itti; Thibaud Damy; Vincent Leroy
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Fat aspiration for amyloidosis screening of 2830 patients from 2013 to 2020: compelling sensitivity for AL and better sensitivity in females for all major subtypes
delete2026-06-26
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deleteChristoph Richard Kimmich; Stefan O. Schönland; Norbert Blank; Tobias Dittrich; Kaya Veelken; Carsten Müller-Tidow; Johan Bijzet; Hans LA Nienhuis; Bouke P. Hazenberg; Ute Hegenbart
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Proteostasis is disrupted in human endothelial cells by serum from ATTR patients and is rescued by tafamidis treatment
delete2026-06-26
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deleteDespoina D. Gianniou; Dimitrios Delialis; Georgios Georgiopoulos; Dimitrios Bampatsias; Eirini Gkogkou; Foteini Theodorakakou; Panagiota Efstathia Nikolaou; Angeliki Choustoulaki; Alexandros Briasoulis; Ioannis Petropoulos; Eleni-Dimitra Papanagnou; Anna Dimoula; Julie Courraud; Raphael Patras; Angelos Soranidis; Meletios-Athanasios Dimopoulos; Ioannis P. Trougakos; Efstathios Kastritis; Kimon Stamatelopoulos
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Long-term outcome of acquired transthyretin amyloidosis
delete2026-01-01
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deleteMisumi, Yohei; Nomura, Toshiya; Yamakawa, Shiori; Taguchi, Tomoaki; Tasaki, Masayoshi; Obayashi, Konen; Yamashita, Taro; Ando, Yukio; Ueda, Mitsuharu
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