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Pharmaceutical Statistics

IF1.4
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Journal Papers 51
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Evolving Variants, Shifting Outcomes: Implications for Nonconcurrent Controls in Platform Trials for COVID-19
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PREAI
deleteWatanabe, Shin; Shimizu, Yosuke; Sato, Hiroyuki; Uemura, Yukari; Hirakawa, Akihiro
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A Seamless Two-Stage Phase I/II Trial Design With Backfill and Joint Monitoring for Dose Optimization
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PREAI
deleteTakeda, Kentaro; Zhu, Jing; Yimer, Belay B.; Hirakawa, Akihiro
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A Dose-Finding Design for Drug Combinations Using a Bayesian 4 Parameter Logistic Model With Penalised D-Optimality
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deleteAjimi, Maxine; Webb, Benjamin; Wheeler, Graham M.; Marshall, Jayne; Mander, Adrian P.
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Phase III Probability of Success When Early Development Is Based on a Putative Surrogate Endpoint: A Vaccine Efficacy Case Study
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PREAI
deleteCallegaro, Andrea; Solmi, Francesca; Noirjean, Silvia; Conti, Valentino; Tibaldi, Fabian; Eletti, Alessia
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RABOTS: A Randomized Adaptive Bayesian Optimization Two-Stage Seamless Design for Dose Optimization and Proof-of-Concept Evaluation
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PREAI
deleteZhu, Xiaochen; Li, Yiwei; Wu, Jiaju; Tang, Yike; Liu, Liangang; Huang, Shu-Pang; Hsieh, Hsin-Ju
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Predictive Biomarker Graphical Approach (PRIME) for Precision Medicine
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PREAI
deleteD'Angelo, Gina; Tian, Xiaowen; Deng, Chuyu; Zhou, Xian
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An Ensemble Classifier for Ordinal Outcomes in High-Dimensional Genomics Data
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PREAI
deleteRathnasekara, Heranga K.; Sikdar, Sinjini
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Integrating Preclinical Insights for Adaptive Dose Escalation in Phase I Oncology Trials
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PREAI
deleteBarnett, Helen; Guhl, Melanie; Di Stefano, Fulvio; Skanji, Donia; Guilleminot, Sandrine; Saint-Hilary, Gaelle; Mozgunov, Pavel; Riviere, Marie-Karelle
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Evaluating Safety Rules in Ongoing Dose-Escalation Trials Using BOIN: A Comparative Analysis of Criteria and Their Impact on Dose-Level Safety Assessments
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PREAI
deleteEnglert, Stefan; Prior, Thomas J.; Mitra, Anirban; Sanusi, Busola; Zhang, Liangcai; Di Scala, Lilla
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Within-Trial Prognostic Score Adjustment Is Targeted Maximum Likelihood Estimation
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PREAI
deleteHojbjerre-Frandsen, Emilie; Schuler, Alejandro
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An Association Test for Ordinal Outcomes in Clustered Data With Informative Cluster Size
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PREAI
deleteSenevirathne, Hasika K. Wickrama; Dutta, Sandipan
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Paired and AB/BA Cross-Over Design in Early Phase Clinical Trials: A Closer Look at Within-Subject Variance Bias
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PREAI
deleteWolfsegger, Martin J.; Xu, Peixin; Cotterill, Amy; Schutz, Helmut; Jaki, Thomas F.
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New, Shorter Small-Sample Intervals for Vaccine Efficacy
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PREAI
deleteGasparini, Mauro; Di Trani, Vincenzo; Ratta, Marco
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