CAG-targeting artificial miRNA with reduced off-target risk for efficient lowering of pathogenic polyglutamine proteins
Pewinska-Kolodziejczak, Marianna; Kotowska-Zimmer, Anna; Przybyl, Lukasz; Wronka, Dorota; Karlik, Anna; Smuszkiewicz, Michal; Balcerek, Julia; Suszynska-Zajczyk, Joanna; Piaszyk-Borychowska, Anna; Urbanek-Trzeciak, Martyna; Sablok, Gaurav; Kozlowska, Emilia; Podkowinski, Jan; Fiszer, Agnieszka; Kozlowski, Piotr; Handschuh, Luiza; Olejniczak, Marta.png)
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Save Integrating transcriptomics and proteomics to assess antisense oligonucleotide safety and efficacy: a time-resolved approachvan Leeuwen, Daniel; Cipullo, Miriam; Williams, Eleanor C.; Iannetta, Anthony; Chu, Britney; Wang, Junmin; Hamza, Ghaith; Crysnanto, Danang; Guzzi, Nicola; Tan, Jennifer Y.; Miele, Eric; Sawarkar, Ritwick; Mohorianu, Irina; Prill, Sebastian; Andersson, Patrik Share Save An integrated computational antigen discovery pipeline with hierarchical filtering for emerging viral variantsRoy, Raj S.; Oh, Jaemin; Abeer, A. N. M. Nafiz; Giraldo, Maria, I; Ikegami, Tesuro; Weaver, Scott C.; Vasilakis, Nikolaos; Yoon, Byung-Jun; Qian, Xiaoning Share Save Genomic instability and mono-parental expression mitigate genomic shock in a cross-subgenus Leishmania hybridLouzada-Flores, Viviane Noll; Cokelaer, Thomas; Fuentes-Carias, Marcela; Pescher, Pascale; Ferreira, Tiago Rodrigues; Latrofa, Maria Stefania; Mendoza-Roldan, Jairo Alfonso; Otranto, Domenico; Spath, Gerald F.; Louradour, Isabelle Share Save Integrating transcriptomics and proteomics to assess antisense oligonucleotide safety and efficacy: a time-resolved approach (Vol 3, ugag016, 2026)Leeuwen, Daniel van; Cipullo, Miriam; Williams, Eleanor C.; Iannetta, Anthony; Chu, Britney; Wang, Junmin; Hamza, Ghaith; Crysnanto, Danang; Guzzi, Nicola; Tan, Jennifer Y.; Miele, Eric; Sawarkar, Ritwick; Mohorianu, Irina; Prill, Sebastian; Andersson, Patrik Share Save Defective plasticity in dermatomyositis patients muscle stem cells is associated with sustained intrinsic inflammatory signaling and disruption of the histone H3.3 chromatin loading pathwayBouchereau, Wilhelm; Chenane, Linda; Weiss-Gayet, Michele; Lessard, Lola; Cardona, Yseult; Mounier, Remi; Gallay, Laure; Allenbach, Yves; Benveniste, Olivier; Corpet, Armelle; Chazaud, Benedicte; Lomonte, Patrick Share Save EBV genome analysis in multiple sclerosis shows extensive viral diversity and links to autoimmunityLehikoinen, Joonas; Hannolainen, Leo; Rautila, Osma S.; Dickson, Zachery W.; Pyoria, Lari; Dieterich, Liane; Jansson, Lilja; Tammi, Silja; Hedman, Klaus; Perdomo, Maria F.; Tienari, Pentti J. Share Save Tetrahedral DNA nanostructure-delivered suppressor tRNA ameliorates nephropathy in COL4A5 nonsense mutation-mediated Alport syndrome miceLv, Jingru; Li, Ying; Hong, Dean; Shen, Yuxuan; Mi, Zeyuan; Liang, Qing; Zheng, Zhetao; Kong, Bangyan; Gao, Wankai; Dou, Zhiyang; Tian, Songlin; Xia, Qing Share Save 
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