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Rare Disease and Orphan Drugs Journal

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Journal Papers 7
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Adeno-associated viral vector gene therapy for canine hemophilia
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deleteDoshi, Bhavya S.; Crudele, Julie M.; Callan, Mary Beth
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Meeting Abstracts from the XVI International Collaboration on Rare Diseases and Orphan Drugs (ICORD): Incentivizing Science and a Comprehensive Program for Rare Diseases
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deleteRoldan, Emilio J. A.; Stefanov, Rumen; Tifft, Cynthia J.; Evelson, Pablo Andres; Posada, Manuel; Lucangioli, Silvia; Taruscio, Domenica; Berg, Gabriela; Demianczuk, Patricia Sonia; Mantovani, Alberto; Del Toro, Mireia; Calogero, Micaela Tamar; Bermejo-Sanchez, Eva; Raices, Bianca; Carta, Claudio; Estebenet, Fabiana; Muthyala, Ramaiah; Barrera, Luis Alejandro; Pacciarini, Guadalupe Velia
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Emerging treatments for systemic lupus erythematosus
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deleteSatoh-Kanda, Yurie; Nakayamada, Shingo; Tanaka, Yoshiya
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