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Molecular Therapy
IF
12
Papers
25488
Citations
35434
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Journal Papers
25488
Related Insights
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Journal Papers
25488
Publication Date
Publication Date
IF
Citations
A dendritic cell-targeting LNP hybridized with multi-antigen cell membrane for precision cancer immunotherapy
Molecular Therapy
IF
12
2026-11-13
0
PRE
AI
Jian Xu; Jiangyue Wang; Yunqiu Miao; Yanqi Zhao; Yixiang Huang; Dian Cai; Zijian Cheng; Lijun Li; Yuqi Xu; Zhangyu Wang; Jie Wang; Fengjiao Jiang; Yanzuo Chen; Xinxin Zhang
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FLT3 Kinase Inhibition Reshapes the Neuronal Transcriptome to Suppress Seizures
Molecular Therapy
IF
12
2026-11-13
0
PRE
AI
Kate Cruite; Madeline Moore; Michael D. Gallagher; Shuqi Lin; Yuqin Yin; Emanuel M. Coleman; Ellie Shahbo; Tenzin Lungjangwa; Xinzhou Ge; Volker Hovestadt; Rudolf Jaenisch; Jamie Maguire; Xin Tang
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Lentivector transduction of hematopoietic stem/progenitor cells improves disease manifestations in mouse models of Farber disease and SMA-PME
Molecular Therapy
IF
12
2026-11-12
0
OA
AI
Jitka Rybova; Ladislav Kuchar; Teresa Sundararajan; Petr Ruzicka; William M. McKillop; Thierry Levade; Jeffrey A. Medin
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Correction of acid ceramidase deficiency by intravenous AAV-mediated gene therapy in symptomatic P361R-Farber mice
Molecular Therapy
IF
12
2026-11-12
0
PRE
AI
Jérôme Denard; Martina Marinello; Marion Derome; Virginie Latournerie; Delphine Bonnin; Louise Mangin; Samia Martin; Jeffrey A. Medin; Ana Buj-Bello
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Clinically relevant AAV8-
PEX1
gene therapy preserves retinal integrity and function long-term in a murine model of Zellweger spectrum disorder
Molecular Therapy
IF
12
2026-11-12
0
PRE
AI
Samy Omri; Erminia Di Pietro; Devin S. McDougald; Shaghayegh Zokaei; Jean Bennett; Joseph G. Hacia; Nancy E. Braverman; Catherine Argyriou
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Therapeutic Landscape of Folate Receptor-α Targeting: Platforms, Progress, and Clinical Translation
Molecular Therapy
IF
12
2026-11-09
0
PRE
AI
Arundhuti Dey; Manan Bhavesh Doshi; Sneha Sandip Raul; Priya Kumari; Ayush Shrivastava; Nitu Mishra; Devivasha Bordoloi
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Development of an Efficient and Precise TadA-based C-to-G Base Editor Mi-zCGBE
Molecular Therapy
IF
12
2026-11-07
0
OA
AI
Jun Zhou; Xiubin Liang; Youcai Xiong; Xiao Han; Li-Kuang Tsai; Xiaofeng Xia; Charles Bisgaier; Michael Iannuzzi; Xiaoqiang Huang; Dongshan Yang; Y. Eugene Chen; Jifeng Zhang; Jie Xu
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Are entirely virus-free CAR T cells as good as lentiviral transduced universal cells?
Molecular Therapy
IF
12
2026-11-06
0
OA
AI
Oliver Gough; Christos Georgiadis; Roland Preece; Renuka Kadirkamanathan; Waseem Qasim
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CD3scFv-Engineered AAV Capsid Drives Superior In Vitro and In Vivo CAR-T Cell Generation and Leads to Complete Eradication of CD19+ Tumors
Molecular Therapy
IF
12
2026-11-06
0
OA
AI
Haifeng Chen; Tsvetelina Hoang; Anastasiya Smith; Tara Shahim; Ching Yi Ho; Platon Selemenakis; Ningguang Luo; Moeed Ahmad; Amna Aqdas; Min Chen
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AAV-mediated expression of a SARS-CoV-2 neutralizing antibody in monocyte-derived dendritic cells and human airway epithelial cells
Molecular Therapy
IF
12
2026-11-06
0
OA
AI
Maureen Obara; Aparna Shandheep; Katharina Rahmel-Stein; Matthias Bruhn; Bibiana Costa; Pimpan Sujariyakul; Andreas Pavlou; Lena Mareike Busker; Sebastian Hook; Stephanie Tamm; Berenike Lange; Lara-Jasmin Schröder; Jan-Christopher Kamp; Frauke Stanke; Michael Ott; Ulrich Kalinke
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IL-1β signaling on dendritic cells expands tumor-specific T cells to overcome immune checkpoint blockade resistance
Molecular Therapy
IF
12
2026-11-06
0
OA
AI
Hojae Lee; Gyu-Bum Yeon; Hyunseo An; Jiwon Oh; Zhichen Sun; Xue Wang; Casey Moore; Eun Byeol Ko; Longchao Liu; Chuanhui Han; Sunkyung Kim; Eunae You; Micheong Cheong; Jaeil Han; Heung Kyu Lee; Jian Qiao; Joonbeom Bae; Yang-Xin Fu
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Chemogenetically silencing NaV1.8
+
sensory neurons with PSAM
4
-GlyR relieves chronic pelvic pain associated with interstitial cystitis in mice
Molecular Therapy
IF
12
2026-11-06
0
PRE
AI
Guangda Lv; Hanwen Liu; Ruize Xu; Zihan Guan; Lei Liu; Weibo Chen; Guomei Ye; Wenzhen Wang; Zhiying Xiao; Jiliang Wen; Guangfeng Shao; Xiulin Zhang
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Disrupting the Importin-5-Glycoprotein Interaction Attenuates LCMV and Confers Protection Against Lethal Challenge
Molecular Therapy
IF
12
2026-11-06
0
PRE
AI
Xiaoqin Jian; Huan Xu; Yuxi Wen; Xinru Dong; Qiyin An; Mengwei Xu; Shujing Zhang; Weiwei Wan; Lin Wang; Runming Jin; Xiaoyan Wu; Fen Zhou; Zhao Wang; Jingshi Wang; Zengqin Deng; Wei Liu; Hao Li; Gengfu Xiao; Hongbo Chen; Leike Zhang
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Enhanced efficacy of gene therapy using a ubiquitous promoter to treat growth hormone-resistant Laron dwarfism in a mouse model
Molecular Therapy
IF
12
2026-11-06
0
PRE
AI
Kian Chuan Sia; Shu Uin Gan; Zhen Ying Fu; John J. Kopchick; Michael J. Waters; Kok-Onn Lee
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Focused ultrasound–mediated AAV gene therapy: Unlocking a new space in the CNS delivery landscape
Molecular Therapy
IF
12
2026-11-06
0
PRE
AI
Nick Todd; Bernie Owusu-Yaw; Elián Hines; Zhenghui Li; Nathan McDannold; Casey A. Maguire; R. Mark Richardson; Fengfeng Bei
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NeuroD1-induced fate conversion partially restores GABAergic neuronal identity in Huntington’s disease
Molecular Therapy
IF
12
2026-11-06
0
OA
AI
Siwoo Lee; Geneva Rose Notario; Jung Hwa Seo; Sung-Rae Cho
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MEK1/2 inhibition ameliorates clinical lesions in experimental pemphigus vulgaris
Molecular Therapy
IF
12
2026-11-06
0
OA
AI
Shirin Emtenani; Sabrina Patzelt; Kiana Zarabadi; Tingyu Yang; Anna M. Sigmund; Maxi Hofrichter; Christian Probst; Jens Waschke; Enno Schmidt
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Mosaic Hemagglutinin-Based Influenza B mRNA-LNP Vaccine Induces Strong Humoral Immune Response in Non-Human Primates
Molecular Therapy
IF
12
2026-11-06
0
OA
AI
Máté Vadovics; Anass Abbad; Temima Yellin; Juan Manuel Carreño; Kieu Lam; Hiromi Muramatsu; Emily F. Daley; András Sárközy; Weina Sun; James Heyes; Florian Krammer; Norbert Pardi
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Sharpening therapeutic tools toward blunting pathological nuclear lamina with advanced
in vitro
disease modeling
Molecular Therapy
IF
12
2026-10-27
0
PRE
AI
Luca Caputo; Pier Lorenzo Puri
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The Circular RNA circSKA3 Binds Integrin β1 to Induce Invadopodium Formation Enhancing Breast Cancer Invasion
Molecular Therapy
IF
12
2026-10-24
0
PRE
AI
William W. Du; Weining Yang; Xiangmin Li; Ling Fang; Nan Wu; Feiya Li; Yu Chen; Qihan He; Elizabeth Liu; Zhenguo Yang; Faryal Mehwish Awan; Mingyao Liu; Burton B. Yang
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