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Haemophilia

IF3
Papers5895
Citations7063
Journal Papers 15469
Publication Date
Understanding Contact Risks of Pediatric Physical Activity: Video Analysis to Inform Decisions for Children at Risk of Bleeding Injuries
delete2026-10-05
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deleteLauren Backstein; Ria Patel; Mona Elmikaty; Brooklyn Westlake; Sarah Sbeiti; Leonardo R. Brandão; Robert Klaassen; Allison Clouthier; Chris Joslin; Ryan Graham; Patricia E. Longmuir
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Real-World Experience With Emicizumab for Haemophilia A From the Physician Perspective in a Real-World Clinical Setting
delete2026-10-03
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deleteMichael Recht; Chris Blazos; Sophie Lai; Nathan Ball; Ella Morton; Lucy Lee; Juliana M. L. Biondo; Janet S. Lee
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Congenital Hemophilia-A With High-Titer Inhibitor and Essential Thrombocythemia: A Rare Coexistence
delete2026-10-03
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PREAI
deleteDeborah Kasmi; Silvia Sorella; Erminia Baldacci; Mario Biglietto; Bianca Maria Mandelli; Antonio Chistolini; Massimo Breccia; Christian Carulli; Cristina Santoro
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Patient Perspectives in Haemophilia A: Unmet Needs of Individuals Receiving Factor and Non-Factor Treatments
delete2026-10-03
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deleteNana Kragh; Veruska Carboni; Duygu Bozkaya; Idaira Rodriguez-Santana; Claudia Mighiu; Bethany Franks; Arnoud Plat; Randall Curtis
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Impact of Gene Therapy on the Haemophilia-Free Mind: Outcomes Before and After Valoctocogene Roxaparvovec in GENEr8-1 Trial Participants
delete2026-10-03
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PREAI
deleteCedric Hermans; Milad Karimi; Charlotte Camp; Steven W. Pipe; Sandra Santos; Simon Harris; Matthew Reaney; David Hinds; Patrick Fogarty; Wolfgang Miesbach; Flora Peyvandi
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Biphasic Transaminitis During Corticosteroid Tapering After Etranacogene Dezaparvovec Gene Therapy for Haemophilia B: Management Lessons From the First Spanish Case
delete2026-09-21
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PREAI
deleteManuel Rodriguez Lopez; María Teresa Alvarez Román; Michael Calviño Suarez; Ramiro José Nuñez Vázquez; Carmen Albo Lopez
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Artificial Intelligence and Machine Learning in the Context of Hemophilia: A Scope Review
delete2026-09-21
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deleteTatyane Oliveira Rebouças; André Cardoso Tavares; Antônio Diego Costa; Cícera Jamille Caldas Rodrigues; Lucilane Maria Sales da Silva
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Lipoprotein(a) in People With Haemophilia: A Forgotten Biomarker in a Population whose Haemostasis We Are Normalising
delete2026-09-21
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PREAI
deleteManuel Rodriguez Lopez; María Teresa Alvarez Román; Michael Calviño Suarez; Ramiro José Nuñez Vázquez; Carmen Albo López
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Underrecognized Iron Deficiency in Pregnant Women With Inherited Bleeding Disorders
delete2026-09-21
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PREAI
deleteGretchen York; Sydney Taylor; Ming Y. Lim
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A Common Language for the Multidisciplinary Team: Point-of-Care Musculoskeletal Ultrasound in Modern Haemophilia Care
delete2026-09-21
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deleteHortensia De la Corte-Rodriguez; María Teresa Álvarez-Román; Mauro Davoli; Magnus Aspdahl; Christina Burgess; Karin Fijinvandraat; Roberta Gualtierotti; Cedric Hermans; Marko Marinić; Carlo Martinoli; Wolfgang Miesbach; Gianluigi Pasta; Michael Sigl-Kraetzig; David Stephensen; Malin Svennefalk; Víctor Jiménez-Yuste; the E.A.H.A.D. Joint Health Group
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Gaps Between Prescription and Practice: Pharmacy-Based Measurement of Prophylaxis Adherence in Haemophilia
delete2026-09-21
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PREAI
deleteDebora M. C. Rocha-Santiago; Jéssica O. Frade-Guanaes; Gabriela G. Yamaguti-Hayakawa; Margareth C. Ozelo; Alessandra N. L. Prezotti; Genival A. dos Santos Junior
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Acquired von Willebrand Syndrome Associated With Wilms Tumour
delete2026-09-18
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PREAI
deleteTakamasa Mizumoto; Tomohei Nakao; Yuuki Shimizu; Atsuhiko Ota; Ryuhei Tanaka; Takumi Gohara; Yujiro Tanaka; Kazuko Obana; Takashi Fukushima
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DDAVP Challenges in 170 Children With von Willebrand Disease: Response Classification Varies According to Criteria Used
delete2026-09-17
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deleteMichael Shu; Caroline Malcolmson; Amanda Fregonas; Tristan E. Knight; Margaret L. Rand; Cindy Wakefield; Vanessa Bouskill; Manuel Carcao
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Treatment Adherence in Haemophilia: Methods of Assessment, Clinical Outcomes, and Real-World Evidence
delete2026-09-17
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PREAI
deleteFiorenzo Santoleri; Romina Giannini; Ruggero Lasala; Alessia Romagnoli; Paolo Abrate; Andrealuna Ucciero; Cosimo De Giorgio; Tiziano Lupi; Myriam Brachet Cota; Domenico Angelo Tarantino; Annalisa Clemente; Pierpaolo Toto; Valentina Isgrò; Alice primomo; Alberto Costantini
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Treatment With Etranacogene Dezaparvovec in a Renal Transplant Recipient With Hemophilia B on Concomitant Systemic Immunosuppressive Therapy
delete2026-09-17
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PREAI
deleteLaura S. Ortega Flores; Erin C. Duffield; Megan F Duperreault; Shawn Newton; George M Rodgers; Ming Y Lim
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Population-Level Real-World Healthcare Costs in Men and Women With Haemophilia A
delete2026-09-16
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deleteSam Hirniak; Samantha S. M. Drover; Andrea N. Edginton; Dagmar M. Hajducek; Alfonso Iorio; Mhd. Wasem Alsabbagh; William W. L. Wong
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Physical Activity, Bleeding Incidence and Health-Related Quality of Life, in Patients With Haemophilia A Without Inhibitors, Treated With Emicizumab: A Post-Hoc Descriptive Analysis of the Power Study Data
delete2026-09-16
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deleteMatteo Nicola Dario Di Minno; Berardino Pollio; Ezio Zanon; Gaetano Giuffrida; Sara Bendinelli; Raffaella Perrone; Giancarlo Castaman; the POWER study sites group
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