CURE ID: A Platform to Collect Real-World Treatment Data for Drug Repurposing in Rare Genetic Disorders
Farid, Tahsin; Ruzhnikov, Maura R. Z.; Duggal, Mili; Tumas, Keyla C.; Strongin, Shira; Sid, Eric; Fuchs, Sarah R.; Sacks, Leonard; Pichard, Dominique C.; Pilgrim-Grayson, Catherine; Mathe, Ewy A.; Stone, Heather A..png)
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