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Molecular Therapy Nucleic Acids

IF6.1
Papers1405
Citations13224
Journal Papers 1386
Publication Date
Gene transfer of microRNA-181a alleviates senescence and apoptosis in tendinopathic tenocytes
delete2026-10-05
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deleteYuh-Ruey Kuo; Che-Chia Hsu; Han-Po Tseng; Jou-Hua Wang; I-Ming Jou; Shih-Yao Chen; Po-Ting Wu
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Gene Therapy Approaches for Hereditary Neuromuscular Diseases
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deleteXue Zhang; Jiahao Wu; Yanjiang Zheng; Yifei Li; Kaiyu Zhou
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LNP-mediated CRISPR gene editing of human vascular endothelial cells in 2D and 3D microfluidic cell culture systems
delete2026-10-01
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deleteAmalie Lykke Olsen; Camilla Blunk Vorsø Brandt; Rasmus Karred Larsen; Sofie Vestergaard Fonager; Judith Zubia-Aranburu; János Haskó; Rikke Bek Helmig; Søren Egedal Degn; Mingdong Dong; Niels Jessen; Anders Etzerodt; Robert Rieben; Lin Lin; Yonglun Luo
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Minimal indel-inducing and window-adjustable base editing using inactive Cas12b effectors
delete2026-09-29
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deleteWi-jae Lee; Yun Gyeong Kim; Yeounsun Oh; Lee Wha Gwon; Dongjae Lim; Ho-Joong Kim; Bo-Woong Sim; Seung Hwan Lee
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Rapid in vivo screening of tumor-targeting aptamers using zebrafish larvae
delete2026-09-29
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deleteMadison A. Schaefer; Brandon Wilbanks; Irene K. Yan; Alexis M. Sosic; Julia Driscoll; Rory L. Smoot; Tushar Patel; L. James Maher; Shizhen Zhu
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cGAS-mediated immunogenicity impairs the stability and safety of LNP-encapsulated DNA in vivo
delete2026-09-29
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deleteXuelin Wang; Tengyuan Liu; Biao Long; Mingya Li; Ying Yao; Yuqin Fu; Si Xie; Yanfang Gu; Weizhou Yue; Yukun Pan; Xiaohui Wu; Lei Sun
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Genome-wide CRISPRa screens identify modulators of CAR T survival across diverse tumor cytokine milieus
delete2026-09-28
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deleteBenjamin C. Curtis; Cailyn H. Spurrell; Lindsay Flint; Aalton M. Lande; Marissa Leonardi; James M. Rosser; Tavie Parker; Tiffanie Chai; Ardizon Valdez; Ryma Toumi; Nat Murren; Michael Fitzgerald; Jasmin Martinez-Reyes; Finn Watt; Christopher P. Saxby; Corinne Summers; Kamila S. Gwiazda; Michael C.V. Jensen; Shannon K. Oda
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Anti–PD-L1 scFv–Secreting Fifth-Generation GD2-CAR T Cells Enhance Antitumor Function Against GD2-Low Retinoblastoma
delete2026-09-24
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deletePornpimon Yuti; Katesara Kongkla; Nunghathai Sawasdee; Yupanun Wutti-in; Nattaporn Phanthaphol; Naravat Poungvarin; Mutita Junking; Pa-thai Yenchitsomanus; Jatuporn Sujjitjoon
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Structural Insights into an Aptainhibitor of the SARS-CoV-2 E Protein Using Molecular Docking, Molecular Dynamics, and Biophysical Analyses
delete2026-09-23
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deleteMiyssa Imam Abdelmageed Mohamed; Jin-Pyo Lee; Woo-Ri Shin; Dae-Young Park; In-Hwan Oh; Su-Min Lee; Jiho Min; Ji-Young Ahn; Yang-Hoon Kim
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AptViralDB: A Repository of Experimentally Validated Antiviral Aptamers
delete2026-09-23
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deleteNisha Bajiya; Shivansh Singh; Pushpendra Singh Gahlot; Gajendra P.S. Raghava
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CasNano: An ultracompact CRISPR-Cas12f with a GC-rich PAM for epigenome editing with therapeutic potential
delete2026-09-18
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deleteDongkyeong Kim; Chia-Wei Huang; Richard Pan; Junming Qian; Xuebing Wu; Orrin Devinsky; Yi-Ting Tsai; Shawn Liu
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Systemic and Local Delivery of siRNA to the CNS and Periphery via Anti-IGF1R Antibody Conjugation
delete2026-09-18
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deleteMengnan Tian; Mehran Nikan; Miran Yoo; Stephanie Klein; Seung-Hwan Kwon; John Matson; Dongin Kim; Jinwon Jung; Sumin Hyeon; Byeong Min Yoo; Hyeon Ji Park; Michael Tanowitz; Asa Wahlander; Weon-Kyoo You; Hakju Kwon; Janel Huffman; Thazha P. Prakash; Sang Hoon Lee; Hien Zhao; Sungwon An
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Aptamer-guided delivery of miR-126 suppresses glioblastoma stem-like cell invasion and tumor progression
delete2026-09-17
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deleteGiorgia Castellani; Mariachiara Buccarelli; Alessandra Affinito; Gabriele De Luca; Ramona Ilari; Francesca Pedini; Alessandra Di Giamberardino; Mariagiovanna Ballato; Gabriele Ricciardi; Martina Offi; Cristiana Mollinari; Nadia Felli; Alessandra Boe; Giovanna Marziali; Mauro Biffoni; Maria Caffo; Gerolama Condorelli; Maurizio Martini; Quintino Giorgio D'Alessandris; Lucia Ricci-Vitiani
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A combination of live-attenuated and adenovirus-based vaccines provides immediate and long-lasting protection against Yersinia pestis in mice
delete2026-09-17
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deleteEmily K. Hendrix; Jian Sha; Paul B. Kilgore; Blake H. Neil; Atul K. Verma; Edwin B. Rodriguez; Ashok K. Chopra
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rAAV-mediated Multi-miRNA Delivery Targeting MAPK Pathway Suppresses Laser-induced Choroidal Neovascularization in Mice
delete2026-09-16
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deleteJung Woo Han; Jin Young Yang; Yeji Kim; Sumin An; Eunjae Yoo; In Hwan Park; Sang-Won Lee; Hyun-Ji Lee; Tae Geol Lee; Wook Hyun Jung; Hyo Song Park; Jin Ha Kim; Jun Sub Choi; Hun Soo Chang; Tae Kwann Park
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