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Intravenous Delivery of a Gene Therapy Vector that Expresses an Antitransferrin Receptor 1 Nanobody-I2S Fusion Protein Rescued Central Nervous System Lysosomal Burden in Mucopolysaccharidosis II Mice Ruangsiriluk, Wanida; Jacobo, Sarah Melissa P.; Iskenderian, Andrea; Modi, Meera; Chen, Nancy; Felice, Brian; Yuan, Shipeng; Mukherji, Shreya T.; Hernandez, Melody Rivera; Sunkara, Shashank; Macdonald, Amanda; Rajarshi, Girija; Palmieri, Kathleen; Crooker, Robert; Wu, Rui; Dalrymple, Margaret; Chheda, Mihir; Megahid, Donia; Arce, Camila; Shen, Mingfang; Dasari, Bhanu; Zhao, Xiaohui; Yalavarthi, Maneesha; Rompikuntal, Pramod; Ayyadurai, Saravanan; Fang, Josephine; Hozanovic, Alen; Pescatore, Brian; Bassous, Dany; Romashko, Alla; Galbreath, Elizabeth; Maccani, Andreas; Steinkellner, Julia; Ehmann, David E.; Choi, Vivian W.; Islam, Rizwana Share Save
Contemporary perspective and practical application of glutamate dehydrogenase in nonclinical studies Kodihalli, Ravindra C.; Ameri, Mehrdad; Baker, Kevin S.; Faber, Samantha C.; Irizarry Rovira, Armando R.; Jackson, Jonathan P.; Norona, Leah M.; Proctor, William R.; Rae, Jessica M. Caverly; Regev, Arie; Sakatis, Melanie Z.; Williams, Dominic P.; Zane, Doris; Rana, Payal Share Save
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Real-world treatment patterns and subsequent treatment effectiveness following frontline brigatinib in the ALTA-1L trial Ahn, Myung-Ju; Delmonte, Angelo; Ghosh, Sharmistha; Hochmair, Maximilian; Yang, Tsung-Ying; Yang, James Chih-Hsin; Han, Ji-Youn; Hansen, Karin Holmskov; Wu, Yanyu; Wan, Yin; Lin, Huamao Mark; Kretz, Julian; Hupf, Bradley; Kurec, Ahmet Melih; Churchill, Eric N.; Fram, Robert J.; Cabasag, Citadel Jungco; Goriya, Vishal; Zhao, Yuzhe; Campelo, Maria Rosario Garcia Share Save
The Reporting and Methodological Recommendations for Observational Studies Estimating the Effects of Deprescribing Medications (REMROSE-D) ISPE-Endorsed Guidance Hayes, Kaleen N.; Niznik, Joshua D.; Gnjidic, Danijela; Moriarty, Frank; Bennett, Dimitri; Laroche, Marie-laure; Talbot, Denis; Alcusky, Matthew; Sessa, Maurizio; Coe, Antoinette B.; Sirois, Caroline; Zullo, Andrew R.; Li, Xiaojuan; Chalasani, Sri Harsha; Syed, Jehath; Sawan, Mouna; Moga, Daniela C. Share Save
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Discovery of Pyrazole-Based Positron Emission Tomography Agent that Maps Histone Deacetylase 6 (HDAC6) in the Nonhuman Primate Brain Yamasaki, Tomoteru; Ohyabu, Norio; Wakabayashi, Takeshi; Ibanez, Ignacio; Iwanaga, Kouichi; Yamamoto, Satoshi; Hattori, Masahiko; Sugita, Taku; Terada, Michiko; Onishi, Tomohiro; Sato, Sho; Kosugi, Yohei; Takano, Akihiro; Mcquade, Paul; Maru, Takamitsu; Inui, Naomi; Fujinaga, Masayuki; Mori, Wakana; Nagai, Yuji; Seki, Chie; Uchida, Shoko; Minamimoto, Takafumi; Higuchi, Makoto; Fushimi, Makoto; Zhang, Ming-Rong Share Save
Unlocking insights from mother-infant linked data in pharmacoepidemiology: opportunities, challenges, and future directions Kaplan, Sigal; Ayele, Henok Tadesse; Bennett, Dimitri; Grandi, Sonia M.; Schachterle, Stephen E.; Simeone, Jason C.; Sun, Jenny W.; Ukah, Ugochinyere Vivian Share Save