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National Center for Advancing Translational Sciences

Scholars88
Papers29
Citations2.0K
Related Papers (29)
Publication Date
New Approaches to Clinical Trials for Rare Diseases: Decentralized Trial Design for Neurofibromatosis Type 1 and Schwannomatosis
errCancers
IF4.4
err2026-08-01
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errOAAI
errVanessa L. Merker; Shivani Ahlawat; Robert A. Avery; Diana Bradford; Andrea M. Gross; Jennifer Janusz; Andrés J. Lessing; Linda Manth; Miranda L. McManus; Beverly Oberlander; Dominique C. Pichard; William Riter; Kavita Y. Sarin; Steven Sheard; Russell Taylor Sundby; Karin S. Walsh; Pamela L. Wolters; Brigitte C. Widemann; Scott R. Plotkin
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In vitro bioactivity profile-driven discovery of drug synergies in hepatocellular carcinoma
err2026-07-28
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errOAAI
errTuan Xu; Miao Xu; Deborah K. Ngan; Tongan Zhao; Catherine Z. Chen; Wei Zheng; Ruili Huang
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Prophylactic inhibition of LATS1/2 before high-dose irradiation promotes the regeneration of the damaged intestinal epithelium
err2026-07-20
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errOAAI
errLucy M. Driver; Frances Anne Tosto; Bridget S. Scherer; Lixia Luo; Katy Harbaugh; Olivia White; Ayra Charania; Jordan Tran; Rebecca Bacon; Patrick J. Morris; Michele Ceribelli; Damien Y. Duveau; Lale Evsen; Scott B. Hoyt; Keerthana Kurapati; Koravit Poysungnoen; John W. Hickey; Jatin Roper; Christine E. Eyler; Craig J. Thomas; Chang-Lung Lee
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Biofabrication and biomedical manufacturing research frontiers in the United States
err2026-07-17
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errOAAI
errYunxia Chen; Kyle R. Phillips; Eben Alsberg; Thomas E. Angelini; Nasim Annabi; Anthony Atala; Amit Bandyopadhyay; Leon M. Bellan; Luiz E. Bertassoni; Adriana Blazeski; Thomas Boland; Susmita Bose; Jason A. Burdick; Robert C. Chang; Christopher S. Chen; Roland K. Chen; Douglas B. Chrisey; Elizabeth Cosgriff-Hernandez; Paul D. Dalton; David Dean; Aixiang Ding; Bin Duan; Marc Ferrer; John P. Fisher; Gabor Forgacs; Debolina Ghosh; Warren L. Grayson; Murat Guvendiren; MD Ahasan Habib; Sarah C. Heilshorn; Ashley Hicks; Scott J. Hollister; Congrui Jin; Yifei Jin; Roger D. Kamm; Bashir Khoda; Robert Langer; Cato T. Laurencin; Sang Jin Lee; Kam W. Leong; Ming C. Leu; Wei Li; Michael Mak; Amir K. Miri; Roger J. Narayan; Liqun Ning; Brenda M. Ogle; Ibrahim T. Ozbolat; Zhijian Pei; Peihua Qiu; Krishanu Saha; Jayant Saksena; Vahid Serpooshan; Albert Shih; Rohan A. Shirwaiker; Pranav Soman; Ali Tamayol; Mark W. Tibitt; Changxue Xu; Yunzhi Peter Yang; Lijie Grace Zhang; James J. Yoo; Shaochen Chen; Yu Shrike Zhang; Yong Huang
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Uncovering the isoform-resolution kinetic landscape of nonsense-mediated mRNA decay with EZbakR
err2026-07-15
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errOAAI
errJustin W. Mabin; Isaac W. Vock; Martin Machyna; Nazmul Haque; Poonam Thakran; Alexandra Zhang; Ganesha Rai; Isabelle Nathalie-Marie Leibler; James Inglese; Matthew D. Simon; J. Robert Hogg
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Translational assessment instruments for preclinical to first-in-human decision-making: a scoping review
err2026-07-13
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errOAAI
errMarco Straccia; David Mawufemor Azilagbetor; Celean Camp; Guilherme S. Ferreira; Maria Laura Garcia-Bermejo; Annalisa Gastaldello; Kurinchi Gurusamy; Francesco Pappalardo; Merel J. Ritskes-Hoitinga; Fabrizio Rossi; Danilo Tagle; Martin Wehling; Francesca Pistollato
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Phenotypic screening for small molecules that lower PrP in cultured cells
err2026-07-09
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errOAAI
errJeannine A. Frei; Andrew G. Reidenbach; Leo M.H. Xu; Raja Mohan Gopalakrishnan; Dominick Casalana; Daniel A. Sprague; Mark-Anthony Bray; Amy Q. Wang; Vanessa Laversenne; Brian Erickson; Craig Braun; Mckenzie Hall; Douglas Auld; Eric Vallabh Minikel; Sonia M. Vallabh
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BDNF-DT and BDNF-AS-DT: novel genes in the BDNF locus
err2026-06-30
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errOAAI
errSvitlana V. Bach; Giovanna Punzi; Nuri E. Smith; Sreya Mukherjee; Joo Heon Shin; Qiang Chen; Geo Pertea; Leonardo Collado-Torres; Kristen R. Maynard; Stephanie C. Page; Joel E. Kleinman; Thomas M. Hyde; Daniel R. Weinberger; Keri Martinowich; Gianluca Ursini
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Combined inhibition of CDK4/6 and PI3K pathways exhibit highly synergistic activity and translational potential in Ewing sarcoma
err2026-06-18
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errOAAI
errHelen F. Gloege; Maria Ana Isabel C. De Los Santos; Advaita Chakraborty; Madhav Chadha; Alejandra Aguilar-Quintero; Min Shen; Caleb O. Heaslip; Sarah Finstuen-Magro; Brigit McDannell; Mohammad Tanhaemami; Stephanie Meyer; Kelly Klega; Ya-Qin Zhang; David S. Shulman; Steven G. DuBois; Matthew D. Hall; Anne-Florence Blandin; Brian D. Crompton
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Induced pluripotent stem cell–derived models of malignant nerve sheath tumor progression mimic glial to neuro-mesenchymal transition and uncover therapeutic opportunities
err2026-06-17
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errOAAI
errItziar Uriarte-Arrazola; Míriam Magallón-Lorenz; Juana Fernández-Rodríguez; Jiajing Zhang; Emily Lee; Sara Ortega-Bertran; Edgar Creus-Bachiller; Judit Farrés-Casas; Kelli M. Wilson; Crystal McKnight; Katlin Recabo; Ignacio Blanco; Héctor Salvador; Cleofé Romagosa; Conxi Lázaro; Helena Mazuelas; Bernat Gel; Marc Ferrer; Meritxell Carrió; Eduard Serra
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Analysis of in vitro profiling data of cosmetic ingredients within the Tox21 10K compound library for bioactivity and potential toxicity
err2026-06-16
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errOAAI
errLaken Kruger; Deborah K. Ngan; Tuan Xu; Menghang Xia; Stephen S. Ferguson; David M. Reif; Anton Simeonov; Ruili Huang
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Metformin on the Presence of COVID-19 Symptoms 6 Months after Infection: The ACTIV-6 Randomized Clinical Trial
err2026-06-04
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errOAAI
errCarolyn T Bramante, MD, MPH; Thomas G Stewart, PhD; David R Boulware, MD, MPH; Matthew W McCarthy, MD; Yue Gao, MS, Med; Russell L Rothman, MD, MPP; Ahmad Mourad, MD; Florence Thicklin; Jonathan B Cohen, MD; Idania T Garcia del Sol, MD; Nirav S Shah, MD, MPH; Manisha Mehta, DPM; Orlando Quintero Cardona, MD; Jake Scott, MD; Adit A Ginde, MD, MPH; Mario Castro, MD, MPH; Dushyantha Jayaweera, MD; Mark Sulkowski, MD; Nina Gentile, MD; Kathleen McTigue, MD; G Michael Felker, MD; Sean Collins, MD, MSci; Sarah E Dunsmore, PhD; Stacey J Adam, PhD; Christopher J Lindsell, PhD; Adrian F Hernandez, MD, MHS; Susanna Naggie, MD, MHS; for the Accelerating COVID-19 Therapeutic Interventions and Vaccines (ACTIV)-6 Study Group and Investigators
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BET inhibitor-based combinations targeting novel dependencies in MECOM-rearranged (r) AML
errLeukemia
IF13.4
err2025-12-19
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errOAAI
errChristine E. Birdwell; Warren Fiskus; Christopher P. Mill; Tapan M. Kadia; Naval Daver; Courtney D. DiNardo; Koji Sasaki; John A. Davis; Kaberi Das; Hanxi Hou; Antrix Jain; Anna Malovannaya; Lauren B. Flores; Rasoul Pourebrahim; Selina Yuan; Xiaoping Su; Michele Ceribelli; Kapil N. Bhalla
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Metabolic engineering and late-stage functionalization expand the chemical space of the antimalarial premarineosin A
err2025-12-05
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errOAAI
errChristina M. McBride; Morgan McCauley; Natalia R. Harris; Sahar Amin; Brian J. Curtis; Linnea Verhey-Henke; Awet A. Teklemichael; Erin N. Oliphant; Patricia Dranchak; Katherine L. Lev; Fengrui Qu; Harrison M. Snodgrass; Jared C. Lewis; James Inglese; Xin-Zhuan Su; Filipa Pereira; David H. Sherman
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Developing Therapeutics for Rare Cardiovascular Diseases
err2025-09-12
err0
PREAI
errJoseph B Lerman; Dwight D. Koeberl; Shilpi Epstein; Lothar Roessig; Rodica Stan; Meghan Halley; Anjali T. Owens; Barry Greenberg; Kevin M. Alexander; Sharlene M. Day; Mathew S. Maurer; Eric D. Adler; Adrian F. Hernandez; Euan A Ashley; G. Michael Felker
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Demonstration of Interoperability Between MIDRC and N3C: A COVID-19 Severity Prediction Use Case
err2025-08-14
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errOAAI
errHeather M. Whitney; Rachel Baccile; Hui Li; Karen Drukker; Christopher Meyer; Nicholas P. Gruszauskas; Weijie Chen; Diane S. Lauderdale; Sandy Napel; Seyed Kahaki; Rui Carlos Sá; Chris Beesley; Brandy Phalora; Sam Michael; Robert L. Grossman; Ken Gersing; Maryellen L. Giger
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A review of diffuse hemispheric glioma, H3 G34-mutant disease development, DNA repair, microenvironment, and treatments on the horizon
err2025-08-14
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errOAAI
errCameron Crowell; Ziwen Zhu; Yingxiang Li; Maria L. Varela; Quinn Ostrom; Patrick J. Cimino; Sohil H. Patel; Suzanne J. Baker; Chetan Bettegowda; Houtan Noushmehr; Claudia L. Kleinman; Laura Canty; Gustavo Alencastro Veiga Cruzeiro; Anandani Nellan; Oren Becher; Tom B. Davidson; Dolores Hambardzumyan; Adam Green; Robert Thorne; Kelli Wilson; Brett Theeler; Jason Gregory; Peter Mathen; Nadia Biassou; Sheila McThenia; Craig Erker; Robert Galvin; Ariane Soldatos; Pedro R. Lowenstein; Maria G. Castro; Sadhana Jackson
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Optimization of IRAK1/4/pan-FLT3 kinase inhibitors as treatments for acute myeloid leukemia
err2025-08-05
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errOAAI
errPatrick J. Sutter; Morgan M. Walker; Chris J. Finocchio; Jian-Kang Jiang; Gregory J. Tawa; Xiaohu Zhang; Xin Xu; Pranav Shah; Glenn Y. Gomba; Daniel T. Starczynowski; Craig J. Thomas; Scott Hoyt
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