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Liposomal lipid nanoparticles for extrahepatic delivery of mRNA Cheng, Miffy Hok Yan; Zhang, Yao; Fox, Kevin; Leung, Jerry; Strong, Colton; Kang, Emma; Chen, Yihang; Tong, Michelle; Bommadevara, Hemashree; Jan, Eric; Ip, Owen Yuk Long; Rodriguez-Rodriguez, Cristina; Saatchi, Katayoun; Hafeli, Urs O.; Abdolahzadeh, Amir; Witzigmann, Dominik; Cullis, Pieter R. Share Save
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Lipid Nanoparticle-Mediated Hit-and-Run Approaches Yield Efficient and Safe In Situ Gene Editing in Human Skin Bolsoni, Juliana; Liu, Danny; Mohabatpour, Fatemeh; Ebner, Ronja; Sadhnani, Gaurav; Tafech, Belal; Leung, Jerry; Shanta, Selina; An, Kevin; Morin, Tessa; Chen, Yihang; Arguello, Alfonso; Choate, Keith; Jan, Eric; Ross, Colin J. D.; Brambilla, Davide; Witzigmann, Dominik; Kulkarni, Jayesh; Cullis, Pieter R.; Hedtrich, Sarah Share Save
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Induction of Bleb Structures in Lipid Nanoparticle Formulations of mRNA Leads to Improved Transfection Potency Cheng, Miffy Hok Yan; Leung, Jerry; Zhang, Yao; Strong, Colton; Basha, Genc; Momeni, Arash; Chen, Yihang; Jan, Eric; Abdolahzadeh, Amir; Wang, Xinying; Kulkarni, Jayesh A. A.; Witzigmann, Dominik; Cullis, Pieter R. R. Share Save
Development of a child-friendly oral drug formulation using liposomal multilamellar vesicle technology Al Fayez, Nojoud; Bottger, Roland; Ghosh, Sreemoyee; Nakajima, Yushi; Chao, Po-Han; Rouhollahi, Elham; Nguyen, Anne; Cullis, Pieter R.; Witzigmann, Dominik; Li, Shyh-Dar Share Save
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Lipid nanoparticle formulations for optimal RNA-based topical delivery to murine airways Tam, A.; Kulkarni, J.; An, K.; Li, L.; Dorscheid, D. R.; Singhera, G. K.; Bernatchez, P.; Reid, G. S. D.; Chan, K. Y. T.; Witzigmann, D.; Cullis, P. R.; Sin, D. D.; Lim, C. J. Share Save
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Anionic Lipid Nanoparticles Preferentially Deliver mRNA to the Hepatic Reticuloendothelial System Pattipeiluhu, Roy; Arias-Alpizar, Gabriela; Basha, Gem; Chan, Karen Y. T.; Bussmann, Jeroen; Sharp, Thomas H.; Moradi, Mohammad-Amin; Sommerdijk, Nico; Harris, Edward N.; Cullis, Pieter R.; Kros, Alexander; Witzigmann, Dominik; Campbell, Frederick Share Save
Simultaneous, Single-Particle Measurements of Size and Loading Give Insights into the Structure of Drug-Delivery Nanoparticles Kamanzi, Albert; Gu, Yifei; Tahvildari, Radin; Friedenberger, Zachary; Zhu, Xingqi; Berti, Romain; Kurylowicz, Marty; Witzigmann, Dominik; Kulkarni, Jayesh A.; Leung, Jerry; Andersson, John; Dahlin, Andreas; Hook, Fredrik; Sutton, Mark; Cullis, Pieter R.; Leslie, Sabrina Share Save
FAM13A as potential therapeutic target in modulating TGF-β-induced airway tissue remodeling in COPD Tam, Anthony; Leclair, Pascal; Li, Ling Vicky; Yang, Chen X.; Li, Xuan; Witzigmann, Dominik; Kulkarni, Jayesh A.; Hackett, Tillie-Louise; Dorscheid, Delbert R.; Singhera, Gurpreet K.; Hogg, James C.; Cullis, Pieter R.; Sin, Don D.; Lim, Chinten James Share Save
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In vivo adenine base editing of PCSK9 in macaques reduces LDL cholesterol levels Rothgangl, Tanja; Dennis, Melissa K.; Lin, Paulo J. C.; Oka, Rurika; Witzigmann, Dominik; Villiger, Lukas; Qi, Weihong; Hruzova, Martina; Kissling, Lucas; Lenggenhager, Daniela; Borrelli, Costanza; Egli, Sabina; Frey, Nina; Bakker, Noelle; Walker, John A., II; Kadina, Anastasia P.; Victorov, Denis V.; Pacesa, Martin; Kreutzer, Susanne; Kontarakis, Zacharias; Moor, Andreas; Jinek, Martin; Weissman, Drew; Stoffel, Markus; van Boxtel, Ruben; Holden, Kevin; Pardi, Norbert; Thoeny, Beat; Haeberle, Johannes; Tam, Ying K.; Semple, Sean C.; Schwank, Gerald Share Save
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