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Dominik Witzigmann

nanovation therapeutics inc.

33H-index
79Paper Count
1.2WCitation Count
Published Papers 45
Publication Date
The landscape of genetic medicines for in vivo T cell reprogramming
err2026-08-03
err0
PREAI
errJens B. Simonsen; Viktor T. Lemgart; Jayesh A. Kulkarni; Dominik Witzigmann
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Lipid nanoparticle delivery of antisense gapmers attenuates pathology in a mouse model of facioscapulohumeral muscular dystrophy
err2026-05-26
err0
errOAAI
errSaeed Anwar; Karen Ying Tung Chan; Abdullah Zia; Samuel L. Beck; Hidenori Moriyama; Kenji Rowel Q. Lim; Md Nur Ahad Shah; Umme Sabrina Haque; Rika Maruyama; Dominik Witzigmann; Yusuke Echigoya; Darko Bosnakovski; Michael Kyba; Pieter Rutter Cullis; Toshifumi Yokota
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Design of Cationic Ionizable Lipids for the Delivery of Therapeutic Nucleic Acids
err2025-09-02
err0
errOAAI
errN. D. Prasad Atmuri; Fariba Saadati; Jayesh Kulkarni; Dominik Witzigmann; Pieter R. Cullis; Marco A. Ciufolini
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Rational design of lipid nanoparticles for enabling gene therapies
err2025-06-18
err0
errOAAI
errCedric A. Brimacombe; Jayesh A. Kulkarni; Miffy H.Y. Cheng; Kevin An; Dominik Witzigmann; Pieter R. Cullis
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Liposomal lipid nanoparticles for extrahepatic delivery of mRNA
err2025-05-03
err0
errOAAI
errCheng, Miffy Hok Yan; Zhang, Yao; Fox, Kevin; Leung, Jerry; Strong, Colton; Kang, Emma; Chen, Yihang; Tong, Michelle; Bommadevara, Hemashree; Jan, Eric; Ip, Owen Yuk Long; Rodriguez-Rodriguez, Cristina; Saatchi, Katayoun; Hafeli, Urs O.; Abdolahzadeh, Amir; Witzigmann, Dominik; Cullis, Pieter R.
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A magnetic separation method for isolating and characterizing the biomolecular corona of lipid nanoparticles
err2024-03-04
err8
errOAAI
errFrancia, Valentina; Zhang, Yao; Cheng, Miffy Hok Yan; Schiffelers, Raymond M.; Witzigmann, Dominik; Cullis, Pieter R.
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Lipid Nanoparticle-Mediated Hit-and-Run Approaches Yield Efficient and Safe In Situ Gene Editing in Human Skin
err2023-11-02
err13
errOAAI
errBolsoni, Juliana; Liu, Danny; Mohabatpour, Fatemeh; Ebner, Ronja; Sadhnani, Gaurav; Tafech, Belal; Leung, Jerry; Shanta, Selina; An, Kevin; Morin, Tessa; Chen, Yihang; Arguello, Alfonso; Choate, Keith; Jan, Eric; Ross, Colin J. D.; Brambilla, Davide; Witzigmann, Dominik; Kulkarni, Jayesh; Cullis, Pieter R.; Hedtrich, Sarah
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A Nanocarrier Approach for Oral Peptide Delivery: Evaluation of Cell-Penetrating-Peptide-Modified Liposomal Formulations in Dogs
err2023-07-10
err6
errOAAI
errUhl, Philipp; Bajraktari-Sylejmani, Gzona; Witzigmann, Dominik; Bay, Cindy; Zimmermann, Stefan; Burhenne, Jurgen; Weiss, Johanna; Haefeli, Walter E.; Sauter, Max
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Induction of Bleb Structures in Lipid Nanoparticle Formulations of mRNA Leads to Improved Transfection Potency
err2023-06-25
err70
errOAAI
errCheng, Miffy Hok Yan; Leung, Jerry; Zhang, Yao; Strong, Colton; Basha, Genc; Momeni, Arash; Chen, Yihang; Jan, Eric; Abdolahzadeh, Amir; Wang, Xinying; Kulkarni, Jayesh A. A.; Witzigmann, Dominik; Cullis, Pieter R. R.
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Development of a child-friendly oral drug formulation using liposomal multilamellar vesicle technology
err2022-09-01
err3
PREAI
errAl Fayez, Nojoud; Bottger, Roland; Ghosh, Sreemoyee; Nakajima, Yushi; Chao, Po-Han; Rouhollahi, Elham; Nguyen, Anne; Cullis, Pieter R.; Witzigmann, Dominik; Li, Shyh-Dar
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The role of lipid components in lipid nanoparticles for vaccines and gene therapy
err2022-09-01
err394
errOAAI
errAlbertsen, Camilla Hald; Kulkarni, Jayesh A.; Witzigmann, Dominik; Lind, Marianne; Petersson, Karsten; Simonsen, Jens B.
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Lipid nanoparticle formulations for optimal RNA-based topical delivery to murine airways
err2022-09-01
err22
errOAAI
errTam, A.; Kulkarni, J.; An, K.; Li, L.; Dorscheid, D. R.; Singhera, G. K.; Bernatchez, P.; Reid, G. S. D.; Chan, K. Y. T.; Witzigmann, D.; Cullis, P. R.; Sin, D. D.; Lim, C. J.
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Lipid nanoparticle-mediated silencing of osteogenic suppressor GNAS leads to osteogenic differentiation of mesenchymal stem cells in vivo
err2022-09-01
err12
errOAAI
errBasha, Genc; Cottle, Andrew G.; Pretheeban, Thavaneetharajah; Chan, Karen YT.; Witzigmann, Dominik; Young, Robert N.; Rossi, Fabio MV.; Cullis, Pieter R.
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Anionic Lipid Nanoparticles Preferentially Deliver mRNA to the Hepatic Reticuloendothelial System
err2022-03-10
err107
errOAAI
errPattipeiluhu, Roy; Arias-Alpizar, Gabriela; Basha, Gem; Chan, Karen Y. T.; Bussmann, Jeroen; Sharp, Thomas H.; Moradi, Mohammad-Amin; Sommerdijk, Nico; Harris, Edward N.; Cullis, Pieter R.; Kros, Alexander; Witzigmann, Dominik; Campbell, Frederick
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Simultaneous, Single-Particle Measurements of Size and Loading Give Insights into the Structure of Drug-Delivery Nanoparticles
err2021-11-29
err30
PREAI
errKamanzi, Albert; Gu, Yifei; Tahvildari, Radin; Friedenberger, Zachary; Zhu, Xingqi; Berti, Romain; Kurylowicz, Marty; Witzigmann, Dominik; Kulkarni, Jayesh A.; Leung, Jerry; Andersson, John; Dahlin, Andreas; Hook, Fredrik; Sutton, Mark; Cullis, Pieter R.; Leslie, Sabrina
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FAM13A as potential therapeutic target in modulating TGF-β-induced airway tissue remodeling in COPD
err2021-08-01
err13
errOAAI
errTam, Anthony; Leclair, Pascal; Li, Ling Vicky; Yang, Chen X.; Li, Xuan; Witzigmann, Dominik; Kulkarni, Jayesh A.; Hackett, Tillie-Louise; Dorscheid, Delbert R.; Singhera, Gurpreet K.; Hogg, James C.; Cullis, Pieter R.; Sin, Don D.; Lim, Chinten James
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The current landscape of nucleic acid therapeutics (vol 16, pg 630, 2021)
err2021-06-30
err7
errOAAI
errKulkarni, Jayesh A.; Witzigmann, Dominik; Thomson, Sarah B.; Chen, Sam; Leavitt, Blair R.; Cullis, Pieter R.; van der Meel, Roy
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The current landscape of nucleic acid therapeutics
err2021-05-31
err795
errOAAI
errKulkarni, Jayesh A.; Witzigmann, Dominik; Thomson, Sarah B.; Chen, Sam; Leavitt, Blair R.; Cullis, Pieter R.; van der Meel, Roy
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In vivo adenine base editing of PCSK9 in macaques reduces LDL cholesterol levels
err2021-05-19
err246
errOAAI
errRothgangl, Tanja; Dennis, Melissa K.; Lin, Paulo J. C.; Oka, Rurika; Witzigmann, Dominik; Villiger, Lukas; Qi, Weihong; Hruzova, Martina; Kissling, Lucas; Lenggenhager, Daniela; Borrelli, Costanza; Egli, Sabina; Frey, Nina; Bakker, Noelle; Walker, John A., II; Kadina, Anastasia P.; Victorov, Denis V.; Pacesa, Martin; Kreutzer, Susanne; Kontarakis, Zacharias; Moor, Andreas; Jinek, Martin; Weissman, Drew; Stoffel, Markus; van Boxtel, Ruben; Holden, Kevin; Pardi, Norbert; Thoeny, Beat; Haeberle, Johannes; Tam, Ying K.; Semple, Sean C.; Schwank, Gerald
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mRNA-lipid nanoparticle COVID-19 vaccines: Structure and stability
err2021-05-01
err907
errOAAI
errSchoenmaker, Linde; Witzigmann, Dominik; Kulkarni, Jayesh A.; Verbeke, Rein; Kersten, Gideon; Jiskoot, Wim; Crommelin, Daan J. A.
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