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MFRP is a molecular hub that organizes the apical membrane of RPE cells by engaging in interactions with specific proteins and lipids Tworak, Aleksander; Smidak, Roman; Menezes, Carolline Rodrigues; Du, Samuel W.; Suh, Susie; Choi, Elliot H.; Imanishi, Sanae S.; Dong, Zhiqian; Lewandowski, Dominik; Fong, Kristen E.; Grigorean, Gabriela; Pinto, Antonio F. M.; Xu, Qianlan; Skowronska-Krawczyk, Dorota; Blackshaw, Seth; Imanishi, Yoshikazu; Palczewski, Krzysztof Share Save
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A large-scale CRISPR screen reveals context-specific genetic regulation of retinal ganglion cell regeneration Emmerich, Kevin; Hageter, John; Hoang, Thanh; Lyu, Pin; Sharrock, Abigail V.; Ceisel, Anneliese; Thierer, James; Chunawala, Zeeshaan; Nimmagadda, Saumya; Palazzo, Isabella; Matthews, Frazer; Zhang, Liyun; White, David T.; Rodriguez, Catalina; Graziano, Gianna; Marcos, Patrick; May, Adam; Mulligan, Tim; Reibman, Barak; Saxena, Meera T.; Ackerley, David F.; Qian, Jiang; Blackshaw, Seth; Horstick, Eric; Mumm, Jeff S. Share Save
A combination treatment based on drug repurposing demonstrates mutation-agnostic efficacy in pre-clinical retinopathy models Leinonen, Henri; Zhang, Jianye; Occelli, Laurence M.; Seemab, Umair; Choi, Elliot H.; Marinho, Luis Felipe L. P.; Querubin, Janice; Kolesnikov, Alexander V.; Galinska, Anna; Kordecka, Katarzyna; Hoang, Thanh; Lewandowski, Dominik; Lee, Timothy T.; Einstein, Elliott E.; Einstein, David E.; Dong, Zhiqian; Kiser, Philip D.; Blackshaw, Seth; Kefalov, Vladimir J.; Tabaka, Marcin; Foik, Andrzej; Petersen-Jones, Simon M.; Palczewski, Krzysztof Share Save
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Elevated nuclear TDP-43 induces constitutive exon skipping Carmen-Orozco, Rogger P.; Tsao, William; Ye, Yingzhi; Sinha, Irika R.; Chang, Koping; Trinh, Vickie T.; Chung, William; Bowden, Kyra; Troncoso, Juan C.; Blackshaw, Seth; Hayes, Lindsey R.; Sun, Shuying; Wong, Philip C.; Ling, Jonathan P. Share Save
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