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Subclonal TP53 and KRAS variants combined with poor treatment response identify ultrahigh-risk pediatric patients with T-ALL Kempter, Tamara; Richter-Pechanska, Paulina; Michel, Katarzyna; Rausch, Tobias; Erarslan-Uysal, Buesra; Eckert, Cornelia; Zimmermann, Martin; Stanulla, Martin; Schrappe, Martin; Cario, Gunnar; Koehrer, Stefan; Attarbaschi, Andishe; Korbel, Jan O.; Kunz, Joachim B.; Kulozik, Andreas E. Share Save
Gene therapy in transfusion-dependent non- (3 0 / (3 0 genotype (3-thalassemia: fi rst real-world experience of beti-cel Mirza, Adil; Ritsert, Mona-Lisa; Tao, Gloria; Thakar, Himal; Lobitz, Stephan; Heine, Sabine; Koscher, Leila; Duerken, Matthias; Schmitt, Anita; Schmitt, Michael; Pavel, Petra; Laier, Sascha; Jakoby, Donate; Greil, Johann; Kunz, Joachim; Kulozik, Andreas Share Save
Betibeglogene autotemcel gene therapy in patients with transfusion-dependent, severe genotype β-thalassaemia (HGB-212): a non-randomised, multicentre, single-arm, open-label, single-dose, phase 3 trial Kwiatkowski, Janet L.; Walters, Mark C.; Hongeng, Suradej; Yannaki, Evangelia; Kulozik, Andreas E.; Kunz, Joachim B.; Sauer, Martin G.; Thrasher, Adrian J.; Thuret, Isabelle; Lal, Ashutosh; Tao, Ge; Ali, Shamshad; Thakar, Himal L.; Elliot, Heidi; Lodaya, Ankit; Lee, Ji; Colvin, Richard A.; Locatelli, Franco; Thompson, Alexis A. Share Save
Systematic analysis of RNA-binding proteins identifies targetable therapeutic vulnerabilities in osteosarcoma Zhou, Yang; Ray, Partho Sarothi; Zhu, Jianguo; Stein, Frank; Rettel, Mandy; Sekaran, Thileepan; Sahadevan, Sudeep; Perez-Perri, Joel I.; Roth, Eva K.; Myklebost, Ola; Meza-Zepeda, Leonardo A.; von Deimling, Andreas; Fu, Chuli; Brosig, Annika N.; Boye, Kjetil; Nathrath, Michaela; Blattmann, Claudia; Lehner, Burkhard; Hentze, Matthias W.; Kulozik, Andreas E. Share Save
Treatment of adult ALL patients with third-generation CD19-directed CAR T cells: results of a pivotal trial Schubert, Maria-Luisa; Schmitt, Anita; Hueckelhoven-Krauss, Angela; Neuber, Brigitte; Kunz, Alexander; Waldhoff, Philip; Vonficht, Dominik; Yousefian, Schayan; Jopp-Saile, Lea; Wang, Lei; Korell, Felix; Keib, Anna; Michels, Birgit; Haas, Dominik; Sauer, Tim; Derigs, Patrick; Kulozik, Andreas; Kunz, Joachim; Pavel, Petra; Laier, Sascha; Wuchter, Patrick; Schmier, Johann; Bug, Gesine; Lang, Fabian; Goekbuget, Nicola; Casper, Jochen; Goerner, Martin; Finke, Juergen; Neubauer, Andreas; Ringhoffer, Mark; Wolleschak, Denise; Brueggemann, Monika; Haas, Simon; Ho, Anthony D.; Mueller-Tidow, Carsten; Dreger, Peter; Schmitt, Michael Share Save
Hypersensitivity Reactions to Native E. coli L-asparaginase in Children With Acute Lymphoblastic Leukemia Treated in Trial ALL-BFM 2000: Impact of Treatment Schedule and Type of Glucocorticoid in Induction Moericke, Anja; Rizzari, Carmelo; Alten, Julia; Attarbaschi, Andishe; Beier, Rita; Biondi, Andrea; Burkhardt, Birgit; Bodmer, Nicole; Boos, Joachim; Cario, Gunnar; Conter, Valentino; Flotho, Christian; Kulozik, Andreas; Lanvers-Kaminsky, Claudia; Mann, Georg; Niggli, Felix; Silvestri, Daniela; von Stackelberg, Arend; Stanulla, Martin; Valsecchi, Maria-Grazia; Schrappe, Martin; Zimmermann, Martin Share Save
Targeted long-read sequencing of the Ewing sarcoma 6p25.1 susceptibility locus identifies germline-somatic interactions with EWSR1-FLI1 binding Lee, Olivia W.; Rodrigues, Calvin; Lin, Shu-Hong; Luo, Wen; Jones, Kristine; Brown, Derek W.; Zhou, Weiyin; Karlins, Eric; Khan, Sairah M.; Baulande, Sylvain; Raynal, Virginie; Surdez, Didier; Reynaud, Stephanie; Rubio, Rebeca Alba; Zaidi, Sakina; Grossetete, Sandrine; Ballet, Stelly; Lapouble, Eve; Laurence, Valerie; Pierron, Gaelle; Gaspar, Nathalie; Corradini, Nadege; Marec-Berard, Perrine; Rothman, Nathaniel; Dagnall, Casey L.; Burdett, Laurie; Manning, Michelle; Wyatt, Kathleen; Yeager, Meredith; Chari, Raj; Leisenring, Wendy M.; Kulozik, Andreas E.; Kriebel, Jennifer; Meitinger, Thomas; Strauch, Konstantin; Kirchner, Thomas; Dirksen, Uta; Mirabello, Lisa; Tucker, Margaret A.; Tirode, Franck; Armstrong, Gregory T.; Bhatia, Smita; Robison, Leslie L.; Yasui, Yutaka; Romero-Perez, Laura; Hartmann, Wolfgang; Metzler, Markus; Diver, W. Ryan; Lori, Adriana; Freedman, Neal D.; Hoover, Robert N.; Morton, Lindsay M.; Chanock, Stephen J.; Grunewald, Thomas G. P.; Delattre, Olivier; Machiela, Mitchell J. Share Save
Functional analysis of structural variants in single cells using Strand-seq Jeong, Hyobin; Grimes, Karen; Rauwolf, Kerstin K.; Bruch, Peter-Martin; Rausch, Tobias; Hasenfeld, Patrick; Benito, Eva; Roider, Tobias; Sabarinathan, Radhakrishnan; Porubsky, David; Herbst, Sophie A.; Erarslan-Uysal, Busra; Jann, Johann-Christoph; Marschall, Tobias; Nowak, Daniel; Bourquin, Jean-Pierre; Kulozik, Andreas E.; Dietrich, Sascha; Bornhauser, Beat; Sanders, Ashley D.; Korbel, Jan O. Share Save
Pediatric T-ALL type-1 and type-2 relapses develop along distinct pathways of clonal evolution Richter-Pechanska, Paulina; Kunz, Joachim B.; Rausch, Tobias; Erarslan-Uysal, Busra; Bornhauser, Beat; Frismantas, Viktoras; Assenov, Yassen; Zimmermann, Martin; Happich, Margit; von Knebel-Doeberitz, Caroline; von Neuhoff, Nils; Kohler, Rolf; Stanulla, Martin; Schrappe, Martin; Cario, Gunnar; Escherich, Gabriele; Kirschner-Schwabe, Renate; Eckert, Cornelia; Avigad, Smadar; Pfister, Stefan M.; Muckenthaler, Martina U.; Bourquin, Jean-Pierre; Korbel, Jan O.; Kulozik, Andreas E. Share Save
Final results of the southwest German pilot study on cystic fibrosis newborn screening - Evaluation of an IRT/PAP protocol with IRT-dependent safety net Sommerburg, Olaf; Stahl, Mirjam; Haemmerling, Susanne; Gramer, Gwendolyn; Muckenthaler, Martina U.; Okun, Juergen; Kohlmueller, Dirk; Happich, Margit; Kulozik, Andreas E.; Mall, Marcus A.; Hoffmann, Georg F. Share Save
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Genetic modifiers of fetal hemoglobin affect the course of sickle cell disease in patients treated with hydroxyurea Allard, Pierre; Alhaj, Nareen; Lobitz, Stephan; Cario, Holger; Jarisch, Andreas; Grosse, Regine; Oevermann, Lena; Hakimeh, Dani; Tagliaferri, Laura; Kohne, Elisabeth; Kopp-Schneider, Annette; Kulozik, Andreas E.; Kunz, Joachim B. Share Save
Benefits of a Disease Management Program for Sickle Cell Disease in Germany 2011-2019: The Increased Use of Hydroxyurea Correlates with a Reduced Frequency of Acute Chest Syndrome Kunz, Joachim B.; Schlotmann, Andreas; Daubenbuechel, Andrea; Lobitz, Stephan; Jarisch, Andrea; Grosse, Regine; Cario, Holger; Oevermann, Lena; Hakimeh, Dani; Tagliaferri, Laura; Kulozik, Andreas E. Share Save
Recommendations for diagnosis and treatment of methemoglobinemia Iolascon, Achille; Bianchi, Paola; Andolfo, Immacolata; Russo, Roberta; Barcellini, Wilma; Fermo, Elisa; Toldi, Gergely; Ghirardello, Stefano; Rees, Davis; Van Wijk, Richard; Kattamis, Antonis; Gallagher, Patrick G.; Roy, Noemi; Taher, Ali; Mohty, Razan; Kulozik, Andreas; De Franceschi, Lucia; Gambale, Antonella; De Montalembert, Mariane; Forni, Gian Luca; Harteveld, Cornelis L.; Prchal, Josef Share Save