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Identification of unique cell type responses in pancreatic islets to stress Maestas, Marlie M.; Ishahak, Matthew; Augsornworawat, Punn; Veronese-Paniagua, Daniel A.; Maxwell, Kristina G.; Velazco-Cruz, Leonardo; Marquez, Erica; Sun, Jiameng; Shunkarova, Mira; Gale, Sarah E.; Urano, Fumihiko; Millman, Jeffrey R. Share Save
GLP-1R agonists demonstrate potential to treat Wolfram syndrome in human preclinical models Gorgogietas, Vyron; Rajaei, Bahareh; Heeyoung, Chae; Santacreu, Bruno J.; Marin-Canas, Sandra; Salpea, Paraskevi; Sawatani, Toshiaki; Musuaya, Anyishai; Arroyo, Maria N.; Moreno-Castro, Cristina; Benabdallah, Khadija; Demarez, Celine; Toivonen, Sanna; Cosentino, Cristina; Pachera, Nathalie; Lytrivi, Maria; Cai, Ying; Carnel, Lode; Brown, Cris; Urano, Fumihiko; Marchetti, Piero; Gilon, Patrick; Eizirik, Decio L.; Cnop, Miriam; Igoillo-Esteve, Mariana Share Save
Autophagy is activated for cell survival after endoplasmic reticulum stress Ogata, Maiko; Hino, Shin-ichiro; Saito, Atsushi; Morikawa, Keisuke; Kondo, Shinichi; Kanemoto, Soshi; Murakami, Tomohiko; Taniguchi, Manabu; Tanii, Ichiro; Yoshinaga, Kazuya; Shiosaka, Sadao; Hammarback, James A.; Urano, Fumihiko; Imaizumi, Kazunori Share Save
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Mammalian ECD Protein Is a Novel Negative Regulator of the PERK Arm of the Unfolded Protein Response Olou, Appolinaire A.; Sarkar, Aniruddha; Bele, Aditya; Gurumurthy, C. B.; Mir, Riyaz A.; Ammons, Shalis A.; Mirza, Sameer; Saleem, Irfana; Urano, Fumihiko; Band, Hamid; Band, Vimla Share Save
Multidimensional analysis and therapeutic development using patient iPSC-derived disease models of Wolfram syndrome Kitamura, Rie Asada; Maxwell, Kristina G.; Ye, Wenjuan; Kries, Kelly; Brown, Cris M.; Augsornworawat, Punn; Hirsch, Yoel; Johansson, Martin M.; Weiden, Tzvi; Ekstein, Joseph; Cohen, Joshua; Klee, Justin; Leslie, Kent; Simeonov, Anton; Henderson, Mark J.; Millman, Jeffrey R.; Urano, Fumihiko Share Save
Blocking CHOP-dependent TXNIP shuttling to mitochondria attenuates albuminuria and mitigates kidney injury in nephrotic syndrome Park, Sun-Ji; Kim, Yeawon; Li, Chuang; Suh, Junwoo; Sivapackiam, Jothilingam; Goncalves, Tassia M.; Jarad, George; Zhao, Guoyan; Urano, Fumihiko; Sharma, Vijay; Chen, Ying Maggie Share Save
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Wolframin is a novel regulator of tau pathology and neurodegeneration Chen, Shuo; Acosta, Diana; Li, Liangping; Liang, Jiawen; Chang, Yuzhou; Wang, Cankun; Fitzgerald, Julie; Morrison, Cody; Goulbourne, Chris N.; Nakano, Yoshi; Villegas, Nancy C. Hernandez; Venkataraman, Lalitha; Brown, Cris; Serrano, Geidy E.; Bell, Erica; Wemlinger, Trina; Wu, Min; Kokiko-Cochran, Olga N.; Popovich, Phillip; Flowers, Xena E.; Honig, Lawrence S.; Vonsattel, Jean Paul; Scharre, Douglas W.; Beach, Thomas G.; Ma, Qin; Kuret, Jeff; Koks, Sulev; Urano, Fumihiko; Duff, Karen E.; Fu, Hongjun Share Save
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Genotype-phenotype correlation analysis and therapeutic development using a patient stem cell-derived disease model of Wolfram syndrome Urano, Fumihiko; Kitamura, Rie Asada; Maxwell, Kristina; Ye, Wenjuan; Kries, Kelly; Brown, Cris; Augsornworawat, Punn; Johansson, Martin; Cohen, Joshua; Klee, Justin; Leslie, Kent; Simeonov, Anton; Hirsch, Joel; Weiden, Tzvi; Henderson, Mark; Millman, Jeffrey; Ekstein, Josef Share Save
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A phase Ib/IIa clinical trial of dantrolene sodium in patients with Wolfram syndrome Abreu, Damien; Stone, Stephen, I; Pearson, Toni S.; Bucelli, Robert C.; Simpson, Ashley N.; Hurst, Stacy; Brown, Cris M.; Kries, Kelly; Onwumere, Chinyere; Gu, Hongjie; Hoekel, James; Tychsen, Lawrence; Van Stavern, Gregory P.; White, Neil H.; Marshall, Bess A.; Hershey, Tamara; Urano, Fumihiko Share Save
A target-agnostic screen identifies approved drugs to stabilize the endoplasmic reticulum-resident proteome Henderson, Mark J.; Trychta, Kathleen A.; Yang, Shyh-Ming; Back, Susanne; Yasgar, Adam; Wires, Emily S.; Danchik, Carina; Yan, Xiaokang; Yano, Hideaki; Shi, Lei; Wu, Kuo-Jen; Wang, Amy Q.; Tao, Dingyin; Zahoranszky-Kohalmi, Gergely; Hu, Xin; Xu, Xin; Maloney, David; Zakharov, Alexey, V; Rai, Ganesha; Urano, Fumihiko; Airavaara, Mikko; Gavrilova, Oksana; Jadhav, Ajit; Wang, Yun; Simeonov, Anton; Harvey, Brandon K. Share Save
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