Not logged in Pharmacokinetics, Pharmacodynamics, and Safety of Subcutaneous Belimumab in Pediatric Patients With Systemic Lupus Erythematosus: A Multicenter, Open-Label Trial Brunner, Hermine I.; Anton, Jordi; Calvo-Penades, Inmaculada; Dimelow, Richard; Horneff, Gerd; Kamphuis, Sylvia; Marino, Rebecca; van Maurik, Andre; Minden, Kirsten; Mori, Masaaki; Ocran-Appiah, Josephine; Wilkinson, Christel; Yamasaki, Yuichi; Assudani, Deepak Share Save
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Identification of strengths and weaknesses of the healthcare system for persons living with rare diseases in Catalonia (Spain), and recommendations to improve its comprehensive attention: the acERca las enfermedades raras project Hernandez-Rodriguez, Jose; Martinez-Valle, Fernando; Acebes, Xenia; Alerany, Carmen; Anton, Jordi; Calvo, Gonzalo; Corral, Marian; Cruz, Jordi; Mangues-Bafalluy, M. Antonia; Mateo, Jose; Rivera, Josefa; Salazar, Albert; Francisco, Roser; Mallol, Cristina; Reig-Viader, Rita; Tigri-Santina, Ariadna; Ricart, Assumpta; Palau, Francesc Share Save
Non-Classical Complications of Adult-Onset Still's Disease: A Multicenter Spanish Study Narvaez, Javier; Palacios-Olid, Judith; de Yebenes, Maria Jesus Garcia; Holgado, Susana; Olive, Alejandro; Casafont-Sole, Ivette; Castaneda, Santos; Valero-Martinez, Cristina; Martin-Lopez, Maria; Carreira, Patricia E.; Mora-Liminana, Maribel; Nuno-Nuno, Laura; Robles-Marhuenda, Angel; Bernabeu, Pilar; Campos, Jose; Grana, Jenaro; Ortiz-Santamaria, Vera; Camacho-Lovillo, Marisol; Vargas, Carmen; Sanchez-Manubens, Judith; Anton, Jordi Share Save
Pharmacokinetics, Efficacy, and Safety of Upadacitinib in Pediatric Patients With Polyarticular-Course Juvenile Idiopathic Arthritis: An Interim Analysis of an Open-Label, Phase 1 Trial Brunner, Hermine I.; Shmagel, Anna; Horneff, Gerd; Foeldvari, Ivan; Anton, Jordi; Ramanan, Athimalaipet V.; Qian, Yuli; Unnebrink, Kristina; Hao, Shuai; Camp, Heidi S.; Khan, Nasser; Liu, Wei; Mohamed, Mohamed-Eslam F. Share Save
Recommendations for Transitioning Young People with Primary Immunodeficiency Disorders and Autoinflammatory Diseases to Adult Care Israni, Muskan; Alderson, Eliska; Mahlaoui, Nizar; Obici, Laura; Rossi-Semerano, Linda; Lachmann, Helen; Avramovic, Mojca Zajc; Guffroy, Aurelien; Dalm, Virgil; Rimmer, Rachel; Solis, Leire; Villar, Carlota; Gennery, Andrew R.; Skeffington, Stephanie; Nordin, Julia; Warnatz, Klaus; Korganow, Anne-Sophie; Anton, Jordi; Cattalini, Marco; Berg, Stefan; Soler-Palacin, Pere; Campbell, Mari; Burns, Siobhan O.; ESID Clinical Working Party, Ann; ERN RITA Transition Working Grp Consortium, Anna Share Save
Characterizing Protracted Febrile Myalgia: Fasciitis and Vasculitis of the Fascia and Muscle as Novel Histopathological Features Hernandez-Rodriguez, Jose; Mestre-Trabal, Lola; Gomez-Caverzaschi, Veronica; Araujo, Olga; Terenas, Magda; Robaina, Ricardo; Bolanos, Julio; Prieto-Gonzalez, Sergio; Anton, Jordi; Yague, Jordi; Tomas, Xavier; Aldecoa, Iban; Grau, Josep M. Share Save
Mevalonate kinase deficiency: an updated clinical overview and revision of the SHARE recommendations Lengvari, Lilla; Takacs, Kata; Lengyel, Anna; Palinkas, Annamaria; Wouters, Carine Helena; Kone-Paut, Isabelle; Kuemmerte-Deschner, Jasmin; Jeyaratnam, Jerold; Anton, Jordi; Lachmann, Helen Jane; Gattorno, Marco; Hofer, Michael; Toplak, NataSa; Weiser, Peter; Kallinich, Tilmann; Ozen, Seza; Hentgen, Veronique; Uziel, Yosef; Horvath, Zsuzsanna; Szabados, Marton; Brogan, Paul; Constantin, Tamas; Frenkel, Joost Share Save
Similarities and differences between systemic juvenile idiopathic arthritis and adult-onset Still's disease: a multicenter Spanish study Anton, Jordi; Mosquera, Juan Manuel; Calzada, Joan; Iglesias, Estibaliz; Zacarias, Andrea; Olive, Alejandro; Bittermann, Violeta; Lorenzo, Tania Rodriguez; Remesal, Agustin; Quintana-Ortega, Cristian; Nuno-Nuno, Laura; Robles-Marhuenda, Angel; de Inocencio, Jaime; Martin-Lopez, Maria; Carreira, Patricia E.; Brandy-Garcia, Anahy M.; Holgado, Susana; Camacho-Lovillo, Marisol; Ruiz-Roman, Alberto; Clemente, Daniel; Narvaez, Javier; Campos, Jose; Sanchez-Manubens, Judith; Bernabeu, Pilar; Grana, Jenaro; Vargas, Carmen; Ortiz-Santamaria, Vera; Castaneda, Santos; de Yebenes, Maria Jesus Garcia; Carmona, Loreto Share Save
Enrichment of Rare Variants of Hemophagocytic Lymphohistiocytosis Genes in Systemic Juvenile Idiopathic Arthritis Marques, Mariana Correia; Rubin, Danielle; Shuldiner, Emily G.; Datta, Mallika; Schmitz, Elizabeth; Cruz, Gustavo Gutierrez; Patt, Andrew; Bennett, Elizabeth; Grom, Alexei; Foell, Dirk; Gattorno, Marco; Bohnsack, John; Yeung, Rae S. M.; Prahalad, Sampath; Mellins, Elizabeth; Anton, Jordi; Len, Claudio A.; Oliveira, Sheila; Woo, Patricia; Ozen, Seza; Deng, Zuoming; Ombrello, Michael J. Share Save
THE EUROFEVER FMF LONGITUDINAL COHORT: FIRST LONGITUDINAL DATA Bustaffa, M.; Amaryan, G.; Gallizzi, R.; Papadopoulou-Alataki, E.; Carrabba, M.; Anton, J.; Simonini, G.; Alessio, M.; Breda, L.; Kuemmerle-Deschner, J. B.; Rigante, D.; Obici, L.; Insalaco, A.; Legger, E.; Caorsi, R.; Ruperto, N.; Gattorno, M.; Ozen, S. Share Save
IS GROWTH ADVERSELY AFFECTED IN CHILDREN WITH CHRONIC NON-BACTERIAL OSTEOMYELITIS? Miettunen, P.; Carlini, L.; Insalaco, A.; Anton, J.; Brunner, J.; Legger, E.; Cattalini, M.; Hoppenreijs, E.; Alessio, M.; Mosci, E.; Caorsi, R.; Ruperto, N.; Gattorno, M. Share Save
INCREASED INCIDENCE OF ADVERSE EVENTS AND EVENTS OF SPECIAL INTEREST WITH TREATMENT INTENSIFICATION IN NON-SYSTEMIC JUVENILE IDIOPATHIC ARTHRITIS Miettunen, P.; Gimenez, A. Rebollo; Carlini, L.; Pistorio, A.; Panaviene, V.; Anton, J.; Kamphuis, S.; Herlin, T.; Dolezalova, P.; Cattalini, M.; Susic, G.; Sanner, H.; Maggio, M. C.; Hashad, S.; Abdwani, R.; Rigante, D.; Lorzano, A. Rodriquez; Pallotti, C.; Swart, J. F.; Ruperto, N. Share Save
DIFFERENCES IN CLINICAL PRESENTATION BETWEEN JUVENILE SYSTEMIC SCLEROSIS PATIENTS WITH DIFFUSE AND LIMITED SUBTYPE. RESULTS FROM THE JUVENILE SCLERODERMA INCEPTION COHORT Foeldvari, I.; Klotsche, J.; Torok, K.; Kasapcopur, O.; Adrovic, A.; Feldman, B.; Anton, J.; Johnson, S. R.; Sztajnbok, F. R.; Terreri, M. T.; Sakamoto, A. P.; Khubchandani, R.; Stanevicha, V.; Schonenberg, D.; Al-Abadi, E.; Alexeeva, E.; Katsikas, M.; Sawhney, S.; Smith, V.; Appenzeller, S.; Avcin, T.; Kostik, M.; Lehman, T.; Malcova, H.; Marrani, E.; Pain, C.; Patwardhan, A.; Sifuentes-Giraldo, W. A.; Vasquez-Canizares, N.; Al Saoud, S. Abu; Reis, P. Costa; Janarthanan, M.; Moll, M.; Nemcova, D.; Santos, M. J.; Battagliotti, C.; Berntson, L.; Bica, B.; Brunner, J.; Eleftheriou, D.; Harel, L.; Horneff, G.; Kaiser, D.; Kallinich, T.; Lazarevic, D.; Minden, K.; Nuruzzaman, F.; Hetlevik, S. Opsahl; Sparchez, M.; Uziel, Y.; Helmus, N. Share Save
PRESENCE OF NAILFOLD CAPILLARY CHANGES CORRELATES WITH MORE SEVERE ORGAN INVOLVEMENT IN JUVENILE SYSTEMIC SCLERODERMA. RESULTS OF THE JUVENILE SCLERODERMA INCEPTION COHORT Foeldvari, I.; Klotsche, J.; Torok, K.; Kasapcopur, O.; Adrovic, A.; Feldman, B.; Anton, J.; Johnson, S. R.; Sztajnbok, F. R.; Terreri, M. T.; Sakamoto, A. P.; Stanevicha, V.; Schonenberg, D.; Alexeeva, E.; Katsikas, M.; Khubchandani, R.; Smith, V.; Al-Abadi, E.; Appenzeller, S.; Avcin, T.; Kostik, M.; Lehman, T.; Sawhney, S.; Malcova, H.; Marrani, E.; Pain, C.; Vasquez-Canizares, N.; Saoud, S. Abu Al; Janarthanan, M.; Sifuentes-Giraldo, A.; Reis, P. Costa; Patwardhan, A.; Moll, M.; Nemcova, D.; Santos, M. J.; Battagliotti, C.; Brunner, J.; Eleftheriou, D.; Harel, L.; Berntson, L.; Horneff, G.; Kallinich, T.; Bica, B.; Lazarevic, D.; Minden, K.; Nielsen, S.; Nuruzzaman, F.; Hetlevik, S. Opsahl; Kaiser, D.; Sparchez, M.; Uziel, Y.; Helmus, N. Share Save
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